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Research Article September 19 2025
Reprogramming glutamine metabolism enhances BCMA-CART cell fitness and therapeutic efficacy in multiple myeloma
Flor Navarro,Teresa Lozano,Andrea Fuentes-García,Inés Sánchez-Moreno,Marta Larrayoz,Pedro Justicia,Beatriz Perucha,Maialen Martinez-Tabar,Rebeca Martinez-Turrillas,Noelia Casares,Celia Martín-Otal,Marta Gorraiz,Erin W Meermeier,Marta Chesi,Douglas Lake,Paul Leif Bergsagel,Eva Santamaría,Maria Erendira Calleja-Cervantes,Patxi San Martín-Úriz,Lorea Jordana-Urriza,Xabier Agirre,Sandra Hervas-Stubbs,Juan Roberto Rodriguez-Madoz,Jose A Martínez-Climent,Felipe Prosper,Juan J Lasarte
Research Article September 19 2025
VEXAS syndrome anemia is a mosaic erythroblastopenia
Francois Rodrigues,Giulia Hardouin,Sara El Hoss,Aya Ghoul,Emilie-Fleur Gautier,Michaël Dussiot,Maria A. Lizarralde-Iragorri,Annalisa Santini,Sandy Peltier,Pascal Amireault,Vanessa Soldan,Annarita Miccio,Mounia Debili,Vincent Jachiet,Thiago Trovati Maciel,Julien Rossignol,Eric Allemand,Arsène M Mékinian,Sophie Anne Georgin-Lavialle, Pr,Mohammad Salma,Eric Soler,Pierre-Emmanuel Gleizes,Marie-Francoise O'Donohue,Olivier Kosmider,Manuel S. Rodriguez,Olivier Hermine
Letter September 19 2025
FLAG-IDA plus venetoclax for children, adolescents, and young adults with newly diagnosed AML
Reeja Raj,Samanta Catueno,Amber Gibson,David McCall,Miriam B. Garcia,Cesar Nunez,Michael E. Roth,Koji Sasaki,Priti Tewari,Ghayas C. Issa,Aziz Farhat,Jeremy S Connors,Irtiza Naseer Sheikh,Yuki Nishida,Joanna S Yi,Alexandra M Stevens,Alex Bataller,Kapil N Bhalla,Demetrios Petropoulos,Naval G Daver,Tapan M. Kadia,Branko Cuglievan,Courtney D. DiNardo
Research Article September 19 2025
The watch-and-wait approach for patients with juvenile myelomonocytic leukemia: results of the French cohort
Quentin Neven,Chloé Arfeuille,Aurélie Caye-Eude,Pauline Durand,Elodie Lainey,Odile Fenneteau,Brigitte Nelken,Marie Nolla,Arthur Sterin,Audrey Grain,Céline Khouri,mathieu simonin,Marie-Emilie Dourthe,Mony Fahd,Fréderic Millot,Bénédicte Neven,Arnaud Petit,Sylvie Chevret,Jean-Hugues Dalle,André Baruchel,Hélène Cavé,Marion Strullu
Research Article September 17 2025
Rbm38 Deficiency Impairs Erythroid Heme Biosynthesis and Induces Porphyria via Reduced Ferrochelatase Expression
Research Article September 17 2025
A genome-wide screen identifies Runx2 as a novel regulator of hematopoietic stem cell expansion and T-cell commitment
Research Article September 17 2025
Sclerotic GVHD and Scleroderma Share Dysregulated Gene Expression that is Ameliorated by EREG Therapeutic Antibody
Brief Report September 12 2025
Impact of immunochemotherapy regimens on outcomes of patients with primary mediastinal B-cell lymphoma in the IELSG37 trial
Emanuele Zucca,Luca Ceriani,Giovannino Ciccone,Alice Di Rocco,Maria Cristina Pirosa,Iryna Kriachok,Barbara Botto,Monica Balzarotti, MD,Alessandra Tucci,Sara Veronica Usai,Vittorio Ruggero Zilioli,Elsa Pennese,Luca Arcaini,Anna P Dabrowska-Iwanicka,Andrés J.M. Ferreri,Francesco Merli,Wei-Li Zhao,Luigi Rigacci,Claudia Cellini,David Hodgson,Codruta Ionescu,Carla Minoia,Elisa Lucchini,Michele Spina,Alexander Fosså,Andrea Janikova,Kate Cwynarski,N. George Mikhaeel,Mats Jerkeman,Anastasios Stathis,Kelly S Cozens,Nicoletta Ielmini,Iolanda De Martino,Jan Walewski,Marek Trněný,Franco Cavalli,Umberto Ricardi,Peter W. M. Johnson,Andrew J Davies,Maurizio Martelli
Research Article September 12 2025
Targeting STK17B kinase activates ferroptosis and suppresses drug resistance in multiple myeloma
Research Article September 9 2025
Isatuximab for Relapsed and/or Refractory AL Amyloidosis: Results of a Prospective Phase 2 Trial (SWOG S1702)
Brief Report September 9 2025
