1-6 of 6
Bobby Gaspar, MD
Close
Save search
Follow your search
Access your saved searches in your account
Would you like to receive an alert when new items match your search?
Close Modal
Sort by
Journal Articles

Preclinical Development of Gene Therapy for X-Linked Severe Combined Immunodeficiency (SCID-X1)

Valentina Poletti, PhD, Sabine Charrier, PhD, Samia Martin, Bernard Gjata, Alban Vignaud, PhD, Fang Zhang, PhD, Karen Buckland, PhD, Michael Rothe, PhD, Axel Schambach, MD PhD, Sung-Yun Pai, MD, David A. Williams, MD, H. Bobby Gaspar, MD PhD, Adrian J Thrasher, MD PhD, Fulvio Mavilio, PhD
Journal: Blood
Blood (2016) 128 (22): 4705.
https://doi.org/10.1182/blood.V128.22.4705.4705
Published: 2016
Journal Articles

New Molecular Surrogate Assay for Genotoxicity Assessment of Gene Therapy Vectors (SAGA)

Adrian Schwarzer, MD PhD, Steven R Talbot, PhD, Oliver Dittrich-Breiholz, PhD, Adrian J Thrasher, MD PhD, Bobby Gaspar, MD, Ute Modlich, Christopher Baum, MD, Axel Schambach, MD PhD, Michael Rothe, PhD
Journal: Blood
Blood (2016) 128 (22): 4710.
https://doi.org/10.1182/blood.V128.22.4710.4710
Published: 2016
Journal Articles

Immune Reconstitution and Preliminary Safety Analysis Of 9 Patients Treated With Somatic Gene Therapy For X-Linked Severe Combined Immunodeficiency (SCID-X1) With a Self-Inactivating Gammaretroviral Vector

Salima Hacein-Bey-Abina, Pharm.D., Ph.D., Sung-Yun Pai, MD, Frederic Bushman, PhD, Myriam Armant, PhD, Stephane Blanche, MD, Johanna Blondeau, Laure Caccavelli, Heather Daley, BS, Colleen Dansereau, RN, BSN, CPN, CPHON, Satiro deOliveira, MD, Dongjing Guo, MPH, Gregory Hopkins, BS, Annick Lim, M.Sci, Wendy B. London, PHD, Nirav Malani, Frances Male, BA, Punam Malik, MD, Maria Angelica Marinovic, MD, Sean McDonough, MS, Matias Oleastro, MD, Capucine Picard, MD PhD, Jerome Ritz, MD, Axel Schambach, MD PhD, Leslie E Silberstein, MD, Alla Tsytsykova, PhD, Johannes C.M. Van der Loo, PhD, Christopher Baum, MD, H. Bobby Gaspar, MD PhD, Donald B. Kohn, MD, Alexandra H. Filipovich, MD, Luigi Daniele Notarangelo, MD, Alain Fischer, MD, Marina Cavazzana-Calvo, MD, PhD, David A. Williams, MD, Adrian J Thrasher, MD, PhD
Journal: Blood
Blood (2013) 122 (21): 715.
https://doi.org/10.1182/blood.V122.21.715.715
Published: 2013
Journal Articles

Gene Therapy for Hemophagocytic Lymphohistiocytosis (HLH): Fixing a Criticial ‘Circuit Breaker’ in the Immune System.

Michael Jordan, MD, Marlene Carmo, PhD, Swati Tiwari, Paritha Arumugam, PhD, Kimberly Risma, MD PhD, Bobby Gaspar, MD, Punam Malik, MD
Journal: Blood
Blood (2012) 120 (21): 3158.
https://doi.org/10.1182/blood.V120.21.3158.3158
Published: 2012
Journal Articles

Dyskeratosis Congenita: Evaluation of Immune Status and Hematopoietic Stem Cell Transplantation. A Literature and EBMT Data Base Survey of 75 Patients,

Elisabeth T Korthof, MD, Judith Van der Zalm, med. student, Martine F Raphael, MD, Dorine Bresters, MD, PhD, Jakub Tolar, MD, PhD, Mahmoud Aljurf, MD, Paul Veys, MD MRCP FRCPath, Rosi Oneto, Andrea Bacigalupo, MD, Christina Peters, MD, Bobby Gaspar, MD, Carlo Dufour, MD, Judith C. W. Marsh, Prof MD PhD
Journal: Blood
Blood (2011) 118 (21): 4144.
https://doi.org/10.1182/blood.V118.21.4144.4144
Published: 2011
Journal Articles

Sustained Polyclonal Hematopoietic Repopulation after Successful SCID-X1 Gene Therapy by Means of a Non Random Integrating Pseudotyped Gammaretrovector.

Kerstin Schwarzwaelder, Manfred Schmidt, PhD, Steven Howe, PhD, Claudia Prinz, Manuela Wissler, Sonja Schmidt, Annette Deichmann, Hanno Glimm, MD, Bobby Gaspar, MD, Adrian Trasher, MD, PhD, Christof von Kalle, MD
Journal: Blood
Blood (2004) 104 (11): 290.
https://doi.org/10.1182/blood.V104.11.290.290
Published: 2004