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Sofia Freiman
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Journal Articles

Single-Cell-Multiomics Demonstrates Molecular Efficacy of a Clinical Lentiviral Vector for Gene Therapy of RPS19-Deficient Diamond-Blackfan Anemia

Sofia Freiman, Jun Chen, Johan Flygare, Chayenne Kampman, Karin Pike-Overzet, Alexander Mohseny, Teng-Cheong Ha, Mathias Lidgren, Shamit Soneji, Stefan Karlsson, Dagmar Pospíšilová, Frank Staal, Axel Schambach, Johan Flygare
Journal: Blood
Blood (2023) 142 (Supplement 1): 943.
https://doi.org/10.1182/blood-2023-185802
Published: 2023