Intestinal hepcidin overexpression promotes iron deficiency anemia and counteracts iron overload via DMT1 downregulation
Research Article September 8 2025
Nuclear respiratory factor 1 promotes cell survival in multiple myeloma under proteasome inhibition therapy
Tiziana Bruno,Maria Chiara Cappelletto,Clelia Cortile,Stefano Di Giovenale,Bruno Amadio,Francesca De Nicola,Italia Falcone,Stefano Giuliani,Belinda Palermo,Valeria Catena,Ludovica Ciuffreda,Fulvia Cerruti,Paolo Cascio,Roberta Merola,Serena Masi,Valentina De Pascale,Ombretta Annibali,Silvia Ferraro, +39,Svitlana Gumenyuk,Francesco Pisani,Francesco Marchesi,Andrea Mengarelli,Maurizio Fanciulli,Giacomo Corleone
Research Article September 8 2025
Fixed-Duration Epcoritamab Plus R2 Drives Favorable Outcomes in Relapsed or Refractory Follicular Lymphoma
Lorenzo Falchi,Anna Sureda,Sirpa Leppä,Joost SP Vermaat,Marcel Nijland,Jacob Haaber Christensen,Sven de Vos,Harald Holte,Reid W Merryman,Pieternella J. Lugtenburg,Pau Abrisqueta,Kim Linton,Gauri Sunkersett,Daniela Hoehn,Ali Rana,Aqeel Abbas,Jennifer Marek,Yi Hao,Andrew J Steele,Christopher Morehouse,Martin Hutchings,David Belada
Research Article September 8 2025
Platelet Factor 4 (PF4) Regulates Hematopoietic Stem Cell Aging
Research Article September 4 2025
Leukemia escapes immunity by imposing a type 1 regulatory program on neoantigen-specific CD4+ T cells
Research Article September 4 2025
Acalabrutinib treatment for older (≥80 years old) and/or frail patients with CLL: primary end point analysis of the CLL-Frail trial
Florian Simon,Rudy Ligtvoet,Jan-Paul Bohn,Thomas Nösslinger,Julia von Tresckow,Rüdiger Liersch,Tobias Gaska,Kathleen Jentsch-Ulrich,Michael Gärtner,Thomas Wolff,Ingo Schwaner,Dominik Wolf,Christof Schneider,Ursula Vehling-Kaiser,Matthias Ritgen,Christian Spoer,Michael J. Eckart,Thomas Decker,Geothy Chakupurakal,Björn Schöttker,Jens Kisro,Karl-Anton Kreuzer,Eugen Tausch,Stephan Stilgenbauer,Sandra Robrecht,Janina Stumpf,Anna Fink,Moritz Fürstenau,Kirsten Fischer,Valentin Goede,Michael J Hallek,Barbara F. Eichhorst
Research Article September 4 2025
A bispecific nanobody for the treatment of von Willebrand disease type 1
Research Article September 3 2025
Off-the-shelf dual CAR-iNKT cell immunotherapy eradicates medullary and leptomeningeal high-risk KMT2A-rearranged leukemia
Hongwei Ren,Natalina Elliott,Bryan Lye,Mohammad Umer Sharif Shohan,Joe Wilson Cross,Lucy May Field,Kanagaraju Ponnusamy,Siobhan Rice,Thomas Jackson,Ilia Leontari,Nouhad El Ouazzani,Rebecca Thomas,Sarah Inglott,Jack Bartram,Owen Smith, Professor,Jonathan Bond,Irene Roberts,Christina Halsey,Rachael Bashford-Rogers,Thomas A Milne,Anindita Roy,Anastasios Karadimitris
Research Article September 2 2025
The Origin, Diagnosis, and Prognosis of Oligomannose-Type Diffuse Large B-Cell Lymphoma
Research Article September 2 2025
Nanoromidepsin, a Polymer Nanoparticle of the HDAC Inhibitor, Improves Safety and Efficacy in Models of T-cell Lymphoma
Research Article September 2 2025
Impact of ASXL1 at diagnosis in patients with CML receiving frontline potent TKIs: high risk of kinase domain mutations
Naranie Shanmuganathan,David T Yeung,Carol Wadham,Adelina Fernandes,Muneeza Maqsood,NurHezrin Shahrin,Verity A Saunders, Ms,Rosalie Kenyon,Ming Lin,John Toubia,Joe McConnell,Dominik Kaczorowski,David M. Ross,Agnes SM Yong,Lynette Chee,Jake Shortt,Nicholas Viiala,Jodi A Braley,Chung Hoow Kok,Timothy P Hughes,Susan Branford
Research Article August 27 2025
Targeting FXR in Hepatocytes: A Promising Approach to Enhance Fibrinolysis and Reduce Deep Vein Thrombosis Risk
Research Article August 27 2025
The impact of fitness and dose intensity on clinical outcomes with venetoclax-obinutuzumab in CLL
