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Journal Articles

Lentiviral Gene Therapy with Autologous Hematopoietic Stem and Progenitor Cells (HSPCs) for the Treatment of Severe Combined Immune Deficiency Due to Adenosine Deaminase Deficiency (ADA-SCID): Results in an Expanded Cohort

Blood (2019) 134 (Supplement_1): 3345.

https://doi.org/10.1182/blood-2019-123432

Published: 2019

Journal Articles

Wiskott-Aldrich Syndrome: A Retrospective Study on 575 Patients Analyzing the Impact of Splenectomy, Stem Cell Transplantation, or No Definitive Treatment on Frequency of Disease-Related Complications and Physician-Perceived Quality of Life

Jannik S Glasmacher, Tanja C Bittner, MD, Hans D Ochs, MD, Alessandro Aiuti, MD PhD, Peter D Arkwright, MD, Dmitry Balashov, Uta Behrends, Bernd H. Belohradsky, MD, Elisa Bertoni, David K. Buchbinder, MD MSHS, Michael Browning, Anastasiia Bondarenko, Fabio Candotti, MD, Alessandro Cattoni, Liudmyla Chernyshova, Joseph H. Chewning, MD, Peter Ciznar, Theresa Cole, Beatriz T Costa-Carvalho, Wojciech Czogala, Gregor Dueckers, David M Edgar, Fatih Erbey, Anders Fasth, MD PhD, Renata Formankova, MD PhD, Tomas Freiberger, Eleonora Gambineri, Andrew Gennery, MD, Frederick D Goldman, MD, Luis I Gonzalez-Granado, Tiago N Gulmaraes, David Hagin, MD PhD, Fabian Hauck, MD PhD, Tarja Heiskanen-Kosma, Manfred Hoenig, MD, Hanna Juntti, Hirokazu Kanegane, Leena Kainulainen, Neslihan E Karaca, Sara S Kilic, Christoph Klein, MD PhD, Sylwia Koltan, Irina Kondratenko, Dawei Liu, MD, Susanne Matthes, MD, Juliana T L Mazzucchelli, Isabelle Meyts, Siraj Misbah, Zohreh Nademi, Gulnara Nasrullayeva, Lucia D Notarangelo, Pere Soler-Palacin, Olga Pashchenko, Srdjan Pasic, Isabelle Pellier, MD, Claudio Pignata, Camilla Roepstorff, Catharina Schuetz, Ansgar S Schulz, MD PhD Prof., Gesmar R S Segundo, Anna Shcherbina, Joanne Smart, Robert A. Sokolic, MD, Polina Stepensky, MD, Troy Torgerson, MD PhD, Svetlana Vakhlyarskaya, Joris van Montfrans, MD PhD, Kim Vettenranta, MD PD, Beata Wolska-Kusnierz, Xiaodong Zhao, John B Ziegler, Xuan Zhang, Michael H. Albert, MD

Blood (2016) 128 (22): 366.

https://doi.org/10.1182/blood.V128.22.366.366

Published: 2016

Journal Articles

What's the 'Skinny' on Microbiome? Interplay of Immune Cells, Microbes, and Skin Barrier in Health and Disease

Julie Segre, PhD, Heidi Kong, MD, Fabio Candotti, MD, Steven M. Holland, MD, Alexandra F Freeman, MD, Julia Oh, PhD, Robert A. Sokolic

Blood (2014) 124 (21): SCI-46.

https://doi.org/10.1182/blood.V124.21.SCI-46.SCI-46

Published: 2014

Journal Articles

Cation Leak in Red Blood Cells of Patients with Wiskott-Aldrich Syndrome Leads to Non-Immunologic Hemolysis

Robert A. Sokolic, MD, Satheesh Chonat, MD, Mary Risinger, RN, Michael Eckhaus, DVM, Elizabeth Garabedian, RN, MSLS, Katherine R. Calvo, MD, PhD, Irina Maric, MD, Theodosia A. Kalfa, MD PhD, Fabio Candotti, MD

Blood (2014) 124 (21): 1338.

