1-12 of 12
Daniel P. Dever
Close
Save search
Follow your search
Access your saved searches in your account
Would you like to receive an alert when new items match your search?
Close Modal
Sort by
Journal Articles

Development of a β-Globin Gene Replacement Strategy As a β-Thalassemia Therapy

Kirby Wallace, Beeke Wienert, Christopher Bandoro, James Partridge, Craig L. Ennis, Casey D. Lalisan, Kristina Krassovsky, Gaia Andreoletti, Rajiv Sharma, Aishwarya Churi, William M. Matern, Sebastian Treusch, Jane Grogan, Daniel P. Dever
Journal: Blood
Blood (2022) 140 (Supplement 1): 12985–12986.
https://doi.org/10.1182/blood-2022-167676
Published: 2022
Journal Articles

Cedar Trial in Progress: A First in Human, Phase 1/2 Study of the Correction of a Single Nucleotide Mutation in Autologous HSCs (GPH101) to Convert HbS to HbA for Treating Severe SCD

Julie Kanter, John F. DiPersio, Patrick Leavey, David C. Shyr, Alexis A Thompson, Matthew H. Porteus, Allison Intondi, Premanjali Lahiri, Daniel P. Dever, Alexandria Petrusich, Joshua Lehrer-Graiwer
Journal: Blood
Blood (2021) 138 (Supplement 1): 1864.
https://doi.org/10.1182/blood-2021-152892
Published: 2021
Journal Articles

Reticular Dysgenesis-Associated Adenylate Kinase 2 Deficiency Impairs Purine Metabolism and Ribosomal Biogenesis during Myelopoiesis

Wenqing Wang, Andrew Devilbiss, Martin Arreola, Thomas Mathews, Misty Martin-Sandoval, Zhiyu Zhao, Avni Awani, Daniel P. Dever, Matthew H. Porteus, Sean Morrison, Katja G Weinacht
Journal: Blood
Blood (2021) 138 (Supplement 1): 3257.
https://doi.org/10.1182/blood-2021-151919
Published: 2021
Journal Articles

Correction of the Energetic Defects in Pyruvate Kinase Deficiency through Genome Editing in Hematopoietic Stem and Progenitor Cells

Sara Fañanas-Baquero, Oscar Quintana Bustamante, PhD, Daniel P. Dever, PhD, Omaira Alberquilla, Rebeca Sanchez-Dominguez, PhD, Joab Camarena, BS, Rolf Turk, José Luis López Lorenzo, MD, Paola Bianchi, BSc, PhD, Mark Behlke, MD PhD, Juan A Bueren, PhD, Matt Porteus, MD PhD, José C Segovia, PhD
Journal: Blood
Blood (2020) 136 (Supplement 1): 29.
https://doi.org/10.1182/blood-2020-139117
Published: 2020
Journal Articles

Reticular Dysgenesis-Associated Adenylate Kinase 2 Deficiency Impairs Hematopoietic Stem and Progenitor Cell Function through Reductive Stress

Wenqing Wang, PhD, Andrew Devilbiss, PhD, Thomas Mathews, PhD, Martin Arreola, Misty Martin, Zhiyu Zhao, DPhil, Avni Awani, PhD, Daniel P. Dever, PhD, Matthew H. Porteus, MD PhD, Sean Morrison, PhD, Katja G Weinacht, MD PhD
Journal: Blood
Blood (2020) 136 (Supplement 1): 33.
https://doi.org/10.1182/blood-2020-138560
Published: 2020
Journal Articles

Adenylate Kinase 2 Links Energy Metabolism and Cell Fate in Hematopoietic Stem and Progenitor Cells

Wenqing Wang, PhD, Avni Awani, PhD, Andrew Devilbiss, PhD, Thomas Mathews, PhD, Daniel Thomas, MD PhD, Daniel P. Dever, PhD, Matthew Porteus, MD PhD, Sean Morrison, PhD, Katja G Weinacht, MD PhD
Journal: Blood
Blood (2019) 134 (Supplement_1): 3705.
https://doi.org/10.1182/blood-2019-129424
Published: 2019
Journal Articles

