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Paul Telfer
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Journal Articles

Multi-dimensional adherence patterns in rare haematological conditions: Longitudinal analysis of real-world patient-reported outcomes

Free
Kim Summers, Orlando Agrippa, Andrea Preston, Muna Yusuf, Tushar Singh, Georgina O'Neill, Claire Harrison, Patrick Harrington, Shirley D'Sa, Paul Telfer, Sanne Lugthart
Journal: Blood
Blood (2025) 146 (Supplement 1): 7973.
https://doi.org/10.1182/blood-2025-7973
Published: 2025
Journal Articles

Long-term follow-up demonstrates durable clinical benefits of exagamglogene autotemcel for sickle cell disease with recurrent vaso-occlusive crises: Final results of climb SCD-121

Free
Stephan Grupp, Franco Locatelli, Akshay Sharma, Monica Bhatia, Markus Mapara, Robert Liem, Laurence Dedeken, Lyndsay Molinari, Michael Eckrich, Kevin Kuo, Paul Telfer, Ami Shah, Marina Cavazzana, Selim Corbacioglu, Mariane de Montalembert, Stephan Lobitz, Damiano Rondelli, Martin Steinberg, Mark Walters, Kevin Boerner, Tina Liu, Suzan Imren, William Hobbs, Haydar Frangoul
Journal: Blood
Blood (2025) 146 (Supplement 1): 2537.
https://doi.org/10.1182/blood-2025-2537
Published: 2025
Journal Articles

Stability and evolution of individual-level biomarker patterns across repeated vaso-occlusive crises in sickle cell disease

Free
Kim Summers, Orlando Agrippa, Alfonso Portabales, Kunjan Rana, Paul Telfer, Sanne Lugthart
Journal: Blood
Blood (2025) 146 (Supplement 1): 6222.
https://doi.org/10.1182/blood-2025-6222
Published: 2025
Journal Articles

Resolvins modulate haematopoietic stem and progenitor cell dysfunction and neutrophil activation in sickle cell disease

Free
Vishaka Gorur, Duco Koenis, Emmanuel Albuquerque-Souza, Monika Buczek, Ditte Olsen, Paul Telfer, Jesmond Dalli
Journal: Blood
Blood (2025) 146 (Supplement 1): 1148.
https://doi.org/10.1182/blood-2025-1148
Published: 2025
Journal Articles

Enhanced Artificial Intelligence (AI)-Driven Prediction of Vaso-Occlusive Crises in Sickle Cell Disease: Precision through Advanced Machine-Learning Frameworks and Digital Remote Monitoring

Free
Kim Z Summers, Orlando Agrippa, David Ade-Odunlade, Kofi A. Anie, Paul Telfer, Sanne Lugthart
Journal: Blood
Blood (2024) 144 (Supplement 1): 522.
https://doi.org/10.1182/blood-2024-209961
Published: 2024
Journal Articles

A Virtual Hospital Approach in Sickle Cell Disease | Remote Biometric, Quality of Life, and Hospitalisations Monitoring

Free
Kim Summers, Orlando Agrippa, Kofi A. Anie, Paul Telfer, Sanne Lugthart
Journal: Blood
Blood (2024) 144 (Supplement 1): 5072.
https://doi.org/10.1182/blood-2024-210919
Published: 2024
Journal Articles

Comparison of Sickle Cell Disease Patient Experiences in Developed and Developing Countries: Insights from UK and India Patient Cohorts

Free
Ashley Lai, Kim Summers, Orlando Agrippa, Kofi A. Anie, Paul Telfer, Sanne Lugthart
Journal: Blood
Blood (2024) 144 (Supplement 1): 5071.
https://doi.org/10.1182/blood-2024-210767
Published: 2024
Journal Articles

Durable Clinical Benefits with Exagamglogene Autotemcel for Severe Sickle Cell Disease

Free
Haydar Frangoul, Franco Locatelli, Akshay Sharma, Monica Bhatia, Markus Y Mapara, Robert I. Liem, Donna Wall, Lyndsay Molinari, Laurence Dedeken, Kevin H.M. Kuo, Paul Telfer, Ami J. Shah, Marina Cavazzana, Selim Corbacioglu, Michael J. Eckrich, Damiano Rondelli, Roland Meisel, Stephan Lobitz, Mariane De Montalembert, Martin H. Steinberg, Mark C. Walters, Laura Bower, Suzan Imren, Tina Liu, Weiyu Zhou, William Hobbs, Stephan A. Grupp
Journal: Blood
Blood (2024) 144 (Supplement 1): 4954.
https://doi.org/10.1182/blood-2024-204001
Published: 2024
Journal Articles

