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Margaret Ragni
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Journal Articles

Royal gene therapy at a royal cost

Margaret Ragni
Journal: Blood
Blood (2021) 138 (18): 1645–1646.
https://doi.org/10.1182/blood.2021012129
Published: 2021
Journal Articles

Gene-produced FVIII: measure for measure

Margaret Ragni
Journal: Blood
Blood (2020) 136 (22): 2483–2484.
https://doi.org/10.1182/blood.2020008974
Published: 2020
Journal Articles

B-YOND Final Results Confirm Established Safety, Sustained Efficacy, and Extended Dosing Interval for Up to 4 Years of Treatment With rFIXFc in Previously Treated Subjects With Severe Hemophilia B

Margaret Ragni, Roshni Kulkarni, K. John Pasi, MB, ChB, PhD FRCP, FRCPath, FRCPCH, Kathelijn Fischer, Johnny Mahlangu, Amy Shapiro, Beatrice Nolan, Johannes Oldenburg, Tadashi Matsushita, Annemieke Willemze, Huixing Yuan, Dan Rudin
Journal: Blood
Blood (2018) 132 (Supplement 1): 1214.
https://doi.org/10.1182/blood-2018-99-110100
Published: 2018
Journal Articles

Hemostatic efficacy, safety, and pharmacokinetics of a recombinant von Willebrand factor in severe von Willebrand disease

Clinical Trials & Observations
Joan C. Gill, Giancarlo Castaman, Jerzy Windyga, Peter Kouides, Margaret Ragni, Frank W. G. Leebeek, Ortrun Obermann-Slupetzky, Miranda Chapman, Sandor Fritsch, Borislava G. Pavlova, Isabella Presch, Bruce Ewenstein
Journal: Blood
Blood (2015) 126 (17): 2038–2046.
https://doi.org/10.1182/blood-2015-02-629873
Published: 2015
Journal Articles

Pharmacokinetic Evaluation of Von Willebrand Factor/Factor VIII Concentrate (Humate-P®) Prior to Elective Surgery in Patients with Von Willebrand Disease.

Jorge Di Paola, MD, Joan Gill, MD, Jonathan Bernstein, MD, Cindy Leissinger, MD, Margaret Ragni, MD, Rinah Shopnik, MD, Leonard Valentino, MD, Carl Friedman, MD, Sigurd Knaub, MD
Journal: Blood
Blood (2006) 108 (11): 4077.
https://doi.org/10.1182/blood.V108.11.4077.4077
Published: 2006
Journal Articles

Predictors of Liver Fibrosis in HCV+ Hemophilic Men.

Kakra Soadwa, MPH, Michael Nalesnik, MD, Qianyu Dang, PhD, Margaret Ragni, MD
Journal: Blood
Blood (2005) 106 (11): 319.
https://doi.org/10.1182/blood.V106.11.319.319
Published: 2005
Journal Articles

Human Immune Responses to AAV-2 Capsid May Limit Duration of Expression in Liver-Directed Gene Transfer in Humans with Hemophilia B.

Katherine High, MD, Michael Tigges, PhD, Catherine Manno, MD, Denise Sabatino, PhD, Valder Arruda, MD, Roland Herzog, PhD, Pradip Rustagi, MD, John Rasko, MD, Jurg Sommer, PhD, Kristen Jaworski, RN, Margaret Ragni, MD, Bertil Glader, MD, Ruth Lessard, Alvin Luk, PhD, Linda Couto, PhD, Haiyan Jiang, PhD, Glenn Pierce, MD, Mark Kay, MD
Journal: Blood
Blood (2004) 104 (11): 413.
https://doi.org/10.1182/blood.V104.11.413.413
Published: 2004