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Emanuela Mrak
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Journal Articles

Gene therapy augments the efficacy of hematopoietic cell transplantation and fully corrects mucopolysaccharidosis type I phenotype in the mouse model

Ilaria Visigalli, Stefania Delai, Letterio S. Politi, Carmela Di Domenico, Federica Cerri, Emanuela Mrak, Raffaele D'Isa, Daniela Ungaro, Merel Stok, Francesca Sanvito, Elisabetta Mariani, Lidia Staszewsky, Claudia Godi, Ilaria Russo, Francesca Cecere, Ubaldo del Carro, Alessandro Rubinacci, Riccardo Brambilla, Angelo Quattrini, Paola Di Natale, Katherine Ponder, Luigi Naldini, Alessandra Biffi
Journal: Blood
Blood (2010) 116 (24): 5130–5139.
https://doi.org/10.1182/blood-2010-04-278234
Published: 2010
Includes: Supplemental data
Journal Articles

Bone marrow as an alternative site for islet transplantation

Elisa Cantarelli, Raffaella Melzi, Alessia Mercalli, Valeria Sordi, Giuliana Ferrari, Carsten Werner Lederer, Emanuela Mrak, Alessandro Rubinacci, Maurilio Ponzoni, Giovanni Sitia, Luca G. Guidotti, Ezio Bonifacio, Lorenzo Piemonti
Journal: Blood
Blood (2009) 114 (20): 4566–4574.
https://doi.org/10.1182/blood-2009-03-209973
Published: 2009
Includes: Supplemental data
Journal Articles

ADA-deficient SCID is associated with a specific microenvironment and bone phenotype characterized by RANKL/OPG imbalance and osteoblast insufficiency

Aisha V. Sauer, Emanuela Mrak, Raisa Jofra Hernandez, Elena Zacchi, Francesco Cavani, Miriam Casiraghi, Eyal Grunebaum, Chaim M. Roifman, Maria C. Cervi, Alessandro Ambrosi, Filippo Carlucci, Maria Grazia Roncarolo, Anna Villa, Alessandro Rubinacci, Alessandro Aiuti
Journal: Blood
Blood (2009) 114 (15): 3216–3226.
https://doi.org/10.1182/blood-2009-03-209221
Published: 2009
Includes: Supplemental data