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Federica Barzaghi
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Journal Articles

Bone Marrow Impairment in Patients with Adenosine Deaminase 2 Deficiency

Maurizio Miano, Michela Lupia, Francesca Schena, Roberta Caorsi, Federica Barzaghi, Mariacarla Giarratana, Anna Corcione, Paola Terranova, Alessandro Aiuti, Alessandra Mortellaro, Alessia Cafaro, Elena Palmisani, Giuliana Cangemi, Sebastiano Barco, Gianluca Dell'Orso, Luca Arcuri, Alice Grossi, Elisabetta Traggiai, Isabella Ceccherini, Marco Gattorno, Carlo Dufour
Journal: Blood
Blood (2024) 144 (Supplement 1): 5396.
https://doi.org/10.1182/blood-2024-204733
Published: 2024
Journal Articles

Lentiviral-Mediated Gene Therapy for the Treatment of Adenosine Deaminase 2 Deficiency

Alessandra Mortellaro, Matteo Zoccolillo, Cristina Mesa Nuñez, Alessia Brix, Immacolata Brigida, Federica Barzaghi, Serena Scala, Raisa Jofra Hernández, Luca Basso-Ricci, Mariasilvia Colantuoni, Simone Cesaro, Francesca Conti, Andrea Pession, Fabio Benedetti, Marco Gattorno, Luigi Naldini, Maria Pia Cicalese, Anna Pistocchi, Alessandro Aiuti
Journal: Blood
Blood (2021) 138 (Supplement 1): 2937.
https://doi.org/10.1182/blood-2021-152127
Published: 2021
Journal Articles

Lentiviral Hematopoietic Stem and Progenitor Cell Gene Therapy for Wiskott-Aldrich Syndrome (WAS): Up to 8 Years of Follow up in 17 Subjects Treated Since 2010

Francesca Ferrua, MD PhD, Maria Pia Cicalese, MD PhD, Stefania Galimberti, PhD, Stefania Giannelli, PhD, Francesca Dionisio, MSc, Federica Barzaghi, MD PhD, Maddalena Migliavacca, MD PhD, Maria Ester Bernardo, MD PhD, Valeria Calbi, MD, Francesca Tucci, MD, Andrea A. Assanelli, MD, Jacopo Peccatori, MD, Elena Albertazzi, PhD, Alessandra G. Clerici, Federica A. Salerio, MSc, Serena Scala, PhD, Luca Basso-Ricci, MSc, Sabina Cenciarelli, MD, Daniele Canarutto, MD, Federico Fraschetta, RN, Antonella Bartoli, MScPharm, Hermann M. Wolf, MD, Paolo Silvani, MD, Salvatore Gattillo, MD, Milena Coppola, MD, Luca Santoleri, MD, Anna Villa, MD, Russell Jones, Chris Dott, PhD, Maria Grazia Valsecchi, PhD, Fabio Ciceri, MD, Luigi Naldini, MD PhD, Alessandro Aiuti, MD PhD
Journal: Blood
Blood (2019) 134 (Supplement_1): 3346.
https://doi.org/10.1182/blood-2019-124665
Published: 2019
Journal Articles

T-cell defects in patients with ARPC1B germline mutations account for combined immunodeficiency

Immacolata Brigida, Matteo Zoccolillo, Maria Pia Cicalese, Laurène Pfajfer, Federica Barzaghi, Serena Scala, Carmen Oleaga-Quintas, Jesus A. Álvarez-Álvarez, Lucia Sereni, Stefania Giannelli, Claudia Sartirana, Francesca Dionisio, Luca Pavesi, Marta Benavides-Nieto, Luca Basso-Ricci, Paola Capasso, Benedetta Mazzi, Jeremie Rosain, Nufar Marcus, Yu Nee Lee, Raz Somech, Massimo Degano, Giuseppe Raiola, Roberta Caorsi, Paolo Picco, Marcela Moncada Velez, Joelle Khourieh, Andrés Augusto Arias, Aziz Bousfiha, Thomas Issekutz, Andrew Issekutz, Bertrand Boisson, Kerry Dobbs, Anna Villa, Angelo Lombardo, Benedicte Neven, Despina Moshous, Jean-Laurent Casanova, José Luis Franco, Luigi D. Notarangelo, Cristina Scielzo, Stefano Volpi, Loïc Dupré, Jacinta Bustamante, Marco Gattorno, Alessandro Aiuti
Journal: Blood
Blood (2018) 132 (22): 2362–2374.
https://doi.org/10.1182/blood-2018-07-863431
Published: 2018
Includes: Supplemental data
Journal Articles

Update on the safety and efficacy of retroviral gene therapy for immunodeficiency due to adenosine deaminase deficiency

Maria Pia Cicalese, Francesca Ferrua, Laura Castagnaro, Roberta Pajno, Federica Barzaghi, Stefania Giannelli, Francesca Dionisio, Immacolata Brigida, Marco Bonopane, Miriam Casiraghi, Antonella Tabucchi, Filippo Carlucci, Eyal Grunebaum, Mehdi Adeli, Robbert G. Bredius, Jennifer M. Puck, Polina Stepensky, Ilhan Tezcan, Katie Rolfe, Erika De Boever, Rickey R. Reinhardt, Jonathan Appleby, Fabio Ciceri, Maria Grazia Roncarolo, Alessandro Aiuti
Journal: Blood
Blood (2016) 128 (1): 45–54.
https://doi.org/10.1182/blood-2016-01-688226
Published: 2016
Includes: Supplemental data
Journal Articles

In Vivo Tracking of T Cells in Humans Unveils Decade-Long Survival and Activity of Genetically Modified T Memory Stem Cells

Serena Scala, Luca Biasco, PhD, Luca Basso Ricci, Francesca Dionisio, Cristina Baricordi, Andrea Calabria, Stefania Giannelli, Nicoletta Cieri, MD PhD, Federica Barzaghi, Roberta Pajno, Hamoud Al-Mousa, Alessia Scarselli, Caterina Cancrini, Claudio Bordignon, MD, Maria Grazia Roncarolo, MD Prof., Eugenio Montini, Chiara Bonini, MD, Alessandro Aiuti, MD
Journal: Blood
Blood (2014) 124 (21): 547.
https://doi.org/10.1182/blood.V124.21.547.547
Published: 2014