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Michael S. Hershfield
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Journal Articles

Outcomes following treatment for ADA-deficient severe combined immunodeficiency: a report from the PIDTC

CME Clinical Trials & Observations
Geoffrey D. E. Cuvelier, Brent R. Logan, Susan E. Prockop, Rebecca H. Buckley, Caroline Y. Kuo, Linda M. Griffith, Xuerong Liu, Alison Yip, Michael S. Hershfield, Paul G. Ayoub, Theodore B. Moore, Morna J. Dorsey, Richard J. O’Reilly, Neena Kapoor, Sung-Yun Pai, Malika Kapadia, Christen L. Ebens, Lisa R. Forbes Satter, Lauri M. Burroughs, Aleksandra Petrovic, Deepak Chellapandian, Jennifer Heimall, David C. Shyr, Ahmad Rayes, Jeffrey J. Bednarski, Sharat Chandra, Shanmuganathan Chandrakasan, Alfred P. Gillio, Lisa Madden, Troy C. Quigg, Emi H. Caywood, Blachy J. Dávila Saldaña, Kenneth DeSantes, Hesham Eissa, Frederick D. Goldman, Jacob Rozmus, Ami J. Shah, Mark T. Vander Lugt, Monica S. Thakar, Roberta E. Parrott, Caridad Martinez, Jennifer W. Leiding, Troy R. Torgerson, Michael A. Pulsipher, Luigi D. Notarangelo, Morton J. Cowan, Christopher C. Dvorak, Elie Haddad, Jennifer M. Puck, Donald B. Kohn
Journal: Blood
Blood (2022) 140 (7): 685–705.
https://doi.org/10.1182/blood.2022016196
Published: 2022
Includes: Supplemental data
Journal Articles

Long-term outcomes after gene therapy for adenosine deaminase severe combined immune deficiency

Clinical Trials & Observations
Bryanna Reinhardt, Omar Habib, Kit L. Shaw, Elizabeth Garabedian, Denise A. Carbonaro-Sarracino, Dayna Terrazas, Beatriz Campo Fernandez, Satiro De Oliveira, Theodore B. Moore, Alan K. Ikeda, Barbara C. Engel, Gregory M. Podsakoff, Roger P. Hollis, Augustine Fernandes, Connie Jackson, Sally Shupien, Suparna Mishra, Alejandra Davila, Jack Mottahedeh, Andrej Vitomirov, Wenzhao Meng, Aaron M. Rosenfeld, Aoife M. Roche, Pascha Hokama, Shantan Reddy, John Everett, Xiaoyan Wang, Eline T. Luning Prak, Kenneth Cornetta, Michael S. Hershfield, Robert Sokolic, Suk See De Ravin, Harry L. Malech, Frederic D. Bushman, Fabio Candotti, Donald B. Kohn
Journal: Blood
Blood (2021) 138 (15): 1304–1316.
https://doi.org/10.1182/blood.2020010260
Published: 2021
Includes: Supplemental data
Journal Articles

Gene therapy for adenosine deaminase–deficient severe combined immune deficiency: clinical comparison of retroviral vectors and treatment plans

Clinical Trials & Observations
Fabio Candotti, Kit L. Shaw, Linda Muul, Denise Carbonaro, Robert Sokolic, Christopher Choi, Shepherd H. Schurman, Elizabeth Garabedian, Chimene Kesserwan, G. Jayashree Jagadeesh, Pei-Yu Fu, Eric Gschweng, Aaron Cooper, John F. Tisdale, Kenneth I. Weinberg, Gay M. Crooks, Neena Kapoor, Ami Shah, Hisham Abdel-Azim, Xiao-Jin Yu, Monika Smogorzewska, Alan S. Wayne, Howard M. Rosenblatt, Carla M. Davis, Celine Hanson, Radha G. Rishi, Xiaoyan Wang, David Gjertson, Otto O. Yang, Arumugam Balamurugan, Gerhard Bauer, Joanna A. Ireland, Barbara C. Engel, Gregory M. Podsakoff, Michael S. Hershfield, R. Michael Blaese, Robertson Parkman, Donald B. Kohn
Journal: Blood
Blood (2012) 120 (18): 3635–3646.
https://doi.org/10.1182/blood-2012-02-400937
Published: 2012
Includes: Supplemental data
Journal Articles

Myeloid dysplasia and bone marrow hypocellularity in adenosine deaminase-deficient severe combined immune deficiency

