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Lyndsay Molinari
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Journal Articles

Long-term follow-up demonstrates durable clinical benefits of exagamglogene autotemcel for sickle cell disease with recurrent vaso-occlusive crises: Final results of climb SCD-121

Free
Stephan Grupp, Franco Locatelli, Akshay Sharma, Monica Bhatia, Markus Mapara, Robert Liem, Laurence Dedeken, Lyndsay Molinari, Michael Eckrich, Kevin Kuo, Paul Telfer, Ami Shah, Marina Cavazzana, Selim Corbacioglu, Mariane de Montalembert, Stephan Lobitz, Damiano Rondelli, Martin Steinberg, Mark Walters, Kevin Boerner, Tina Liu, Suzan Imren, William Hobbs, Haydar Frangoul
Journal: Blood
Blood (2025) 146 (Supplement 1): 2537.
https://doi.org/10.1182/blood-2025-2537
Published: 2025
Journal Articles

CRISPR-Cas12a gene editing of the HBG1/2 promoters leads to sustained normalization of total hemoglobin and increased fetal hemoglobin in patients with severe sickle cell disease: Updated Results from the RUBY trial

Free
Rabi Hanna, Haydar Frangoul, Luis Pineiro, Christopher McKinney, Markus Mapara, Jignesh Dalal, Hemalatha Rangarajan, Harold Atkins, Monica Bhatia, Deepakbabu Chellapandian, Jennifer Jaroscak, Lakshmanan Krishnamurti, Janet Kwiatkowski, Lyndsay Molinari, Elizabeth Stenger, Michael Jaskolka, Qifeng Yu, Nnenna Badamosi, Brieana Cox-Buckley, Baisong Mei, Olubunmi Afonja, Mark Walters
Journal: Blood
Blood (2025) 146 (Supplement 1): 4314.
https://doi.org/10.1182/blood-2025-4314
Published: 2025
Journal Articles

Durable Clinical Benefits with Exagamglogene Autotemcel for Severe Sickle Cell Disease

Free
Haydar Frangoul, Franco Locatelli, Akshay Sharma, Monica Bhatia, Markus Y Mapara, Robert I. Liem, Donna Wall, Lyndsay Molinari, Laurence Dedeken, Kevin H.M. Kuo, Paul Telfer, Ami J. Shah, Marina Cavazzana, Selim Corbacioglu, Michael J. Eckrich, Damiano Rondelli, Roland Meisel, Stephan Lobitz, Mariane De Montalembert, Martin H. Steinberg, Mark C. Walters, Laura Bower, Suzan Imren, Tina Liu, Weiyu Zhou, William Hobbs, Stephan A. Grupp
Journal: Blood
Blood (2024) 144 (Supplement 1): 4954.
https://doi.org/10.1182/blood-2024-204001
Published: 2024
Journal Articles

Exagamglogene Autotemcel for Severe Sickle Cell Disease

Free
Haydar Frangoul, Franco Locatelli, Akshay Sharma, Monica Bhatia, Markus Mapara, Lyndsay Molinari, Donna Wall, Robert I. Liem, Paul Telfer, Ami J. Shah, Marina Cavazzana, Selim Corbacioglu, Damiano Rondelli, Roland Meisel, Laurence Dedeken, Stephan Lobitz, Mariane de Montalembert, Martin H. Steinberg, Mark C. Walters, Laura Bower, Suzan Imren, Christopher Simard, Fengjuan Xuan, Weiyu Zhou, Phuong Khanh Morrow, William Hobbs, Stephan Grupp
Journal: Blood
Blood (2023) 142 (Supplement 1): 1052.
https://doi.org/10.1182/blood-2023-190139
Published: 2023
Journal Articles

Efficacy and Safety of a Single Dose of Exagamglogene Autotemcel for Severe Sickle Cell Disease

Free
Haydar Frangoul, Franco Locatelli, Monica Bhatia, Markus Y. Mapara, Lyndsay Molinari, Akshay Sharma, Stephan Lobitz, Mariane de Montalembert, Damiano Rondelli, Martin Steinberg, Mark C. Walters, Suzan Imren, Lanju Zhang, Anjali Sharma, Yang Song, Christopher Simard, William Hobbs, Stephen Grupp
Journal: Blood
Blood (2022) 140 (Supplement 1): 29–31.
https://doi.org/10.1182/blood-2022-162353
Published: 2022