Highly Efficient Editing of the Beta-Globin Gene in Patient Derived Hematopoietic Stem and Progenitor Cells to Treat Sickle Cell Disease

So Hyun Park, BS, Ciaran M Lee, PhD, Daniel P. Dever, PhD, Timothy H Davis, BS, Joab Camarena, BS, Yankai Zhang, PhD, Matthew Porteus, MD PhD, Vivian A Sheehan, MD PhD, Gang Bao, PhD
Journal: Blood
Blood (2018) 132 (Supplement 1): 2192.
https://doi.org/10.1182/blood-2018-99-117371
Published: 2018
Journal Articles

Pharmacological Inhibition of Nlk (Nemo-like Kinase) Rescues Erythropoietic Defects in Pre-Clinical Models of Diamond Blackfan Anemia

Mark C Wilkes, Jun Chen, MD PhD, Kavitha Siva, PhD, Gianluca Veretti, PhD, Daniel P. Dever, PhD, Minyoung Youn, PhD, Hee-Don Chae, PhD, Jacqueline D Mercado, Mallika Saxena, Anupama Narla, MD, Bertil Glader, MD, Matthew Porteus, MD PhD, Claire E Repellin, PhD, Hanna T Gazda, MD PhD, Manuel Serrano, PhD, Johan Flygare, MD PhD, Kathleen M. Sakamoto, MD PhD
Journal: Blood
Blood (2018) 132 (Supplement 1): 754.
https://doi.org/10.1182/blood-2018-99-119954
Published: 2018
Journal Articles

An Engineered Cell-Traceable Model of Reticular Dysgenesis in Human Hematopoietic Stem Cells Linking Metabolism and Differentiation

Wenqing Wang, PhD, Avni Awani, PhD, Lauren Reich, Yusuke Nakauchi, MD PhD, Daniel Thomas, MD PhD, Daniel P. Dever, PhD, Matthew Porteus, MD PhD, Katja G. Weinacht, MD PhD
Journal: Blood
Blood (2018) 132 (Supplement 1): 2558.
https://doi.org/10.1182/blood-2018-99-117926
Published: 2018
Journal Articles

Efficient CRISPR/Cas9-Mediated Gene Editing of Pklr in Human Hematopoietic Progenitors and Stem Cells for the Gene Therapy of Pyruvate Kinase Deficiency

Oscar Quintana Bustamante, PhD, Sara Fañanas-Baquero, Daniel P. Dever, PhD, Alberquilla Omaira, Joab Camarena, BS, Rebeca Sanchez-Dominguez, PhD, Matias Morin, Val Fernandez, Miguel Angel Moreno-Pelayo, Juan A. Bueren, PhD, Matthew Porteus, MD PhD, Jose C Segovia, PhD
Journal: Blood
Blood (2018) 132 (Supplement 1): 5792.
https://doi.org/10.1182/blood-2018-99-111772
Published: 2018
Journal Articles

Priming Human Hematopoietic Stem and Progenitor Cells for Cas9/Sgrna and rAAV6-Mediated Homologous Recombination

Joab Camarena, BS, Carsten T Charlesworth, BS, Michael Kyle Cromer, BS, MPhil, PhD, Sriram Vaidyanathan, PhD, Rasmus O Bak, PhD, Jason Carte, PhD, Jason Potter, PhD, Daniel P. Dever, PhD, Matthew Porteus, MD PhD
Journal: Blood
Blood (2017) 130 (Supplement 1): 3342.
https://doi.org/10.1182/blood.V130.Suppl_1.3342.3342
Published: 2017
Journal Articles

Preclinical Development of HBB Gene Correction in Autologous Hematopoietic Stem and Progenitor Cells to Treat Severe Sickle Cell Disease

Daniel P. Dever, PhD, Joab Camarena, BS, Ciaran Lee, PhD, Christopher Vakulskas, PhD, Mark Behlke, MD PhD, Gang Bao, PhD, Matthew Porteus, MD PhD
Journal: Blood
Blood (2017) 130 (Supplement 1): 4620.
https://doi.org/10.1182/blood.V130.Suppl_1.4620.4620
Published: 2017