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Sylvia Von Mackensen, PhD
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Journal Articles

Spk-9001: Adeno-Associated Virus Mediated Gene Transfer for Hemophilia B - 1 Year Follow up and Impact of Baseline Characteristics on Transgene-Derived Factor IX Activity and Persistence

Lindsey A. George, MD, Spencer K. Sullivan, MD, Adam Giermasz, MD, Ben J. Samelson-Jones, MD PhD, Jonathan M. Ducore, MD, Jerome M. Teitel, MD FRCPC, Adam Cuker, MD MS, Sylvia Von Mackensen, PhD, Suvankar Majumdar, MD, Catherine E. McGuinn, MD, Alexa R. Runoski, MS, Fraser Wright, PhD, Sue Dasen, MS, Kimberly Barber, Yifeng Chen, MD, Daniel J. Hui, PhD, Ruchi Patel, Yun Liu, PhD, Katie Wachtel, MS, Dan Takefman, Linda B. Couto, PhD, Kathleen Z. Reape, Marcus E. Carr, MD PhD, Xavier M. Anguela, PhD, Katherine A. High, MD
Journal: Blood
Blood (2017) 130 (Supplement 1): 601.
https://doi.org/10.1182/blood.V130.Suppl_1.601.601
Published: 2017
Journal Articles

Gastrointestinal Bleeding and Angiodysplasia in Von Willebrand Disease: Results from the Ongoing French HRQoL Study: Wish-Qol

Annie Borel-Derlon, MD PhD, Dominique Desprez, MD, Fabienne Volot, MD, Herve Chambost, MD PhD, Sophie Bayard, MD, Catherine Chatelanaz, Catherine Doriat-Robin, Yves Gruel, MD PhD, Agnès Veyradier, Sr., MD PhD, Jenny Goudemand, MD PhD, Sylvia Von Mackensen, PhD
Journal: Blood
Blood (2017) 130 (Supplement 1): 4866.
https://doi.org/10.1182/blood.V130.Suppl_1.4866.4866
Published: 2017
Journal Articles

Wish-Qol Study - Assessment of Health-Related Quality of Life (HRQoL) and Health-Economic Aspects in Patients with Von Willebrand Disease (VWD) in France: Results of the Women Cohort

Annie Borel-Derlon, MD PhD, Jenny Goudemand, MD PhD, Dominique Desprez, MD, Fabienne Volot, MD, Yves Gruel, MD, Sophie Bayard, MD, Catherine Chatelanaz, Catherine Doriat-Robin, Agnes Veyradier, MD PhD, Edith Fressinaud, MD, Sylvia von Mackensen, PhD
Journal: Blood
Blood (2016) 128 (22): 1395.
https://doi.org/10.1182/blood.V128.22.1395.1395
Published: 2016
Journal Articles

Expectations and Concerns Towards New Extended Half-Life (EHL) Products - Results of Surveys Among Haemophilia Patients from the Dach Region

Sylvia von Mackensen, PhD, Werner Kalnins, Hostettler Lino, Krucker Joerg, Manuela Albisetti, MD, Josef Weiss, Ingrid Pabinger, Prof, Johannes Oldenburg, Prof
Journal: Blood
Blood (2016) 128 (22): 4740.
https://doi.org/10.1182/blood.V128.22.4740.4740
Published: 2016
Journal Articles

Perception of Actual Factor Concentrates and Expectations Towards Future Treatment with New Long-Lasting Products - Results of a Survey Among Haemophilia Patients in Germany

Sylvia von Mackensen, PhD, Struck Heinrich, Werner Kalnins, Johannes Oldenburg
Journal: Blood
Blood (2015) 126 (23): 4449.
https://doi.org/10.1182/blood.V126.23.4449.4449
Published: 2015
Journal Articles

Perception of Actual Factor Concentrates and Expectations Towards Future Treatment with New Long-Lasting Products - Results of a Survey Among Haemophilia Patients in Germany - Analysis of Open Questions

Werner Kalnins, Wolfgang A. Miesbach, MD PhD, Sylvia von Mackensen, PhD
Journal: Blood
Blood (2015) 126 (23): 3269.
https://doi.org/10.1182/blood.V126.23.3269.3269
Published: 2015
Journal Articles

Self- and Parent/Proxies-Reported Health-Related Quality Of Life In Children and Adolescents With Bleeding Disorders: Cross Sectional Investigation and Comparison With Healthy Siblings and Healthy Peers

Neuner Bruno, Sylvia von Mackensen, PhD, Susan Halimeh, MD, Susanne Holzhauer, MD, Robert Klamroth, MD, PhD, Karin Kurnik, MD, Anne Kruempel, MD, Michael Fruewald, Henning Krampe, Ulrike Nowak-Goettl
Journal: Blood
Blood (2013) 122 (21): 4773.
https://doi.org/10.1182/blood.V122.21.4773.4773
Published: 2013
Journal Articles

Psychometric Evaluation Of Health-Related Quality Of Life Assessments From The Along and Blong Hemophilia Clinical Trials

Kathleen W Wyrwich, PhD, Priscilla Auguste, MHS, Robyn von Maltzahn, MS, Ren Yu, MA, Sangeeta Krishnan, PharmD, MS, Nigel Dodd, MSc, Sylvia von Mackensen, PhD
Journal: Blood
Blood (2013) 122 (21): 423.
https://doi.org/10.1182/blood.V122.21.423.423
Published: 2013