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Jeffrey C. Miller
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Journal Articles

A Potential Therapy for Beta-Thalassemia (ST-400) and Sickle Cell Disease (BIVV003)

Michael C. Holmes, PhD, Andreas Reik, PhD, Edward J. Rebar, PhD BS, Jeffrey C. Miller, PhD, Yuanyue Zhou, Lei Zhang, PhD, Patrick Li, Sagar Vaidya
Journal: Blood
Blood (2017) 130 (Supplement 1): 2066.
https://doi.org/10.1182/blood.V130.Suppl_1.2066.2066
Published: 2017
Journal Articles

In vivo genome editing of the albumin locus as a platform for protein replacement therapy

Rajiv Sharma, Xavier M. Anguela, Yannick Doyon, Thomas Wechsler, Russell C. DeKelver, Scott Sproul, David E. Paschon, Jeffrey C. Miller, Robert J. Davidson, David Shivak, Shangzhen Zhou, Julianne Rieders, Philip D. Gregory, Michael C. Holmes, Edward J. Rebar, Katherine A. High
Journal: Blood
Blood (2015) 126 (15): 1777–1784.
https://doi.org/10.1182/blood-2014-12-615492
Published: 2015
Includes: Supplemental data
Journal Articles

Targeted Gene Modification In Hematopoietic Stem Cells: A Potential Treatment For Thalassemia and Sickle Cell Anemia

Andreas Reik, PhD, Kai-Hsin Chang, PhD, Sandra Stehling-Sun, PhD, Yuanyue Zhou, Gary K Lee, PhD, Lynn Truong, Travis Wood, Ziying Zhang, Albert Luong, Andy Chan, Pei-Qi Liu, PhD, Jeffrey C Miller, PhD, David E Paschon, PhD, Dmitry Y Guschin, PhD, Lei Zhang, PhD, Evangelia Yannaki, MD, Martin A Giedlin, PhD, Edward J Rebar, PhD, Philip D Gregory, PhD, Fyodor D Urnov, PHD, Thalia Papayannopoulou, MD, George Stamatoyannopoulos, MD, DSci
Journal: Blood
Blood (2013) 122 (21): 434.
https://doi.org/10.1182/blood.V122.21.434.434
Published: 2013
Journal Articles

Robust ZFN-mediated genome editing in adult hemophilic mice

Brief Report
Xavier M. Anguela, Rajiv Sharma, Yannick Doyon, Jeffrey C. Miller, Hojun Li, Virginia Haurigot, Michelle E. Rohde, Sunnie Y. Wong, Robert J. Davidson, Shangzhen Zhou, Philip D. Gregory, Michael C. Holmes, Katherine A. High
Journal: Blood
Blood (2013) 122 (19): 3283–3287.
https://doi.org/10.1182/blood-2013-04-497354
Published: 2013
Includes: Supplemental data
Journal Articles

Toward eliminating HLA class I expression to generate universal cells from allogeneic donors

Hiroki Torikai, Andreas Reik, Frank Soldner, Edus H. Warren, Carrie Yuen, Yuanyue Zhou, Denise L. Crossland, Helen Huls, Nicholas Littman, Ziying Zhang, Scott S. Tykodi, Partow Kebriaei, Dean A. Lee, Jeffrey C. Miller, Edward J. Rebar, Michael C. Holmes, Rudolf Jaenisch, Richard E. Champlin, Philip D. Gregory, Laurence J. N. Cooper
Journal: Blood
Blood (2013) 122 (8): 1341–1349.
https://doi.org/10.1182/blood-2013-03-478255
Published: 2013
Includes: Supplemental data
Journal Articles

A foundation for universal T-cell based immunotherapy: T cells engineered to express a CD19-specific chimeric-antigen-receptor and eliminate expression of endogenous TCR

Hiroki Torikai, Andreas Reik, Pei-Qi Liu, Yuanyue Zhou, Ling Zhang, Sourindra Maiti, Helen Huls, Jeffrey C. Miller, Partow Kebriaei, Brian Rabinovitch, Dean A. Lee, Richard E. Champlin, Chiara Bonini, Luigi Naldini, Edward J. Rebar, Philip D. Gregory, Michael C. Holmes, Laurence J. N. Cooper
Journal: Blood
Blood (2012) 119 (24): 5697–5705.
https://doi.org/10.1182/blood-2012-01-405365
Published: 2012
Includes: Supplemental data
Journal Articles

“Designer” Cells for Cellular Immunotherapy: Zinc Finger Nuclease (ZFN) Stimulated Targeted Recombination for the Simultaneous Disruption of the Endogenous Glucocorticoid Receptor and Site-Specific Addition of the IL13-Zetakine.

Andreas Reik, PhD, Michael C. Holmes, Ph.D., Fyodor D. Urnov, Ph.D., Yuanyue Zhou, Matthew Mendel, Pei-Qi Liu, Ph.D., Erica Moehle, Edward J. Rebar, Ph.D., Jeffrey C. Miller, Ph.D., Dale Ando, M.D., Philip D. Gregory, Ph.D., Michael Jensen, M.D.
Journal: Blood
Blood (2006) 108 (11): 3705.
https://doi.org/10.1182/blood.V108.11.3705.3705
Published: 2006