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Journal Articles

Lentiviral gene therapy for X-linked chronic granulomatous disease recapitulates endogenous CYBB regulation and expression

Ryan L. Wong, Sarah Sackey, Devin Brown, Shantha Senadheera, Katelyn Masiuk, Jason P. Quintos, Nicole Colindres, Luke Riggan, Richard A. Morgan, Harry L. Malech, Roger P. Hollis, Donald B. Kohn

Blood (2023) 141 (9): 1007–1022.

https://doi.org/10.1182/blood.2022016074

Published: 2023

Includes: Supplemental data

Journal Articles

Long-term outcomes after gene therapy for adenosine deaminase severe combined immune deficiency

Blood (2021) 138 (15): 1304–1316.

https://doi.org/10.1182/blood.2020010260

Published: 2021

Includes: Supplemental data

Journal Articles

Investigating Zeta Globin Gene Expression to Develop a Potential Therapy for Alpha Thalassemia Major

Georgia L. Gregory, BS, Beeke Wienert, PhD, Marisa Schwab, MD, Billie Rachael Lianoglou, MS, Roger P. Hollis, PhD, Donald B. Kohn, MD, Bruce R. Conklin, MD, Tippi C. MacKenzie, MD

Blood (2020) 136 (Supplement 1): 3–4.

https://doi.org/10.1182/blood-2020-142922

Published: 2020

Journal Articles

Lentiviral Gene Therapy with Autologous Hematopoietic Stem and Progenitor Cells (HSPCs) for the Treatment of Severe Combined Immune Deficiency Due to Adenosine Deaminase Deficiency (ADA-SCID): Results in an Expanded Cohort

Blood (2019) 134 (Supplement_1): 3345.

https://doi.org/10.1182/blood-2019-123432

Published: 2019

Journal Articles

Development of a Treg Lineage Specific Lentiviral Vector for the Treatment of IPEX Syndrome

Katelyn E Masiuk, BS, Jennifer Laborada, BS, Roger P Hollis, PhD, Donald B Kohn, MD

Blood (2017) 130 (Supplement 1): 528.

https://doi.org/10.1182/blood.V130.Suppl_1.528.528

Published: 2017

Journal Articles

Enrichment of Hematopoietic Stem Cells Using Immunomagnetic Beads to Facilitate Gene Therapy

Katelyn E Masiuk, BS, Devin Brown, BA, Fabrizia Urbinati, PhD, Roger P Hollis, PhD, Donald B Kohn

Blood (2016) 128 (22): 2313.

https://doi.org/10.1182/blood.V128.22.2313.2313

Published: 2016

Journal Articles

Preservation of Gene Edited Hematopoietic Stem Cells By Transient Overexpression of BCL-2 mRNA

Carmen Flores Bjurström, PhD, Michelle Mojadidi, MSc, Anastasia Lomova, BS, Stephen Lai, Sorel Fitz-Gibbon, PhD, Matteo Pellegrini, PhD, Aaron R Cooper, PhD, Georgia R Lill, MSc, Michael Kaufman, MSc, Gregory J Cost, PhD, Michael C. Holmes, PhD, Roger P Hollis, PhD, Donald B Kohn

Blood (2016) 128 (22): 3636.

https://doi.org/10.1182/blood.V128.22.3636.3636

Published: 2016

Journal Articles

Correction of the sickle cell disease mutation in human hematopoietic stem/progenitor cells

Blood (2015) 125 (17): 2597–2604.

https://doi.org/10.1182/blood-2014-12-615948

Published: 2015

Includes: Supplemental data

Journal Articles

Systematic Comparison of the EF-1 Alpha Short (EFS) and Viral Promoters for Gene Modification of Human Primary Cells for Clinical Applications

Roy L. Kao, MD, Eric H. Gschweng, BS, Avigael Rebecca Lerman, Sarah M. Larson, MD, Andy Tu, Tulika Tyagi, MS, Shantha Senadheera, MS, Roger P. Hollis, PhD, Satiro N. De Oliveira, MD

Blood (2014) 124 (21): 3497.

https://doi.org/10.1182/blood.V124.21.3497.3497

Published: 2014

Journal Articles

Second-Generation Chimeric Antigen Receptors Successfully Modify Hematopoietic Stem Cells for Immunotherapy of B-Lineage Malignancies

