1-4 of 4
Boya Liu
Close
Save search
Follow your search
Access your saved searches in your account
Would you like to receive an alert when new items match your search?
Close Modal
Sort by
Journal Articles

Long-term follow-up of the first in human post-transcriptional genetic silencing of BCL11A in sickle cell disease in a phase 1 pilot and feasibility trial

Free
Erica Esrick, Leslie Lehmann, Amy Federico, Heather Daley, Colleen Dansereau, Satiro DeOliveira, John Everett, Pei-Chi Kao, Boya Liu, Theodore Moore, Emily Morris, Helene Negre, Kit Shaw, Gavin Roach, Jerome Ritz, Aoife Doto, Olivia Silva, Helene Vincon, Frederic Bushman, Donald Kohn, Akshat Jain, Wendy London, David Justus, Myriam Armant, John Manis, David Williams
Journal: Blood
Blood (2025) 146 (Supplement 1): 2533.
https://doi.org/10.1182/blood-2025-2533
Published: 2025
Journal Articles

Refined design of a CD117 antibody-drug conjugate safely and effectively conditions non-human primates for autologous transplant-based gene therapy

Free
Lev Gorfinkel, Boya Liu, Yi Liu, Madhura Panditrao, Sukhdeep Sahambi, Eric Peters, Sherif Sharaby, Sejong Chun, Victor Tkachev, Matthew Warren, Elisa Rojas Palato, Jennifer Lane, Ulrike Gerdemann, Francesca Alvarez Calderon, Leah Desrochers, Gwen Lavalla, Owen Stanbro, Lorenzo Cagnin, Serena De Vita, David Williams, Susan Cellitti, Leslie Kean
Journal: Blood
Blood (2025) 146 (Supplement 1): 5871.
https://doi.org/10.1182/blood-2025-5871
Published: 2025
Journal Articles

UM171 Enhances Fitness and Engraftment of Gene Modified Hematopoietic Stem Cells from Sickle Cells Disease Patients

Free
Boya Liu, Denise Klatt, Yu Zhou, John Manis, Guy Sauvageau, Christian Brendel, David A. Williams
Journal: Blood
Blood (2023) 142 (Supplement 1): 18.
https://doi.org/10.1182/blood-2023-182099
Published: 2023
Journal Articles

Combining the Anti-Sickling βAS3-Globin Gene with BCL11A and ZNF410 Double Shmirs for the Treatment of Sickle Cell Disease

Free
Boya Liu, Kevyn Hart, Christian Brendel, Donald B. Kohn, David A. Williams
Journal: Blood
Blood (2022) 140 (Supplement 1): 7786–7787.
https://doi.org/10.1182/blood-2022-163469
Published: 2022