Clinical Trials & Observations
Robert Sokolic, Irina Maric, Chimene Kesserwan, Elizabeth Garabedian, I. Celine Hanson, Margaret Dodds, Rebecca Buckley, Andrew C. Issekutz, Naynesh Kamani, Kit Shaw, Ben Tan, Pawan Bali, Michael S. Hershfield, Donald B. Kohn, Alan S. Wayne, Fabio Candotti
Journal: Blood
Blood (2011) 118 (10): 2688–2694.
https://doi.org/10.1182/blood-2011-01-329359
Published: 2011
Journal Articles

How I treat ADA deficiency

H. Bobby Gaspar, Alessandro Aiuti, Fulvio Porta, Fabio Candotti, Michael S. Hershfield, Luigi D. Notarangelo
Journal: Blood
Blood (2009) 114 (17): 3524–3532.
https://doi.org/10.1182/blood-2009-06-189209
Published: 2009
Journal Articles

Patients with adenosine deaminase deficiency surviving after hematopoietic stem cell transplantation are at high risk of CNS complications

Clinical Trials & Observations
Manfred Hönig, Michael H. Albert, Ansgar Schulz, Monika Sparber-Sauer, Catharina Schütz, Bernd Belohradsky, Tayfun Güngör, Markus T. Rojewski, Harald Bode, Ulrich Pannicke, Dominique Lippold, Klaus Schwarz, Klaus-Michael Debatin, Michael S. Hershfield, Wilhelm Friedrich
Journal: Blood
Blood (2006) 109 (8): 3595–3602.
https://doi.org/10.1182/blood-2006-07-034678
Published: 2006
Journal Articles

Prolonged pancytopenia in a gene therapy patient with ADA-deficient SCID and trisomy 8 mosaicism: a case report

Brief Report
Barbara C. Engel, Greg M. Podsakoff, Joanna L. Ireland, E. Monika Smogorzewska, Denise A. Carbonaro, Kathy Wilson, Ami Shah, Neena Kapoor, Mirna Sweeney, Mark Borchert, Gay M. Crooks, Kenneth I. Weinberg, Robertson Parkman, Howard M. Rosenblatt, Shi-Qi Wu, Michael S. Hershfield, Fabio Candotti, Donald B. Kohn
Journal: Blood
Blood (2006) 109 (2): 503–506.
https://doi.org/10.1182/blood-2006-06-031476
Published: 2006
Journal Articles

Adenosine deaminase deficiency with mosaicism for a “second-site suppressor” of a splicing mutation: decline in revertant T lymphocytes during enzyme replacement therapy

Francisco X. Arredondo-Vega, Ines Santisteban, Eva Richard, Pawan Bali, Majed Koleilat, Michael Loubser, Abdulaziz Al-Ghonaium, Mariam Al-Helali, Michael S. Hershfield
Journal: Blood
Blood (2002) 99 (3): 1005–1013.
https://doi.org/10.1182/blood.V99.3.1005
Published: 2002
Journal Articles

T-cell lines from 2 patients with adenosine deaminase (ADA) deficiency showed the restoration of ADA activity resulted from the reversion of an inherited mutation

Brief Report
Tadashi Ariga, Noriko Oda, Koji Yamaguchi, Nobuaki Kawamura, Hideaki Kikuta, Shoichiro Taniuchi, Yohnosuke Kobayashi, Kihei Terada, Hisami Ikeda, Michael S. Hershfield, Kunihiko Kobayashi, Yukio Sakiyama
Journal: Blood
Blood (2001) 97 (9): 2896–2899.
https://doi.org/10.1182/blood.V97.9.2896
Published: 2001
Journal Articles

Full hematopoietic engraftment after allogeneic bone marrow transplantation without cytoreduction in a child with severe combined immunodeficiency

Clinical Trials & Observations Brief Report
Ronald J. Rubocki, Jennifer R. Parsa, Michael S. Hershfield, Warren G. Sanger, Samuel J. Pirruccello, Ines Santisteban, Bruce G. Gordon, Sarah E. Strandjord, Phyllis I. Warkentin, Peter F. Coccia
Journal: Blood
Blood (2001) 97 (3): 809–811.
https://doi.org/10.1182/blood.V97.3.809
Published: 2001
Journal Articles

Adenosine Deaminase Deficiency in Adults

Hulya Ozsahin, Francisco X. Arredondo-Vega, Ines Santisteban, Hanspeter Fuhrer, Peter Tuchschmid, Wolfram Jochum, Adriano Aguzzi, Howard M. Lederman, Amy Fleischman, Jerry A. Winkelstein, Reinhard A. Seger, Michael S. Hershfield
Journal: Blood
Blood (1997) 89 (8): 2849–2855.
https://doi.org/10.1182/blood.V89.8.2849
Published: 1997