https://doi.org/10.1182/blood.V124.21.1338.1338

Published: 2014

Journal Articles

AK2 Deficiency In Zebrafish Recapitulates Human Reticular Dysgenesis, An Autosomal Recessive Form Of Severe Combined Immunodeficiency

Alberto Rissone, PhD, Jaya Jagadeesh, Karen Simon, Kevin Bishop, Raman B. Sood, PhD, Fabio Candotti, MD

Blood (2013) 122 (21): 2416.

https://doi.org/10.1182/blood.V122.21.2416.2416

Published: 2013

Journal Articles

Negative Control Region Is a Critical Element Of Insertional Oncogenesis After Gene Transfer Into Hematopoietic Progenitors With Moloney Murine Leukemia Viruses

Yasuhiro Ikawa, MD, PhD, Toru Uchiyama, MD, PhD, Guridevi Jayashree Jagadeesh, MS, Fabio Candotti, MD

Blood (2013) 122 (21): 164.

https://doi.org/10.1182/blood.V122.21.164.164

Published: 2013

Journal Articles

Adenylate Kinase 2 Regulates Zebrafish Primitive and Definitive Hematopoiesis

Alberto Rissone, PhD, Jaya Jagadeesh, Simon Karen, Kevin Bishop, Trevor Blake, Raman B. Sood, PhD, Fabio Candotti, MD

Blood (2012) 120 (21): 1208.

https://doi.org/10.1182/blood.V120.21.1208.1208

Published: 2012

Journal Articles

Analysis of Risk and Mechanism of Insertional Oncogenesis After Gene Transfer Into Hematopoietic Progenitors with Integrating Viral Vectors

Yasuhiro Ikawa, MD, PhD, Toru Uchiyama, MD, PhD, Guridevi Jayashree Jagadeesh, MS, Fabio Candotti, MD

Blood (2012) 120 (21): 2049.

https://doi.org/10.1182/blood.V120.21.2049.2049

Published: 2012

Journal Articles

Platelets From WAS Patients Are More Susceptible Than Controls to Phagocytosis by Activated THP-1 Cells

Ted Strom, MD, PhD, Xueying Zeng, Fabio Candotti, MD, PhD, Mary Ellen Conley, MD, PhD, Praveen Anur, MD, Amanda Prislovsky

Blood (2011) 118 (21): 2222.

https://doi.org/10.1182/blood.V118.21.2222.2222

Published: 2011

Journal Articles

Characterization of AK2 Gene Function in Zebrafish Hematopoiesis

Alberto F Rissone, Guridevi Jayashree Jagadeesh, MS, Karen Simon, Kevin Bishop, Milton English, Trevor Blake, Robert M Nissen, Raman B. Sood, PhD, Fabio Candotti, MD

Blood (2011) 118 (21): 2185.

https://doi.org/10.1182/blood.V118.21.2185.2185

Published: 2011

Journal Articles

Comparison of Immortalization Potential of Gamma-Retroviral, Lentiviral and Foamy Virus Gene Transfer Vectors

Yasuhiro Ikawa, MD, PhD, Toru Uchiyama, MD, PhD, Guridevi Jayashree Jagadeesh, MS, Fabio Candotti, MD

Blood (2011) 118 (21): 3116.

https://doi.org/10.1182/blood.V118.21.3116.3116

Published: 2011

Journal Articles

Human Adenylate Kinase 2 Deficiency Causes a Profound Haematopoietic Defect Associated with Sensorineural Deafness

Blood (2008) 112 (11): lba-2.

https://doi.org/10.1182/blood.V112.11.lba-2.lba-2

Published: 2008

Journal Articles

Dermatofibrosarcoma Protuberans in 3 Patients with ADA-SCID

Chimene Kesserwan, MD, Robert A. Sokolic, MD, Kerstin Heselmeyer, PhD, Clarymar Ortiz-Melendez, B.Sc, Jeffrey Cohen, MD, Jaya Jagadeesh, M.Sc, Elizabeth Garabedian, M.Sc, Kristin Baird, MD, Alan S. Wayne, MD, Edward W. Cowen, MD, Stefania Pittaluga, MD, PhD, Chyi-Chia Richard Lee, MD, PhD, Richard Sherry, MD, Julia Bridge, MD, Laura Finlayson, MD, Noreen Walsh, MD, Andrew Issekutz, MD, Fabio Candotti, MD

