1-8 of 8
Carolyn Lutzko, PhD
Close
Save search
Follow your search
Access your saved searches in your account
Would you like to receive an alert when new items match your search?
Close Modal
Sort by
Journal Articles

Early Results from a Phase 1/2 Study of Aru-1801 Gene Therapy for Sickle Cell Disease (SCD): Manufacturing Process Enhancements Improve Efficacy of a Modified Gamma Globin Lentivirus Vector and Reduced Intensity Conditioning Transplant

Michael Grimley, MD, Monika Asnani, PhD, Archana Shrestha, Sydney Felker, Carolyn Lutzko, PhD, Paritha I. Arumugam, PhD, Scott Witting, PhD, Jennifer Knight-Madden, MBBS, PhD, Omar Niss, MD, Charles T. Quinn, MD, Chris Lo, BS, Courtney R Little, BSN, Joseph W. McIntosh, MD, Punam Malik, MD
Journal: Blood
Blood (2020) 136 (Supplement 1): 20–21.
https://doi.org/10.1182/blood-2020-140963
Published: 2020
Journal Articles

VPS4A mutations Cause a Syndrome with Dyserythropoiesis, Hemolytic Anemia, and Neurodevelopmental Delay

Katie Giger Seu, PhD, Lisa Trump, PhD, Sana Emberesh, MBBS, Robert B. Lorsbach, MD PhD, Clarissa E. Johnson, MD, Jessica Meznarich, MD, Hunter Underhill, MD PhD, Haripriya Sakthivel, Omar Niss, MD, Shannon Nortman, Lionel Blanc, PhD, Wenying Zhang, MD PhD, Carolyn Lutzko, PhD, Theodosia A. Kalfa, MD PhD
Journal: Blood
Blood (2019) 134 (Supplement_1): 339.
https://doi.org/10.1182/blood-2019-128230
Published: 2019
Journal Articles

Peroxiredoxin II ( PRDX2 ) Is a Novel Candidate Gene for Congenital Dyserythropoietic Anemia

Myesa Emberesh, MBBS, Katie Giger Seu, PhD, Sana Emberesh, MBBS, Lisa Trump, Mary Risinger, PhD, Wenying Zhang, MD PhD, Ammar Husami, Carolyn Lutzko, PhD, Vinod Gidvani-Diaz, Robert B. Lorsbach, MD PhD, Theodosia A. Kalfa, MD PhD
Journal: Blood
Blood (2018) 132 (Supplement 1): 3605.
https://doi.org/10.1182/blood-2018-99-120056
Published: 2018
Journal Articles

Gene Therapy for Sickle Cell Anemia Using a Modified Gamma Globin Lentivirus Vector and Reduced Intensity Conditioning Transplant Shows Promising Correction of the Disease Phenotype

Punam Malik, MD, Michael Grimley, MD, Charles T. Quinn, MD, Amy Shova, RN, Little Courtney, RN, Carolyn Lutzko, PhD, Theodosia A. Kalfa, MD PhD, Omar Niss, MD, Parinda A Mehta, MD, Sharat Chandra, MBBS,MD, Elke Grassman, Johannes C.M. Van der Loo, PhD, Scott Witting, MS, Diana Nordling, Archana Shreshta, PhD, Sydney Felker, BS, Catherine Terrell, BS, Lilith Reeves, MS, MT(ASCP), Devin Pillis, MS, Loberg Anastacia, Frederic D Bushman, PhD, Jennifer Knight-Madden, Karen Kalinyak, MD, Stella M. Davies, PhD MBBS, MRCP, Monika Asnani, PhD
Journal: Blood
Blood (2018) 132 (Supplement 1): 1021.
https://doi.org/10.1182/blood-2018-99-119591
Published: 2018
Journal Articles

The First Registry for Patients with Congenital Dyserythropoietic Anemia in North America: Design and Preliminary Results

Omar Niss, MD, Robert B. Lorsbach, MD PhD, Georgios E Christakopoulos, MD, Lisa Trump, Megan Reynolds, Katie Giger, PhD, Clarissa E. Johnson, MD, Ammar Husami, David K. Buchbinder, MD MSHS, Jennifer A. Rothman, MD, Gavin D. Roach, MDMS, Adrienne Lee, MD, Vinod Gidvani-Diaz, Morgan L. McLemore, MD, Satheesh Chonat, MD, Adam S. Nelson, James B. Ball, MD, Bruce J. Aronow, PhD, Carolyn Lutzko, PhD, Kejian Zhang, MD MBA, Theodosia A. Kalfa, MD PhD
Journal: Blood
Blood (2017) 130 (Supplement 1): 2210.
https://doi.org/10.1182/blood.V130.Suppl_1.2210.2210
Published: 2017
Journal Articles

VPS4A : A Novel Candidate Gene for Congenital Dyserythropoietic Anemia

Katie Giger, PhD, Georgios E Christakopoulos, MD, Lisa Trump, Clarissa E. Johnson, MD, Haripriya Sakthivel, Mary Risinger, Omar Niss, MD, Kejian Zhang, MD MBA, Lionel Blanc, PhD, Robert B. Lorsbach, MD PhD, Paritha I. Arumugam, PhD, Carolyn Lutzko, PhD, Theodosia A. Kalfa, MD PhD
Journal: Blood
Blood (2017) 130 (Supplement 1): 923.
https://doi.org/10.1182/blood.V130.Suppl_1.923.923
Published: 2017
Journal Articles

Innovative Hematopoietic Gene-Therapy Concepts for Hereditary Pulmonary Alveolar Proteinosis Utilizing Hematopoietic Stem Cell Derived Macrophages

Nico Lachmann, PhD, Christine Happle, MD, Takuji Suzuki, MD, Miriam Hetzel, Kevin A. Link, PhD, Adele Mucci, Paritha Arumugam, PhD, Jens Bankstahl, PhD, Dagmar Dilloo, MD, Punam Malik, MD, Carolyn Lutzko, PhD, Axel Schambach, MD PhD, Bruce Colston Trapnell, MD, Gesine Hansen, MD, Thomas Moritz, MD
Journal: Blood
Blood (2015) 126 (23): 4417.
https://doi.org/10.1182/blood.V126.23.4417.4417
Published: 2015
Journal Articles

Myelopoiesis From Induced Pluripotent Stem Cells Reveals The Role Of Elastase Activity In The Pathogenesis Of Severe Congenital Neutropenia

Ramesh C Nayak, PH.D., Lisa Trump, PhD, H. Leighton Grimes, PhD, Carolyn Lutzko, PhD, Jose A. Cancelas, M.D. PhD.
Journal: Blood
Blood (2013) 122 (21): 442.
https://doi.org/10.1182/blood.V122.21.442.442
Published: 2013