Real-World Outcomes and Digitally Monitored Quality of Life in Voxelotor-Treated Patients with Sickle Cell Disease

Free
Kim Summers, Orlando Agrippa, Oliver Shastri, Seraj Sharif, Kofi Anie, Paul Telfer, Sanne Lugthart
Journal: Blood
Blood (2023) 142 (Supplement 1): 2383.
https://doi.org/10.1182/blood-2023-181426
Published: 2023
Journal Articles

Predicting Vaso-Occlusive Crises in Sickle Cell Disease through Digital, Longitudinal Tracking of Wearable Metrics and Patient-Reported Outcomes

Free
Kim Summers, Orlando Agrippa, Sanne Lugthart, Kofi Anie, Paul Telfer
Journal: Blood
Blood (2023) 142 (Supplement 1): 1059.
https://doi.org/10.1182/blood-2023-181407
Published: 2023
Journal Articles

Over 4 Years of Safety and Efficacy with Voxelotor Treatment for Patients with Sickle Cell Disease: Updated Results from an Open-Label Extension of the Phase 3 HOPE Trial

Free
Maureen Okam Achebe, Hoda MA Hassab, Salam Al-Kindi, Clark Brown, Paul Telfer, Bart J. Biemond, Thokozeni Lipato, Mark Davis, Sarah Gray, Victor R. Gordeuk
Journal: Blood
Blood (2023) 142 (Supplement 1): 2527.
https://doi.org/10.1182/blood-2023-188616
Published: 2023
Journal Articles

Exagamglogene Autotemcel for Severe Sickle Cell Disease

Free
Haydar Frangoul, Franco Locatelli, Akshay Sharma, Monica Bhatia, Markus Mapara, Lyndsay Molinari, Donna Wall, Robert I. Liem, Paul Telfer, Ami J. Shah, Marina Cavazzana, Selim Corbacioglu, Damiano Rondelli, Roland Meisel, Laurence Dedeken, Stephan Lobitz, Mariane de Montalembert, Martin H. Steinberg, Mark C. Walters, Laura Bower, Suzan Imren, Christopher Simard, Fengjuan Xuan, Weiyu Zhou, Phuong Khanh Morrow, William Hobbs, Stephan Grupp
Journal: Blood
Blood (2023) 142 (Supplement 1): 1052.
https://doi.org/10.1182/blood-2023-190139
Published: 2023
Journal Articles

Severe Acute Complications of Sickle Cell Disease in Two Expert Referral Centers (UK and Italy): Natural History Studies Highlight Ongoing Unmet Need for Effective Disease Modifying or Curative Therapies

Free
Raffaella Colombatti, Cynthia Sangarappillai, Muriel Soriano, Jonathan Bestwick, Will Hann, Karolina Wieczorek, Vania Munaretto, Beatrice Coppadoro, Giulia Reggiani, Laura Sainati, Anjulika Chawla, Charu Puri-Sharma, Courtney Walls, Sanjeev Kommera, Paul Telfer
Journal: Blood
Blood (2021) 138 (Supplement 1): 3093.
https://doi.org/10.1182/blood-2021-151407
Published: 2021
Journal Articles

Long-Term Safety and Efficacy of Voxelotor for Patients with Sickle Cell Disease: Results from an Open-Label Extension of the Phase 3 HOPE Trial

Free
Maureen Achebe, Hoda Hassab, Salam Alkindi, R. Clark Clark Brown, Paul Telfer, Bart J. Biemond, Victor R. Gordeuk, Thokozeni Lipato, Margaret Tonda, Sarah Gray, Joanna Howard
Journal: Blood
Blood (2021) 138 (Supplement 1): 3114.
https://doi.org/10.1182/blood-2021-153582
Published: 2021
Journal Articles

Higher Hemoglobin Levels Achieved with Voxelotor Are Associated with Lower Vaso-occlusive Crisis Incidence: 72-Week Analysis from the HOPE Study

