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Journal Articles

Long-term effect of hematopoietic cell transplantation on systemic inflammation in patients with mucopolysaccharidoses

Brigitte T.A. van den Broek, Caroline A. Lindemans, Jaap Jan Boelens, Eveline M. Delemarre, Julia Drylewicz, Nanda Verhoeven-Duif, Peter M. van Hasselt, Stefan Nierkens
Journal: Blood Advances
Blood Adv (2021) 5 (16): 3092–3101.
https://doi.org/10.1182/bloodadvances.2020003824
Published: 2021
Includes: Supplemental data
Journal Articles

Hurdles in treating Hurler disease: potential routes to achieve a “real” cure

Brigitte T. A. van den Broek, Jaap van Doorn, Charlotte V. Hegeman, Stefan Nierkens, Caroline A. Lindemans, Nanda Verhoeven-Duif, Jaap Jan Boelens, Peter M. van Hasselt
Journal: Blood Advances
Blood Adv (2020) 4 (12): 2837–2849.
https://doi.org/10.1182/bloodadvances.2020001708
Published: 2020
Journal Articles

Immune cytopenia post–cord transplant in Hurler syndrome is a forme fruste of graft rejection

David Deambrosis, Su Han Lum, Ryan M. Hum, Kay Poulton, Wendy Ogden, Simon Jones, Simon Stanworth, Denise Bonney, Prashant Hiwarkar, Robert F. Wynn
Journal: Blood Advances
Blood Adv (2019) 3 (4): 570–574.
https://doi.org/10.1182/bloodadvances.2018026963
Published: 2019
Includes: Supplemental data
Journal Articles

Aldenhoven M, van den Broek BTA, Wynn RF, et al. Quality of life of Hurler syndrome patients after successful hematopoietic stem cell transplantation. Blood Adv. 2017;1(24):2236-2242.

Journal: Blood Advances
Blood Adv (2017) 1 (26): 2535.
https://doi.org/10.1182/bloodadvances.2017014407
Published: 2017
Journal Articles

Quality of life of Hurler syndrome patients after successful hematopoietic stem cell transplantation

Clinical Trials & Observations
Mieke Aldenhoven, Brigitte T. A. van den Broek, Robert F. Wynn, Anne O’Meara, Paul Veys, Attilio Rovelli, Simon A. Jones, Rossella Parini, Peter M. van Hasselt, Marleen Renard, Victoria Bordon, Tom J. de Koning, Jaap Jan Boelens
Journal: Blood Advances
Blood Adv (2017) 1 (24): 2236–2242.
https://doi.org/10.1182/bloodadvances.2017011387
Published: 2017
Includes: Supplemental data