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Gene Therapy
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Journal Articles
Clinical Trials & Observations
Nora M. Gibson, Eugene Khandros, Caitlin W. Elgarten, Elizabeth Worster, Dimitrios S. Monos, Alexis A. Thompson, Janet L. Kwiatkowski, Timothy S. Olson
Journal:
Blood
Blood (2025) 145 (22): 2666–2670.
Published: 2025
Includes: Supplemental data
Journal Articles
Clinical Trials & Observations
Julio C. Chavez, Michael Dickinson, Javier Munoz, Matthew L. Ulrickson, Catherine Thieblemont, Olalekan O. Oluwole, Alex F. Herrera, Chaitra S. Ujjani, Yi Lin, Peter A. Riedell, Natasha Kekre, Sven de Vos, Jacob Wulff, Chad M. Williams, Joshua Winters, Ioana Kloos, Hairong Xu, Sattva S. Neelapu
Journal:
Blood
Blood (2025) 145 (20): 2303–2311.
Published: 2025
Includes: Supplemental data
Journal Articles
An erythroid-specific lentiviral vector improves anemia and iron metabolism in a new model of XLSA
Available to PurchaseCarlo Castruccio Castracani, Laura Breda, Tyler E. Papp, Amaliris Guerra, Enrico Radaelli, Charles-Antoine Assenmacher, Giovanni Finesso, Barbara L. Mui, Ying K. Tam, Simona Fontana, Chiara Riganti, Veronica Fiorito, Sara Petrillo, Emanuela Tolosano, Hamideh Parhiz, Stefano Rivella
Journal:
Blood
Blood (2025) 145 (1): 98–113.
Published: 2025
Includes: Supplemental data
Journal Articles
How I treat sickle cell disease with gene therapy
Available to Purchase
Journal:
Blood
Blood (2024) 144 (26): 2693–2705.
Published: 2024
Journal Articles
T-cell lymphomas in recipients of CAR-T cells: assessing risks and causalities
Available to Purchase
Journal:
Blood
Blood (2024) 144 (24): 2473–2481.
Published: 2024
Journal Articles
Coagulation factor VIII: biological basis of emerging hemophilia A therapies
Available to Purchase
Journal:
Blood
Blood (2024) 144 (21): 2185–2197.
Published: 2024
Includes: Supplemental data
Journal Articles
Genetic engineering of transfusable platelets with mRNA-lipid nanoparticles is compatible with blood banking practices
Available to PurchaseColton Strong, Jerry Leung, Emma Kang, Katherine E. Badior, Madelaine Robertson, Nicolas Pereyra, Elyn M. Rowe, Amanda Wietrzny, Brenda Ma, Zechariah Noronha, Deaglan Arnold, Marco A. Ciufolini, Dana V. Devine, Eric Jan, Pieter R. Cullis, Christian J. Kastrup
Journal:
Blood
Blood (2024) 144 (21): 2223–2236.
Published: 2024
Includes: Supplemental data
Journal Articles
Use of HSC-targeted LNP to generate a mouse model of lethal α-thalassemia and treatment via lentiviral gene therapy
Available to PurchaseMaxwell E. Chappell, Laura Breda, Lucas Tricoli, Amaliris Guerra, Danuta Jarocha, Carlo Castruccio Castracani, Tyler E. Papp, Naoto Tanaka, Nolan Hamilton, Michael P. Triebwasser, Valentina Ghiaccio, Megan T. Fedorky, Kandace L. Gollomp, Veronica Bochenek, Aoife M. Roche, John K. Everett, Emma J. Cook, Frederic D. Bushman, Nattiya Teawtrakul, Stavros Glentis, Antonis Kattamis, Barbara L. Mui, Ying K. Tam, Drew Weissman, Osheiza Abdulmalik, Hamideh Parhiz, Stefano Rivella
Journal:
Blood
Blood (2024) 144 (15): 1633–1645.
Published: 2024
Includes: Supplemental data
Journal Articles
Christopher J. Nicolai, Maura H. Parker, Jim Qin, Weiliang Tang, Justin T. Ulrich-Lewis, Rebecca J. Gottschalk, Sara E. Cooper, Susana A. Hernandez Lopez, Don Parrilla, Richard S. Mangio, Nolan G. Ericson, Alissa H. Brandes, Saluwa Umuhoza, Kathryn R. Michels, Mollie M. McDonnell, Lisa Y. Park, Seungjin Shin, Wai-Hang Leung, Andrew M. Scharenberg, Hans-Peter Kiem, Ryan P. Larson, Laurie O. Beitz, Byoung Y. Ryu
Journal:
Blood
Blood (2024) 144 (9): 977–987.
Published: 2024
Includes: Supplemental data
Journal Articles
Carys S. Johnson, Matthew Williams, Kendig Sham, Serena Belluschi, Wenjuan Ma, Xiaonan Wang, Winnie W. Y. Lau, Kerstin B. Kaufmann, Gabriela Krivdova, Emily F. Calderbank, Nicole Mende, Jessica McLeod, Giovanna Mantica, Juan Li, Charlotte Grey-Wilson, Michael Drakopoulos, Shaaezmeen Basheer, Shubhankar Sinha, Evangelia Diamanti, Christina Basford, Nicola K. Wilson, Steven J. Howe, John E. Dick, Berthold Göttgens, Anthony R. Green, Natalie Francis, Elisa Laurenti
Journal:
Blood
Blood (2024) 144 (7): 729–741.
