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Laurent Gouya, MD, PhD
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Journal Articles

Eighteen-Month Interim Analysis of Efficacy and Safety of Givosiran, an RNAi Therapeutic for Acute Hepatic Porphyria, in the Envision Open Label Extension

David J. Kuter, MD, Sioban Keel, MD, Charles J. Parker, MD, David C. Rees, MD, Ulrich Stölzel, MD, Paolo Ventura, MD, Manisha Balwani, Laurent Gouya, MD, PhD, Amy Simon, MD, Shangbin Liu, PhD, John J Ko, PharmD,MSc, Sean Rhyee, MD, M.P.H, Samuel M. Silver, MD PhD
Journal: Blood
Blood (2020) 136 (Supplement 1): 13.
https://doi.org/10.1182/blood-2020-134564
Published: 2020
Journal Articles

Hepcidin, Soluble Transferrin Receptor, and Other Biomarkers of Iron Status Distributions in Healthy 2 Years Old Infants from a National Ambulatory Study in France

Anne-Sylvia Sacri, MD PhD, Thibaud Lefebvre, Pharm D.,PhD, Mariane De Montalembert, MD, Alain Bocquet, MD, Piotr Gembara, MD, Brigitte Pinçant, MD, Serge Hercberg, MD, PhD, Corinne Levy, MD, Amandine Ganon, Pharm D., Laurent Gouya, MD, PhD, Martin Chalumeau, MD, PhD
Journal: Blood
Blood (2019) 134 (Supplement_1): 4809.
https://doi.org/10.1182/blood-2019-128982
Published: 2019
Journal Articles

A Dominant Mutation in Mitochondrial Unfoldase CLPX Results in Erythropoietic Protoporphyria

Yvette Y Yien, PhD, Gael Nicolas, PhD, Lisa van der Vorm, Laurent Gouya, MD PhD, Hector Begonia, Martin Kafina, Jean-Charles Deybach, MD PhD, Tania Baker, PhD, Julia Kardon, PhD, John D. Phillips, PhD, Hervé Puy, MD PhD, Barry H. Paw, MD, PhD
Journal: Blood
Blood (2016) 128 (22): 77.
https://doi.org/10.1182/blood.V128.22.77.77
Published: 2016