Roy L. Kao, MD, Tulika Tyagi, MS, Sarah M. Larson, MD, Andy Tu, Shantha Senadheera, MS, Roger P. Hollis, PhD, Satiro N. De Oliveira, MD

Blood (2014) 124 (21): 655.

https://doi.org/10.1182/blood.V124.21.655.655

Published: 2014

Journal Articles

Envelope, please. And the award goes to…

Donald B. Kohn, Roger P. Hollis

Blood (2014) 124 (8): 1203–1204.

https://doi.org/10.1182/blood-2014-06-583823

Published: 2014

Journal Articles

A Pre-Clinical Model Of Hematopoietic Stem Cell Based Immunotherapy For Cancer Utilizing The NY-ESO-1 T-Cell Receptor and sr39TK PET Reporter / Suicide Gene

Eric H. Gschweng, BS, Melissa N. McCracken, BS, Thinle Chodon, MD, PhD, Richard C Koya, MD, PhD, Michael L Kaufman, MS, Michelle Ho, BS, Navdeep Saini, Roger P. Hollis, PhD, Antoni Ribas, MD, PhD, Satiro N. De Oliveira, MD, Owen N. Witte, MD, Donald B. Kohn, MD

Blood (2013) 122 (21): 2020.

https://doi.org/10.1182/blood.V122.21.2020.2020

Published: 2013

Journal Articles

Zinc Finger Nucleases Targeting The β-Globin Locus Drive Efficient Correction Of The Sickle Mutation In CD34 + Cells

Megan D Hoban, BS, Alok V Joglekar, PhD, David Gray, BS, Michael L Kaufman, MS, Fabrizia Urbinati, PhD, Shantha Senadheera, MS, Gregory Cost, PhD, Andreas Reik, PhD, Michael C. Holmes, PhD, Philip D Gregory, PhD, Roger P. Hollis, PhD, Donald B. Kohn, MD

Blood (2013) 122 (21): 2904.

https://doi.org/10.1182/blood.V122.21.2904.2904

Published: 2013

Journal Articles

Inducing Definitive Erythropoiesis From Human Embryonic Stem Cells Through a Novel Intracellular MPL Dimerization Strategy

William Sang Kim, B.S., Yuhua Zhu, B.S., Qiming Deng, B.S., Amanda J. Grieco, B.S., Gautam G. Dravid, Ph.D, Chintan Parekh, MBBS, Roger P. Hollis, PhD, Timothy Lane, Ph.D, Eric E. Bouhassira, PhD, Donald B. Kohn, MD, Gay M. Crooks, MBBS

Blood (2013) 122 (21): 1172.

https://doi.org/10.1182/blood.V122.21.1172.1172

Published: 2013

Journal Articles

Anti-CD117 (c-Kit) Monoclonal Antibodies Deplete Human Hematopoietic Stem Cells and Facilitate Their Replacement in Humanized NOD/SCID/IL2Rγ −/− Mice: A Non-Toxic Conditioning Regimen for Allotransplantation

Aaron C. Logan, MD, PhD, Agnieszka Czechowicz, MD, PhD, Benjamin V. Kelley, BS, Theingi M. Thway, PhD, Ivan Magana, Mark R. Krampf, MS, Jessica Poyser, Roger P. Hollis, PhD, Donald B. Kohn, MD, Irving L. Weissman, MD, Judith A. Shizuru, MD, PhD

Blood (2012) 120 (21): 4099.

https://doi.org/10.1182/blood.V120.21.4099.4099

Published: 2012

Journal Articles

Efficient Erythropoiesis From Human Embryonic Stem Cells Through Dimerization of Intracellular MPL.

