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Suk See De Ravin, MD
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Journal Articles

Preclinical Evaluation for Engraftment of Gene-Edited CD34+ Cells with a Sickle Cell Disease Mutation in a Rhesus Transplantation Model

Naoya Uchida, MD, Linhong Li, PhD, Tina Nassehi, Morgan Yapundich, Jackson Gamer, Claire Drysdale, Juan J. Haro-Mora, PhD, Selami Demirci, PhD, Aylin Bonifacino, MS, Allen Krouse, Nathaniel S. Linde, Cornell Allen, MS, Suk See De Ravin, MD, PhD, Robert E. Donahue, VMD, Harry L. Malech, MD, Madhusudan Peshwa, PhD, John F. Tisdale, MD
Journal: Blood
Blood (2019) 134 (Supplement_1): 609.
https://doi.org/10.1182/blood-2019-122727
Published: 2019
Journal Articles

Enhanced Transduction Lentivector Gene Therapy for Treatment of Older Patients with X-Linked Severe Combined Immunodeficiency

Suk See De Ravin, MD, PhD, Sandra Anaya O'Brien, Nana Kwatemaa, RN, MSN, CCRP, Narda Theobald, BS, Siyuan Liu, Janet Lee, BS, Lela Kardava, Taylor Liu, Frederick Goldman, MDMS, Susan Moir, Jack Bleesing, MD PhD, Benedicte Neven, MD PhD, Jennifer Puck, MD, Morton J Cowan, MD, Ewelina Mamcarz, MD, Stephen Gottschalk, MD, Michael M Meagher, PhD, Luigi Notarangelo, MD, Elizabeth Kang, MD, Xiaolin Wu, PhD, Harry L. Malech, MD
Journal: Blood
Blood (2019) 134 (Supplement_1): 608.
https://doi.org/10.1182/blood-2019-127439
Published: 2019
Journal Articles

Lentiviral Gene Therapy with Low Dose Busulfan for Infants with X-SCID Results in the Development of a Functional Normal Immune System: Interim Results of an Ongoing Phase I/II Clinical Study

Ewelina Mamcarz, MD, Sheng Zhou, PhD, Timothy Lockey, PhD, Shannon Boi, PhD, Yan Koon-Kiu, PhD, Shane Cross, Pharm.D., Guolian Kang, PhD, Zhijun Ma, MD, Jose Marcos Condori, PhD, Jolanta Dowdy, M.S., Jean-Yves Metais, PhD, Deanna Langfitt, PhD, Brandon Triplett, MD, Chen Li, M.S., Xiwen Zhao, MSPH, Gabriela Maron, MD, Sneha Suresh, MD, Juan Carlos Aldave Becerra, MD, Joseph Church, MD, Elif Dokmeci, MD, James T Love, MD, PhD, Hedi van der Watt, MD, Ana C da Matta Ain, MD, Christa Krupski, DO, MPH, Jiyang Yu, PhD, Lance E. Palmer, PhD, William Janssen, PhD, Suk See De Ravin, MD, PhD, Mitchell J. Weiss, MD, PhD, Benjamin Youngblood, PhD, Janel R Long-Boyle, PharmD, PhD, Michael M Meagher, PhD, Harry L. Malech, MD, Jennifer Puck, MD, Morton J Cowan, MD, Stephen Gottschalk, MD
Journal: Blood
Blood (2019) 134 (Supplement_1): 2058.
https://doi.org/10.1182/blood-2019-126746
Published: 2019
Journal Articles

Gene Editing and mRNA-Based Therapy: Two Complementary Therapeutic Approaches for the Treatment of Patients with Xmen Disease

Julie Brault, PhD PharmD, Ezekiel Bello, Ronald J. Meis, PhD, Taylor Liu, Sherry M. Koontz, BS, Kennichi Dowdell, PhD, Linhong Li, PhD, Cornell Allen, MS, Narda Theobald, BS, Janet Lee, BS, Aaron B. Clark, BS, Juan C. Ravell, MD, Michael Lenardo, MD, Gary A. Dahl, PhD, Harry L. Malech, MD, Suk See De Ravin, MD, PhD
Journal: Blood
Blood (2019) 134 (Supplement_1): 4637.
https://doi.org/10.1182/blood-2019-129062
Published: 2019
Journal Articles

Development of a Clinically Applicable Method for High-Efficiency Gene Correction of Plerixafor-Mobilized CD34 + Cells from Patients with Sickle Cell Disease

