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Journal Articles

Hurdles in treating Hurler disease: potential routes to achieve a “real” cure

Brigitte T. A. van den Broek, Jaap van Doorn, Charlotte V. Hegeman, Stefan Nierkens, Caroline A. Lindemans, Nanda Verhoeven-Duif, Jaap Jan Boelens, Peter M. van Hasselt
Journal: Blood Advances
Blood Adv (2020) 4 (12): 2837–2849.
https://doi.org/10.1182/bloodadvances.2020001708
Published: 2020