William Sang Kim, B.S., Gautam G. Dravid, Ph.D, Yuhua Zhu, B.S., Chintan Parekh, MBBS, Qiming Deng, B.S., Roger P. Hollis, PhD, Timothy Lane, Ph.D, Donald B. Kohn, MD, Gay M. Crooks, MBBS

Blood (2012) 120 (21): 2291.

https://doi.org/10.1182/blood.V120.21.2291.2291

Published: 2012

Journal Articles

Preclinical Studies for Sickle Cell Disease Gene Therapy Using Bone Marrow CD34+ Cells Modified with a βAS3-Globin Lentiviral Vector

Fabrizia Urbinati, Ph.D, Zulema Romero Garcia, Ph.D, Sabine Geiger, Rafael Ruiz de Assin, Ph.D, Gabriela Kuftinec, Roger P. Hollis, PhD, Satiro N. De Oliveira, MD, Jennifer Wherley, Aaron Cooper, Tim M. Townes, PhD, Gay M. Crooks, MBBS, Elizabeth J Read, MD, Mark C. Walters, MD, Herbert J. Meiselman, ScD, Thomas D. Coates, MD, Victor J. Marder, M.D., Donald B. Kohn, MD

Blood (2011) 118 (21): 3119.

https://doi.org/10.1182/blood.V118.21.3119.3119

Published: 2011

Journal Articles

CD19 Fc-Fusion Protein for Detection of Cells Expressing Anti-CD19 Chimeric Antigen Receptors.

Satiro N. De Oliveira, MD, Jiexin Wang, MD, Roger P. Hollis, PhD, Donald B. Kohn, MD

Blood (2010) 116 (21): 3756.

https://doi.org/10.1182/blood.V116.21.3756.3756

Published: 2010

Journal Articles

Optimization of the Sleeping Beauty Transposon System to Achieve Stable Transgene Expression in Human CD34+ Hematopoietic Progenitor Cells

Teiko Sumiyoshi, MS, Roger P Hollis, PhD, Nathalia Holt, MS, Donald B. Kohn, MD

Blood (2008) 112 (11): 3527.

https://doi.org/10.1182/blood.V112.11.3527.3527

Published: 2008

NARROW

Lentiviral gene therapy for X-linked chronic granulomatous disease recapitulates endogenous CYBB regulation and expression

Long-term outcomes after gene therapy for adenosine deaminase severe combined immune deficiency

Investigating Zeta Globin Gene Expression to Develop a Potential Therapy for Alpha Thalassemia Major

Lentiviral Gene Therapy with Autologous Hematopoietic Stem and Progenitor Cells (HSPCs) for the Treatment of Severe Combined Immune Deficiency Due to Adenosine Deaminase Deficiency (ADA-SCID): Results in an Expanded Cohort

Development of a Treg Lineage Specific Lentiviral Vector for the Treatment of IPEX Syndrome

Enrichment of Hematopoietic Stem Cells Using Immunomagnetic Beads to Facilitate Gene Therapy

Preservation of Gene Edited Hematopoietic Stem Cells By Transient Overexpression of BCL-2 mRNA

Correction of the sickle cell disease mutation in human hematopoietic stem/progenitor cells

Systematic Comparison of the EF-1 Alpha Short (EFS) and Viral Promoters for Gene Modification of Human Primary Cells for Clinical Applications

Second-Generation Chimeric Antigen Receptors Successfully Modify Hematopoietic Stem Cells for Immunotherapy of B-Lineage Malignancies

Envelope, please. And the award goes to…

A Pre-Clinical Model Of Hematopoietic Stem Cell Based Immunotherapy For Cancer Utilizing The NY-ESO-1 T-Cell Receptor and sr39TK PET Reporter / Suicide Gene

Zinc Finger Nucleases Targeting The β-Globin Locus Drive Efficient Correction Of The Sickle Mutation In CD34 + Cells

Inducing Definitive Erythropoiesis From Human Embryonic Stem Cells Through a Novel Intracellular MPL Dimerization Strategy

Anti-CD117 (c-Kit) Monoclonal Antibodies Deplete Human Hematopoietic Stem Cells and Facilitate Their Replacement in Humanized NOD/SCID/IL2Rγ −/− Mice: A Non-Toxic Conditioning Regimen for Allotransplantation

Efficient Erythropoiesis From Human Embryonic Stem Cells Through Dimerization of Intracellular MPL.

Preclinical Studies for Sickle Cell Disease Gene Therapy Using Bone Marrow CD34+ Cells Modified with a βAS3-Globin Lentiviral Vector

CD19 Fc-Fusion Protein for Detection of Cells Expressing Anti-CD19 Chimeric Antigen Receptors.

Optimization of the Sleeping Beauty Transposon System to Achieve Stable Transgene Expression in Human CD34+ Hematopoietic Progenitor Cells

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American Society of Hematology

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American Society of Hematology

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