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Brigitte T. A. van den Broek
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Journal Articles

Hurdles in treating Hurler disease: potential routes to achieve a “real” cure

Brigitte T. A. van den Broek, Jaap van Doorn, Charlotte V. Hegeman, Stefan Nierkens, Caroline A. Lindemans, Nanda Verhoeven-Duif, Jaap Jan Boelens, Peter M. van Hasselt
Journal: Blood Advances
Blood Adv (2020) 4 (12): 2837–2849.
https://doi.org/10.1182/bloodadvances.2020001708
Published: 2020
Journal Articles

Early and late outcomes after cord blood transplantation for pediatric patients with inherited leukodystrophies

Clinical Trials & Observations
Brigitte T. A. van den Broek, Kristin Page, Annalisa Paviglianiti, Janna Hol, Heather Allewelt, Fernanda Volt, Gerard Michel, Miguel Angel Diaz, Victoria Bordon, Tracey O'Brien, Peter J. Shaw, Chantal Kenzey, Amal Al-Seraihy, Peter M. van Hasselt, Andrew R. Gennery, Eliane Gluckman, Vanderson Rocha, Annalisa Ruggeri, Joanne Kurtzberg, Jaap Jan Boelens
Journal: Blood Advances
Blood Adv (2018) 2 (1): 49–60.
https://doi.org/10.1182/bloodadvances.2017010645
Published: 2018
Includes: Supplemental data
Journal Articles

Quality of life of Hurler syndrome patients after successful hematopoietic stem cell transplantation

Clinical Trials & Observations
Mieke Aldenhoven, Brigitte T. A. van den Broek, Robert F. Wynn, Anne O’Meara, Paul Veys, Attilio Rovelli, Simon A. Jones, Rossella Parini, Peter M. van Hasselt, Marleen Renard, Victoria Bordon, Tom J. de Koning, Jaap Jan Boelens
Journal: Blood Advances
Blood Adv (2017) 1 (24): 2236–2242.
https://doi.org/10.1182/bloodadvances.2017011387
Published: 2017
Includes: Supplemental data