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    Ketty Sinigaglia
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    Journal Articles

    Lentiviral hematopoietic stem and progenitor cell gene therapy for Wiskott-Aldrich Syndrome: Early access experience in Italian patients based on 648/1996 law

    Free
    Sabina Cenciarelli, Stefania Giannelli, Federico Fraschetta, Carmen Caputo, Davide Sala, Ketty Sinigaglia, Mariam Datukishvili, Elena Tomasetto, Francesca Ciotti, Maddalena Fraschini, Federica Salerio, Camilla Ferri, Federica Barzaghi, Valeria Calbi, Daniele Canarutto, Giulia Consiglieri, Matteo Doglio, Francesca Fumagalli, Vera Gallo, Maddalena Migliavacca, Salvatore Recupero, Francesca Tucci, Maria Ester Bernardo, Maria Pia Cicalese, Federica Miotto, Alessandro Aiuti, Francesca Ferrua
    Journal: Blood
    Blood (2025) 146 (Supplement 1): 4312.
    https://doi.org/10.1182/blood-2025-4312
    Published: 2025

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