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Doyoung Lee
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Journal Articles

Enhancing FVIII Expression By Modifying B-Domain Sequence for Hemophilia A Gene Therapy

Doyoung Lee, PhD, Jenny McIntosh, PhD, Allison Dane, PhD, Cecilia Rosales, PhD, Anne Riddell, Edward Tuddenham, MD, Amit C Nathwani, MD PhD
Journal: Blood
Blood (2018) 132 (Supplement 1): 3484.
https://doi.org/10.1182/blood-2018-99-113830
Published: 2018
Journal Articles

Preclinical Evaluation of an Engineered AAV Capsid in Non-Human Primates for the Treatment of Haemophilia B

Allison Dane, PhD, Jenny McIntosh, Doyoung Lee, PhD, Rose Sheridan, Mark Maginn, Romuald Corbau, PhD, Andrew M. Davidoff, MD, Amit C Nathwani, MD PhD
Journal: Blood
Blood (2018) 132 (Supplement 1): 2197.
https://doi.org/10.1182/blood-2018-99-117969
Published: 2018
Journal Articles

GO-8: Preliminary Results of a Phase I/II Dose Escalation Trial of Gene Therapy for Haemophilia a Using a Novel Human Factor VIII Variant

Amit C Nathwani, MD PhD, Edward Tuddenham, MD, Pratima Chowdary, MD, Jenny McIntosh, PhD, Doyoung Lee, PhD, Cecilia Rosales, PhD, Mark Phillips, Jun Pie, Zhou Junfang, Michael M Meagher, PhD, Ulrike Reiss, MD, Andrew M. Davidoff, MD, Chris L Morton, Anne Riddell
Journal: Blood
Blood (2018) 132 (Supplement 1): 489.
https://doi.org/10.1182/blood-2018-99-118256
Published: 2018
Journal Articles

Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant

Jenny McIntosh, Peter J. Lenting, Cecilia Rosales, Doyoung Lee, Samira Rabbanian, Deepak Raj, Nishil Patel, Edward G. D. Tuddenham, Olivier D. Christophe, John H. McVey, Simon Waddington, Arthur W. Nienhuis, John T. Gray, Paolo Fagone, Federico Mingozzi, Shang-Zhen Zhou, Katherine A. High, Maria Cancio, Catherine Y. C. Ng, Junfang Zhou, Christopher L. Morton, Andrew M. Davidoff, Amit C. Nathwani
Journal: Blood
Blood (2013) 121 (17): 3335–3344.
https://doi.org/10.1182/blood-2012-10-462200
Published: 2013
Includes: Supplemental data