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Fulvio Mavilio
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Journal Articles

Correction of β-thalassemia by CRISPR/Cas9 editing of the α-globin locus in human hematopoietic stem cells

Giulia Pavani, Anna Fabiano, Marine Laurent, Fatima Amor, Erika Cantelli, Anne Chalumeau, Giulia Maule, Alexandra Tachtsidi, Jean-Paul Concordet, Anna Cereseto, Fulvio Mavilio, Giuliana Ferrari, Annarita Miccio, Mario Amendola
Journal: Blood Advances
Blood Adv (2021) 5 (5): 1137–1153.
https://doi.org/10.1182/bloodadvances.2020001996
Published: 2021
Includes: Supplemental data
Journal Articles

Gene transfer into hematopoietic stem cells reduces HLH manifestations in a murine model of Munc13-4 deficiency

Tayebeh Soheili, Amandine Durand, Fernando E. Sepulveda, Julie Rivière, Chantal Lagresle-Peyrou, Hanem Sadek, Geneviève de Saint Basile, Samia Martin, Fulvio Mavilio, Marina Cavazzana, Isabelle André-Schmutz
Journal: Blood Advances
Blood Adv (2017) 1 (27): 2781–2789.
https://doi.org/10.1182/bloodadvances.2017012088
Published: 2017