Published: 2024
Includes: Supplemental data
Journal Articles
CAR T cells vs bispecific antibody as third- or later-line large B-cell lymphoma therapy: a meta-analysis
Available to Purchase
Clinical Trials & Observations
Journal:
Blood
Blood (2024) 144 (6): 629–638.
Published: 2024
Includes: Supplemental data
Journal Articles
Human herpesvirus 6 reactivation and disease are infrequent in chimeric antigen receptor T-cell therapy recipients
Available to Purchase
Clinical Trials & Observations
Brief Report
Eleftheria Kampouri, Elizabeth M. Krantz, Hu Xie, Sarah S. Ibrahimi, Erika S. Kiem, Mandeep K. Sekhon, Emily C. Liang, Andrew J. Cowan, Andrew Portuguese, Damian J. Green, Aya Albittar, Jennifer J. Huang, Jordan Gauthier, Ailyn C. Pérez-Osorio, Keith R. Jerome, Danielle M. Zerr, Michael J. Boeckh, Joshua A. Hill
Journal:
Blood
Blood (2024) 144 (5): 490–495.
Published: 2024
Includes: Supplemental data
Journal Articles
SOX11 expression is restricted to EBV-negative Burkitt lymphoma and is associated with molecular genetic features
Available to PurchaseMarta Sureda-Gómez, Ingram Iaccarino, Anna De Bolòs, Mieke Meyer, Patricia Balsas, Julia Richter, Marta-Leonor Rodríguez, Cristina López, Maria Carreras-Caballé, Selina Glaser, Ferran Nadeu, Pedro Jares, Guillem Clot, Maria Chiara Siciliano, Cristiana Bellan, Salvatore Tornambè, Roberto Boccacci, Lorenzo Leoncini, Elias Campo, Reiner Siebert, Virginia Amador, Wolfram Klapper
Journal:
Blood
Blood (2024) 144 (2): 187–200.
Published: 2024
Includes: Supplemental data
Journal Articles
Integration of ζ -deficient CARs into the CD3 ζ gene conveys potent cytotoxicity in T and NK cells
Available to PurchaseJonas Kath, Clemens Franke, Vanessa Drosdek, Weijie Du, Viktor Glaser, Carla Fuster-Garcia, Maik Stein, Tatiana Zittel, Sarah Schulenberg, Caroline E. Porter, Lena Andersch, Annette Künkele, Joshua Alcaniz, Jens Hoffmann, Hinrich Abken, Mohamed Abou-el-Enein, Axel Pruß, Masataka Suzuki, Toni Cathomen, Renata Stripecke, Hans-Dieter Volk, Petra Reinke, Michael Schmueck-Henneresse, Dimitrios L. Wagner
Journal:
Blood
Blood (2024) 143 (25): 2599–2611.
Published: 2024
Includes: Supplemental data
Journal Articles
CME
Clinical Trials & Observations
Adetola A. Kassim, Josu de la Fuente, Erfan Nur, Karina L. Wilkerson, Ali D. Alahmari, Adriana Seber, Carmem Bonfim, Belinda Pinto Simões, Mohsen Alzahrani, Michael J. Eckrich, Biljana Horn, Rabi Hanna, Nathalie Dhedin, Hemalatha G. Rangarajan, Roseane Vasconcelos Gouveia, Fahad Almohareb, Mahmoud Aljurf, Mohammed Essa, Bader Alahmari, Katie Gatwood, James A. Connelly, Elisabeth Dovern, Mark Rodeghier, Michael R. DeBaun
Journal:
Blood
Blood (2024) 143 (25): 2654–2665.
Published: 2024
Includes: Supplemental data
Journal Articles
Vector integration and fate in the hemophilia dog liver multiple years after AAV-FVIII gene transfer
Available to PurchasePaul Batty, Sylvia Fong, Matteo Franco, Choong-Ryoul Sihn, Laura L. Swystun, Saira Afzal, Lorianne Harpell, David Hurlbut, Abbey Pender, Cheng Su, Hauke Thomsen, Christopher Wilson, Loubna Youssar, Andrew Winterborn, Irene Gil-Farina, David Lillicrap
Journal:
Blood
Blood (2024) 143 (23): 2373–2385.
Published: 2024
Includes: Supplemental data
Journal Articles
Clinical Trials & Observations
Magdi Elsallab, Moataz Ellithi, Matthew A. Lunning, Christopher D’Angelo, Jihyun Ma, Miguel-Angel Perales, Matthew Frigault, Marcela V. Maus
Journal:
Blood
Blood (2024) 143 (20): 2099–2105.
Published: 2024
Includes: Supplemental data
Journal Articles
Journal Articles
Wei Liu, Yue Wu, Huaiqing Wei, Juan Ma, Wenya Feng, Qiuyuan Yang, Shuping Zhang, Tomas Ganz, Sijin Liu
Journal:
Blood
Blood (2024) 143 (11): 1045–1049.
Published: 2024
Includes: Supplemental data
Journal Articles
Clinical Trials & Observations
Andrew D. Leavitt, Barbara A. Konkle, Kimo C. Stine, Nathan Visweshwar, Thomas J. Harrington, Adam Giermasz, Steven Arkin, Annie Fang, Frank Plonski, Anne Yver, Florence Ganne, Delphine Agathon, Maria de los Angeles Resa, Li-Jung Tseng, Gregory Di Russo, Bettina M. Cockroft, Liching Cao, Jeremy Rupon
Journal:
Blood
Blood (2024) 143 (9): 796–806.
Published: 2024
Includes: Supplemental data
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