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Francesca Ciotti
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Journal Articles

Lentiviral hematopoietic stem and progenitor cell gene therapy for Wiskott-Aldrich Syndrome: Early access experience in Italian patients based on 648/1996 law

Free
Sabina Cenciarelli, Stefania Giannelli, Federico Fraschetta, Carmen Caputo, Davide Sala, Ketty Sinigaglia, Mariam Datukishvili, Elena Tomasetto, Francesca Ciotti, Maddalena Fraschini, Federica Salerio, Camilla Ferri, Federica Barzaghi, Valeria Calbi, Daniele Canarutto, Giulia Consiglieri, Matteo Doglio, Francesca Fumagalli, Vera Gallo, Maddalena Migliavacca, Salvatore Recupero, Francesca Tucci, Maria Ester Bernardo, Maria Pia Cicalese, Federica Miotto, Alessandro Aiuti, Francesca Ferrua
Journal: Blood
Blood (2025) 146 (Supplement 1): 4312.
https://doi.org/10.1182/blood-2025-4312
Published: 2025
Journal Articles

Gene Therapy for Beta Thalassemia: Preliminary Results from the PHASE I/II Tiget-Bthal Trial of Autologous Hematopoietic Stem Cells Genetically Modified with GLOBE Lentiviral Vector

Free
Sarah Marktel, MD, Maria Pia Cicalese, Fabio Giglio, MD, Samantha Scaramuzza, Valeria Calbi, Miriam Casiraghi, Francesca Ciotti, Maria Rosa Lidonnici, Claudia Rossi, Nicoletta Masera, Emanuela D'Angelo, Nadia Mirra, Raffaella Origa, MD, Immacolata Tartaglione, Giacomo Mandelli, Raffaella Milani, Salvatore Gattillo, Milena Coppola, Gianluca Viarengo, Luca Santoleri, Andrea Calabria, Silverio Perrotta, Eugenio Montini, Giovanna Graziadei, MD, Luigi Naldini, MD PhD, Maria Domenica Cappellini, MD, Fabio Ciceri, MD, Alessandro Aiuti, Giuliana Ferrari
Journal: Blood
Blood (2017) 130 (Supplement 1): 355.
https://doi.org/10.1182/blood.V130.Suppl_1.355.355
Published: 2017