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Katelyn Masiuk
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Journal Articles

Ex Vivo Lentiviral Hematopoietic Stem Cell (HSC) Gene Therapy May Represent a Curative Therapy for the Life-Threatening Inborn Error of Immunity Severe Combined Immunodeficiency Due to Adenosine Deaminase (ADA) Deficiency (ADA-SCID)

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Katelyn Masiuk, Jinhua Xu-Bayford, Augustine Fernandes, Konstantinos Vazouras, Danilo Pellin, Havinder Hara, Sohini Roy, Beatriz Campo Fernandez, Thao Thai Dang, Kimberly Gilmour, Elena Alvarez Mediavilla, Beatrice Curio-Penny, Gráinne O'Toole, Rima Ahmed, Jordyn Arnold, Elizabeth Garabedian, Harry L Malech, Kenneth Cornetta, Claire Booth, Donald B. Kohn
Journal: Blood
Blood (2024) 144 (Supplement 1): 1051.
https://doi.org/10.1182/blood-2024-202543
Published: 2024
Journal Articles

Lentiviral gene therapy for X-linked chronic granulomatous disease recapitulates endogenous CYBB regulation and expression

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Ryan L. Wong, Sarah Sackey, Devin Brown, Shantha Senadheera, Katelyn Masiuk, Jason P. Quintos, Nicole Colindres, Luke Riggan, Richard A. Morgan, Harry L. Malech, Roger P. Hollis, Donald B. Kohn
Journal: Blood
Blood (2023) 141 (9): 1007–1022.
https://doi.org/10.1182/blood.2022016074
Published: 2023
Includes: Supplemental data