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Leslie Weber, MSc
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Journal Articles

Induction of Fetal Hemoglobin Synthesis By Crispr/Cas9-Mediated Disruption of the β-Globin Locus Architecture

Chiara Antoniani, MSc, Vasco Meneghini, Annalisa Lattanzi, PhD, Giulia Pavani, PhD, Tristan Felix, MSc, Fatima Amor, MSc, Oriana Romano, Elisa Magrin, PhD, Leslie Weber, MSc, Thomas Cradick, Ante S Lundberg, MD, Matthew Porteus, MD PhD, Mario Amendola, Marina Cavazzana, MD PhD, Fulvio Mavilio, PhD, Annarita Miccio, PhD
Journal: Blood
Blood (2016) 128 (22): 321.
https://doi.org/10.1182/blood.V128.22.321.321
Published: 2016
Journal Articles

Update from the Hgb-205 Phase 1/2 Clinical Study of Lentiglobin Gene Therapy: Sustained Clinical Benefit in Severe Hemoglobinopathies

Jean-Antoine Ribeil, MD PhD, Salima Hacein-Bey-Abina, Pharm.D., PhD, Emmanuel Payen, PhD, Michaela Semeraro, PhD, Magrin Elisa, PhD, Laure Caccavelli, PhD, Fabien Touzot, MD PhD, Francois Lefrere, MD, Felipe Suarez, MD PhD, Olivier Hermine, MD PhD, Valentine Brousse, MD, Catherine Poirot, MD PhD, Benedicte Neven, MD PhD, Philippe Bourget, PharmD, PhD, Wassim El Nemer, PhD, Pablo Bartolucci, MD PhD, Leslie Weber, MSc, Hervé Puy, MD PhD, Jean-François Méritet, PhD, David Grevent, MD, Yves Beuzard, MD, Stany Chrétien, MD, Thibaud Lefebvre, MD, Mohammed Asmal, MD PhD, Marcelyne Joseney-Antoine, Mariane De Montalembert, MD PhD, Stephane Blanche, MD, Philippe Leboulch, MD, Marina Cavazzana, MD PhD
Journal: Blood
Blood (2016) 128 (22): 2311.
https://doi.org/10.1182/blood.V128.22.2311.2311
Published: 2016