Blood (2008) 112 (11): 4833.

https://doi.org/10.1182/blood.V112.11.4833.4833

Published: 2008

Journal Articles

Comparative Results of Gene Therapy for Adenosine Deaminase Deficiency with or without PEG-ADA Withdrawal and Myelosuppressive Chemotherapy.

Robert Sokolic, MD, Greg Podsakoff, MD, Linda Muul, PhD, Barbara Engel, MD, Jayashree Jagadeesh, BS, Elizabeth Garabedian, RN, MSLS, Denise Carbonaro, Laura Tuschong, BS, Joanna Ireland, Michael Hershfield, MD, John Tisdale, MD, Cynthia Dunbar, MD, Alan Wayne, MD, Donald Kohn, MD, Fabio Candotti, MD

Blood (2007) 110 (11): 501.

https://doi.org/10.1182/blood.V110.11.501.501

Published: 2007

Journal Articles

Analysis of Retroviral Vector Insertion Sites after T-Cell Directed Gene Therapy.

Akihiro Konno, MD, PhD, G. Jayashree Jagadeesh, BS, Daniele Moratto, PhD, Marita Bosticardo, PhD, Ingeborg Holt, PhD, Linda M. Muul, PhD, Shepherd H. Schurman, MD, Tyra Wolfsberg, PhD, Fabio Candotti, MD

Blood (2004) 104 (11): 289.

https://doi.org/10.1182/blood.V104.11.289.289

Published: 2004

NARROW

Lentiviral Gene Therapy with Autologous Hematopoietic Stem and Progenitor Cells (HSPCs) for the Treatment of Severe Combined Immune Deficiency Due to Adenosine Deaminase Deficiency (ADA-SCID): Results in an Expanded Cohort

Wiskott-Aldrich Syndrome: A Retrospective Study on 575 Patients Analyzing the Impact of Splenectomy, Stem Cell Transplantation, or No Definitive Treatment on Frequency of Disease-Related Complications and Physician-Perceived Quality of Life

What's the 'Skinny' on Microbiome? Interplay of Immune Cells, Microbes, and Skin Barrier in Health and Disease

Cation Leak in Red Blood Cells of Patients with Wiskott-Aldrich Syndrome Leads to Non-Immunologic Hemolysis

AK2 Deficiency In Zebrafish Recapitulates Human Reticular Dysgenesis, An Autosomal Recessive Form Of Severe Combined Immunodeficiency

Negative Control Region Is a Critical Element Of Insertional Oncogenesis After Gene Transfer Into Hematopoietic Progenitors With Moloney Murine Leukemia Viruses

Adenylate Kinase 2 Regulates Zebrafish Primitive and Definitive Hematopoiesis

Analysis of Risk and Mechanism of Insertional Oncogenesis After Gene Transfer Into Hematopoietic Progenitors with Integrating Viral Vectors

Platelets From WAS Patients Are More Susceptible Than Controls to Phagocytosis by Activated THP-1 Cells

Characterization of AK2 Gene Function in Zebrafish Hematopoiesis

Comparison of Immortalization Potential of Gamma-Retroviral, Lentiviral and Foamy Virus Gene Transfer Vectors

Human Adenylate Kinase 2 Deficiency Causes a Profound Haematopoietic Defect Associated with Sensorineural Deafness

Dermatofibrosarcoma Protuberans in 3 Patients with ADA-SCID

Comparative Results of Gene Therapy for Adenosine Deaminase Deficiency with or without PEG-ADA Withdrawal and Myelosuppressive Chemotherapy.

Analysis of Retroviral Vector Insertion Sites after T-Cell Directed Gene Therapy.

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American Society of Hematology

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American Society of Hematology

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