Othman Al-Sawaf,Moritz Fürstenau,Adam Giza,Sandra Robrecht,Julia von Tresckow,Anna Fink,Florian Simon,Eugen Tausch,Christof Schneider,Liliya Sivcheva,Anthony P. Schwarer,Javier Loscertales,Robert Weinkove,Dirk Strumberg,Allanah Kilfoyle,Gunnar Juliusson,Caspar da Cunha-Bang,Thomas Illmer,Michael Gregor,Patrick Thornton,Ann Janssens,Tamar Tadmor,Vesa Lindstrom,Philipp B. Staber,Mark-David Levin,Clemens-Martin Wendtner,Karl-Anton Kreuzer,Matthias Ritgen,Stephan Stilgenbauer,Arnon P. Kater,Carsten Utoft Niemann,Kirsten Fischer,Barbara F. Eichhorst,Michael J Hallek
Research Article August 27 2025
CD371-Targeted CAR T cells Secreting Interleukin-18 Exhibit Robust Expansion and Clear Refractory Acute Myeloid Leukemia
Mark B. Geyer,Susan DeWolf,Xiaoli Mi,Kenyon Weis,Brian C. Shaffer,Briana Cadzin,Devin McAvoy,Zoe A Katsamakis,Rachel Lorenc,Alexander M Lewis,Brianna Gipson,M. Adriana Cuibus,Narina N. Girotra,Kenton Wu,Natalie Smith,Erin R. Burns,Jasmine S. Um,Sarah Yoo,Behzad Kharabi Masouleh,Pallavi K. Galera,Kinga Hosszu,Jagrutiben Chaudhari,Xiuyan Wang,Qianqian Lin,Kevin J. Curran,Jae H Park,David A Scheinberg,Marcel R.M. van den Brink,Omar Abdel-Wahab,Renier J. Brentjens,Anthony F. Daniyan
Research Article August 27 2025
An immunostimulatory CELMoD combination overcomes resistance to T-cell engagers caused by a high multiple myeloma burden
Research Article August 27 2025
Long term follow-up outcomes in congenital thrombotic thrombocytopenic purpura
Research Article August 26 2025
Chronic NK cell activation results in a dysfunctional, tissue resident-like state mediated by KLF2 deficiency
Brief Report August 26 2025
A prime editing strategy to rewrite the γ-globin promoters and reactivate fetal hemoglobin for sickle cell disease
Brief Report August 26 2025
Plasma lipid levels predict chemotherapy response and survival in acute myeloid leukemia
Research Article August 26 2025
LEF1 Intragenic Deletion Induces a Dominant-Negative isoform and unveils a Wnt/β3-Catenin Vulnerability in T-ALL
Research Article August 22 2025
Mitochondrial DNA via recipient TLR9 acts as a potent first-hit in murine transfusion-related acute lung injury (TRALI)
Research Article August 22 2025
F8 gene variants influence the response to desmopressin in hemophilia A carriers
Benoît Guillet,Roseline D'Oiron,Marc Trossaert,Bénédicte Wibaut,Brigitte Pan-Petesch,Birgit Frotscher,Fabienne Genre-Volot,Laurent Ardillon,Stéphanie Desage,Céline Falaise,Christine Biron-Andreani,Vincent Cussac,Brigitte Tardy,Yoann Huguenin,Herve Chambost,Sophie Bayart,Sabine-Marie Castet,Xavier Delavenne
Research Article August 20 2025
Challenging the Concept of Functional High-Risk Myeloma through Transcriptional and Genetic Profiling
Research Article August 19 2025
A T-cell-based metric of immune age predicts outcomes in older patients with myeloma receiving daratumumab-based therapy
Wassilis S.C. Bruins,Febe Smits,Carolien Duetz,Kaz Groen,Charlotte L.B.M. Korst,A. Vera de Jonge, dr.,Christie P.M. Verkleij,Rosa Rentenaar,Meliha Cosovic,Merve Eken,Inoka Twickler,Paola M. Homan-Weert,Pieter Sonneveld,Philippe Moreau,Jürgen Claesen,Niels W.C.J. van de Donk,Sonja Zweegman,Tuna Mutis
Research Article August 19 2025
A phase 2 study of zanubrutinib in combination with rituximab and lenalidomide in de novo diffuse large B-cell lymphoma
Research Article August 19 2025
Proteomic subtypes enrich current acute myeloid leukemia nomenclature and reflect intrinsic pathogenesis alongside aging
Wenyan Cheng,Xiao Yi,Zhenyi Wang,Jian-Feng Li,Jun-Yi Zhang,Rui-Hong Zhang,Qian-Qian Zhang,Xiangqin Weng,Ting Huang,Yong-Mei Zhu,Chao Wang,Wei Yin,Jia-Nan Zhang,Hui-Yi Wu,Jun-Min Li,Hongming Zhu,Li Chen,Wen-Fang Wang,Yuting Dai,Chen-Xu Gao,Xuan Liu,Shan Wang,Shengyue Wang,Bo Jiao,Zhu Chen,Hai Fang,Tong Yin,Yang Shen,Sai-Juan Chen
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