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Daniel LeBlanc
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Journal Articles

In Vitro and In Vivo Potency Differences between AAVRh74var and AAV5 Vectors Encoding the Same High-Activity Human Factor IX Variant, FIX-R338L, Expression Cassette: Implications for Hemophilia B Gene Therapy

Debra D Pittman, Swapnil Rakhe, Lisa J Wilcox, Daniel LeBlanc, Vicente Pagan, Megan L Brophy, Diana Sapashnik, Annette Sievers
Journal: Blood
Blood (2024) 144 (Supplement 1): 3581.
https://doi.org/10.1182/blood-2024-203983
Published: 2024