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Journal Articles

Safety and Efficacy of Aru-1801 in Patients with Sickle Cell Disease: Early Results from the Phase 1/2 Momentum Study of a Modified Gamma Globin Gene Therapy and Reduced Intensity Conditioning

Michael Grimley, Monika Asnani, Archana Shrestha, Sydney Felker, Carolyn Lutzko, Paritha I. Arumugam, Scott Witting, Jennifer Knight-Madden, Omar Niss, Charles T. Quinn, Chris Lo, Courtney R. Little, Alisa Dong, Punam Malik

Blood (2021) 138 (Supplement 1): 3970.

https://doi.org/10.1182/blood-2021-147469

Published: 2021

Journal Articles

Early Results from a Phase 1/2 Study of Aru-1801 Gene Therapy for Sickle Cell Disease (SCD): Manufacturing Process Enhancements Improve Efficacy of a Modified Gamma Globin Lentivirus Vector and Reduced Intensity Conditioning Transplant

Michael Grimley, MD, Monika Asnani, PhD, Archana Shrestha, Sydney Felker, Carolyn Lutzko, PhD, Paritha I. Arumugam, PhD, Scott Witting, PhD, Jennifer Knight-Madden, MBBS, PhD, Omar Niss, MD, Charles T. Quinn, MD, Chris Lo, BS, Courtney R Little, BSN, Joseph W. McIntosh, MD, Punam Malik, MD

Blood (2020) 136 (Supplement 1): 20–21.

https://doi.org/10.1182/blood-2020-140963

Published: 2020

Journal Articles

Diminished Renal Pathology in a Mouse Model of Sickle Cell Anemia in Which Fibrinogen Binding to Mac-1 Is Inhibited

Md Nasimuzzaman, PhD, Paritha I. Arumugam, PhD, Eric S. Mullins, MD, Jeanne M James, MD, Katherine VandenHeuvel, MD, Marilou Narciso, BS, Maureen A. Shaw, MSc, Sarah McGraw, Bruce J. Aronow, PhD, Matthew J. Flick, PhD, Punam Malik, MD

Blood (2018) 132 (Supplement 1): 267.

https://doi.org/10.1182/blood-2018-99-112641

Published: 2018

Journal Articles

VPS4A : A Novel Candidate Gene for Congenital Dyserythropoietic Anemia

Katie Giger, PhD, Georgios E Christakopoulos, MD, Lisa Trump, Clarissa E. Johnson, MD, Haripriya Sakthivel, Mary Risinger, Omar Niss, MD, Kejian Zhang, MD MBA, Lionel Blanc, PhD, Robert B. Lorsbach, MD PhD, Paritha I. Arumugam, PhD, Carolyn Lutzko, PhD, Theodosia A. Kalfa, MD PhD

Blood (2017) 130 (Supplement 1): 923.

https://doi.org/10.1182/blood.V130.Suppl_1.923.923

Published: 2017

Journal Articles

Genetic diminution of circulating prothrombin ameliorates multiorgan pathologies in sickle cell disease mice

Paritha I. Arumugam, Eric S. Mullins, Shiva Kumar Shanmukhappa, Brett P. Monia, Anastacia Loberg, Maureen A. Shaw, Tilat Rizvi, Janaka Wansapura, Jay L. Degen, Punam Malik

Blood (2015) 126 (15): 1844–1855.

https://doi.org/10.1182/blood-2015-01-625707

Published: 2015

Includes: Supplemental data

Journal Articles

Elements of a Chromatin Insulator Necessary for Consistent, High-Level Globin Gene Expression

Paritha I. Arumugam, PhD, Ping Xia, MD, Fabrizia Urbinati, PhD, Punam Malik, MD

Blood (2007) 110 (11): 3731.

https://doi.org/10.1182/blood.V110.11.3731.3731

Published: 2007

Journal Articles

Self-Inactivating Lentiviral Vectors Flanked by a Chromatin Insulator Element Result in Increased, Consistent Expression of Human Beta Globin.

Paritha I. Arumugam, PhD, Jessica Scholes, Natalya Perelman, Alexander Zarzuela, Punam Malik, MD

Blood (2005) 106 (11): 527.

https://doi.org/10.1182/blood.V106.11.527.527

Published: 2005

NARROW

Safety and Efficacy of Aru-1801 in Patients with Sickle Cell Disease: Early Results from the Phase 1/2 Momentum Study of a Modified Gamma Globin Gene Therapy and Reduced Intensity Conditioning

Early Results from a Phase 1/2 Study of Aru-1801 Gene Therapy for Sickle Cell Disease (SCD): Manufacturing Process Enhancements Improve Efficacy of a Modified Gamma Globin Lentivirus Vector and Reduced Intensity Conditioning Transplant

Diminished Renal Pathology in a Mouse Model of Sickle Cell Anemia in Which Fibrinogen Binding to Mac-1 Is Inhibited

VPS4A : A Novel Candidate Gene for Congenital Dyserythropoietic Anemia

Genetic diminution of circulating prothrombin ameliorates multiorgan pathologies in sickle cell disease mice

Elements of a Chromatin Insulator Necessary for Consistent, High-Level Globin Gene Expression

Self-Inactivating Lentiviral Vectors Flanked by a Chromatin Insulator Element Result in Increased, Consistent Expression of Human Beta Globin.

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ASH Publications

American Society of Hematology

Safety and Efficacy of Aru-1801 in Patients with Sickle Cell Disease: Early Results from the Phase 1/2 Momentum Study of a Modified Gamma Globin Gene Therapy and Reduced Intensity Conditioning

Early Results from a Phase 1/2 Study of Aru-1801 Gene Therapy for Sickle Cell Disease (SCD): Manufacturing Process Enhancements Improve Efficacy of a Modified Gamma Globin Lentivirus Vector and Reduced Intensity Conditioning Transplant

Diminished Renal Pathology in a Mouse Model of Sickle Cell Anemia in Which Fibrinogen Binding to Mac-1 Is Inhibited

VPS4A : A Novel Candidate Gene for Congenital Dyserythropoietic Anemia

Genetic diminution of circulating prothrombin ameliorates multiorgan pathologies in sickle cell disease mice

Elements of a Chromatin Insulator Necessary for Consistent, High-Level Globin Gene Expression

Self-Inactivating Lentiviral Vectors Flanked by a Chromatin Insulator Element Result in Increased, Consistent Expression of Human Beta Globin.

Email alerts

ASH Publications

American Society of Hematology

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