Naoya Uchida, MD, Linhong Li, Juan J Haro-Mora, PhD, Selami Demirci, PhD, Tina Nassehi, Jackson Gamer, Claire Drysdale, Morgan Yapundich, Cornell Allen, Suk See De Ravin, MD PhD, Harry L Malech, MD, Madhusudan Peshwa, PhD, John F. Tisdale, MD
Journal: Blood
Blood (2018) 132 (Supplement 1): 2191.
https://doi.org/10.1182/blood-2018-99-111677
Published: 2018
Journal Articles

Aberrant Clonal Hematopoiesis of the Erythroid and Myeloid Lineages in a Lentivirally Barcoded Rhesus Macaque

Diego A Espinoza, BA, Chuanfeng Wu, MD, Xing Fan, MD, Di Yang, MD, Idalia Montano Yabe, MS, Selami Demirci, PhD, So Gun Hong, PhD, Aylin Bonifacino, MS, Allen Krouse, Mark Metzger, Rong Lu, PhD, Katherine R Calvo, MD PhD, John F Tisdale, MD, Xiaolin Wu, PhD, Suk See De Ravin, MD PhD, Harry L Malech, MD, Robert E Donahue, VMD, Cynthia E Dunbar, MD
Journal: Blood
Blood (2017) 130 (Supplement 1): 606.
https://doi.org/10.1182/blood.V130.Suppl_1.606.606
Published: 2017
Journal Articles

Interim Results from a Phase I/II Clinical Gene Therapy Study for Newly Diagnosed Infants with X-Linked Severe Combined Immunodeficiency Using a Safety-Modified Lentiviral Vector and Targeted Reduced Exposure to Busulfan

Ewelina Mamcarz, MD, Sheng Zhou, PhD, Timothy Lockey, PhD, Hossam Abdelsamed, PhD, Shane Cross, Pharm D, Zhijun Ma, MD, Jola Dowdy, Brandon Triplett, MD, Mitchell J. Weiss, MD PhD, Byoung Y. Ryu, PhD, Elif Dokmeci, MD, Juan Carlos Aldave, MD, Suk See De Ravin, MD PhD, Benjamin Youngblood, PhD, Janel R. Long-Boyle, PharmD, PhD, Michael M Meagher, PhD, Harry L Malech, MD, Jennifer Puck, MD, Morton Jerome Cowan, MD, Brian Sorrentino, MD
Journal: Blood
Blood (2017) 130 (Supplement 1): 523.
https://doi.org/10.1182/blood.V130.Suppl_1.523.523
Published: 2017
Journal Articles

High Titer Lentivector from a Stable Lenti-Producer Efficiently Corrects CD34+ Hematopoietic Stem Cells from Patients with p47phox-Deficient Chronic Granulomatous Disease

Uimook Choi, PhD, Narda Theobald, Throm E Robert, PhD, John Gray, PhD, David J. Rawlings, MD, Brian P. Sorrentino, MD, Harry Malech, Suk See De Ravin, MD
Journal: Blood
Blood (2015) 126 (23): 2036.
https://doi.org/10.1182/blood.V126.23.2036.2036
Published: 2015
Journal Articles

Correction of Human X-Linked Chronic Granulomatous Disease (X-CGD) Following Transduction of X-CGD CD34+ Cells with a Modified RD114-Pseudotyped Simian Immunodeficiency Virus Lentiviral Vector in a NOD/SCID Mouse Xenograft Model.

Nora Naumann, MD, PhD, Suk See De Ravin, MD, PhD, Uimook Choi, PhD, Morvarid Moayeri, MD, PhD, Yasuhiro Ikeda, DVM, PhD, Harry L. Malech, MD
Journal: Blood
Blood (2006) 108 (11): 3278.
https://doi.org/10.1182/blood.V108.11.3278.3278
Published: 2006
Journal Articles

Improvement of Canine XSCID by In Vivo Gene Therapy Using RD114/TR-Pseudotyped SIV Lentiviral Vectors.

Morvarid Moayeri, MD, PhD, Suk See De Ravin, MD, PhD, Douglas R. Kennedy, BS, Nora Naumann, MD,PhD, Yasuhiro Ikeda, DVM,PhD, Peter J. Felsburg, VMD,PhD, Harry L. Malech, MD
Journal: Blood
Blood (2006) 108 (11): 3275.
https://doi.org/10.1182/blood.V108.11.3275.3275
Published: 2006