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Herve Puy, MD PhD
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Journal Articles

Results from the Completed Hgb-205 Trial of Lentiglobin for β-Thalassemia and Lentiglobin for Sickle Cell Disease Gene Therapy

Elisa Magrin, PhD, Michaela Semeraro, MD PhD, Alessandra Magnani, MD PhD, Hervé Puy, MD PhD, Annarita Miccio, PhD, Nicolas Hebert, Jean-Sebastien Diana, MD, Francois Lefrere, MD, Felipe Suarez, MD PhD, Olivier Hermine, MD PhD, Valentine Brousse, MD, Catherine Poirot, MD PhD, Philippe Bourget, PharmD, PhD, Wassim El Nemer, PhD, Isabelle Guichard, MD, Despina Moshous, MD PhD, Benedicte Neven, MD, Fabrice Monpoux, MD, Marilyne Poirée, MD, Pablo Bartolucci, MD PhD, Jean-François Meritet, MD, David Grévent, MD, Thibaud Lefebvre, Pharm D.,PhD, Mohammed Asmal, MD PhD, Erin Whitney, MBA, Marisa Gayron, MS, Wenmei Huang, PhD MS, Isabelle Funck-Brentano, PsyD, Mariane de Montalembert, MD PhD, Laure Joseph, MD, Jean-Antoine Ribeil, MD PhD, Marina Cavazzana
Journal: Blood
Blood (2019) 134 (Supplement_1): 3358.
https://doi.org/10.1182/blood-2019-127393
Published: 2019
Journal Articles

A Dominant Mutation in Mitochondrial Unfoldase CLPX Results in Erythropoietic Protoporphyria

Yvette Y Yien, PhD, Gael Nicolas, PhD, Lisa van der Vorm, Laurent Gouya, MD PhD, Hector Begonia, Martin Kafina, Jean-Charles Deybach, MD PhD, Tania Baker, PhD, Julia Kardon, PhD, John D. Phillips, PhD, Hervé Puy, MD PhD, Barry H. Paw, MD, PhD
Journal: Blood
Blood (2016) 128 (22): 77.
https://doi.org/10.1182/blood.V128.22.77.77
Published: 2016
Journal Articles

Update from the Hgb-205 Phase 1/2 Clinical Study of Lentiglobin Gene Therapy: Sustained Clinical Benefit in Severe Hemoglobinopathies

Jean-Antoine Ribeil, MD PhD, Salima Hacein-Bey-Abina, Pharm.D., PhD, Emmanuel Payen, PhD, Michaela Semeraro, PhD, Magrin Elisa, PhD, Laure Caccavelli, PhD, Fabien Touzot, MD PhD, Francois Lefrere, MD, Felipe Suarez, MD PhD, Olivier Hermine, MD PhD, Valentine Brousse, MD, Catherine Poirot, MD PhD, Benedicte Neven, MD PhD, Philippe Bourget, PharmD, PhD, Wassim El Nemer, PhD, Pablo Bartolucci, MD PhD, Leslie Weber, MSc, Hervé Puy, MD PhD, Jean-François Méritet, PhD, David Grevent, MD, Yves Beuzard, MD, Stany Chrétien, MD, Thibaud Lefebvre, MD, Mohammed Asmal, MD PhD, Marcelyne Joseney-Antoine, Mariane De Montalembert, MD PhD, Stephane Blanche, MD, Philippe Leboulch, MD, Marina Cavazzana, MD PhD
Journal: Blood
Blood (2016) 128 (22): 2311.
https://doi.org/10.1182/blood.V128.22.2311.2311
Published: 2016
Journal Articles

Assessment of Cardiac Iron Overload in Chonically Transfused Patients with Thalassemia, Sickle Cell Anemia, and Myelodysplastic Syndromes

Mariane De Montalembert, MD PhD, Jean-Antoine Ribeil, MD PhD, Valentine Brousse, Agnes Guerci-Bresler, MD, Aspasia Stamatoullas, MD, Jean Pierre Vannier, MD, Agnes Lahary, MD, Mohamed Touati, MD, Krimo Bouabdallah, MD, Marina Cavazzana, MD PhD, Emmanuelle Chauzit, MD, Amandine Baptiste, MD, Thibaud Lefebvre, MD, Herve Puy, MD PhD, Caroline Elie, MD PhD, Zoubida Karim, PhD, Olivier Ernst, MD PhD, Christian Rose
Journal: Blood
Blood (2015) 126 (23): 2151.
https://doi.org/10.1182/blood.V126.23.2151.2151
Published: 2015
Journal Articles

Erythropoietic Protoporphyric Red Blood Cells Are Resistant to the Growth of Malarial Parasites

Brendan John McMorran, BSc (Hons), PhD, Clare M Smith, BSc (Hons), PhD, Ante Jerkovic, Hervé Puy, MD PhD, Ingrid Winship, Jean-Charles Deybach, Laurent Gouya, Giel van Dooren, Christopher Dean Goodman, Angelika Sturm, Hana Manceau, Geoffrey Ian McFadden, Peter David, Odile Mercereau-Puijalon, Gaetan Burgio, Simon J Foote, MBBS, PhD
Journal: Blood
Blood (2014) 124 (21): 2670.
https://doi.org/10.1182/blood.V124.21.2670.2670
Published: 2014