Free
Elliott Vichinsky, MD, Victor R. Gordeuk, MD, Paul Telfer, DM, FRCP, Adlette Inati, MD FAAP, Margaret Tonda, PharmD, Sarah Gray, PhD, Irene Agodoa, MD, Kenneth I. Ataga, MD
Journal: Blood
Blood (2020) 136 (Supplement 1): 31–32.
https://doi.org/10.1182/blood-2020-140863
Published: 2020
Journal Articles

Improvement in the Clinical Global Impression of Change with Voxelotor in Patients with Sickle Cell Disease in the Phase 3 HOPE Trial

Free
Wally R Smith, MD, Jane S. Hankins, MD MS, Miguel R Abboud, MD, Ze Cong, PhD, Jonathan Sorof, MD, Sarah Gray, PhD, Carolyn Hoppe, MD, Paul Telfer, DM, FRCP
Journal: Blood
Blood (2020) 136 (Supplement 1): 5–6.
https://doi.org/10.1182/blood-2020-137121
Published: 2020
Journal Articles

Incidence of Vaso-Occlusive Crisis Does Not Increase with Achieving Higher Hemoglobin Levels on Voxelotor Treatment or after Discontinuation: Analyses of the HOPE Study

Free
Elliott P. Vichinsky, MD, Paul Telfer, DM, FRCP, Adlette Inati, MD, Margaret Tonda, PharmD, Barbara Tong, PhD, Irene Agodoa, MD, Joshua Lehrer-Graiwer, MD MPhil, FACC, Kenneth I. Ataga, MD
Journal: Blood
Blood (2019) 134 (Supplement_1): 2313.
https://doi.org/10.1182/blood-2019-129026
Published: 2019
Journal Articles

Routine Management, Healthcare Resource Use and Patient/Caregiver-Reported Outcomes of Patients with Transfusion-Dependent β-Thalassaemia in the United Kingdom: A Mixed Methods Observational Study

Free
Farrukh Shah, MDMBBS,FRCPath, Paul Telfer, DM, FRCP, Mark Velangi, Shivan Pancham, Robert Wynn, Sally Pollard, Elizabeth Chalmers, Jonathan Kell, MD, Joe Hickey, PhD, Clark Paramore, MPH, Minesh Jobanputra, MD, Kate Ryan, MD
Journal: Blood
Blood (2019) 134 (Supplement_1): 3550.
https://doi.org/10.1182/blood-2019-129930
Published: 2019
Journal Articles

A phase 1/2 ascending dose study and open-label extension study of voxelotor in patients with sickle cell disease

Free
Clinical Trials & Observations
Jo Howard, Claire Jane Hemmaway, Paul Telfer, D. Mark Layton, John Porter, Moji Awogbade, Timothy Mant, Daniel D. Gretler, Kobina Dufu, Athiwat Hutchaleelaha, Mira Patel, Vincent Siu, Sandra Dixon, Noel Landsman, Margaret Tonda, Joshua Lehrer-Graiwer
Journal: Blood
Blood (2019) 133 (17): 1865–1875.
https://doi.org/10.1182/blood-2018-08-868893
Published: 2019
Journal Articles

Results from Part A of the Hemoglobin Oxygen Affinity Modulation to Inhibit HbS Polymerization (HOPE) Trial (GBT440-031), a Placebo-Controlled Randomized Study Evaluating Voxelotor (GBT440) in Adults and Adolescents with Sickle Cell Disease

Free
Elliott Vichinsky, MD, Carolyn Hoppe, Jo Howard, Kenneth I. Ataga, Videlis Nduba, Amal El-Beshlawy, David L. Diuguid, Salam Al-Kindi, Clark Brown, Hoda Hassab, MD, Paul Telfer, Dimitris A. Tsitsikas, Selma Unal, Julie Kanter, MD, Miguel R. Abboud, Victor R. Gordeuk, MD, Joshua Lehrer-Graiwer, Claire Sherman, Margaret Tonda, PharmD, Allison Intondi, Yifah Yaron, Russell E. Ware, MD PhD
Journal: Blood
Blood (2018) 132 (Supplement 1): 505.
https://doi.org/10.1182/blood-2018-99-118508
Published: 2018