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Journal Articles

Immunoadsorption enables successful rAAV5-mediated repeated hepatic gene delivery in nonhuman primates

David Salas, Karin L. Kwikkers, Nerea Zabaleta, Andrea Bazo, Harald Petry, Sander J. van Deventer, Gloria Gonzalez Aseguinolaza, Valerie Ferreira
Journal: Blood Advances
Blood Adv (2019) 3 (17): 2632–2641.
https://doi.org/10.1182/bloodadvances.2019000380
Published: 2019
Includes: Supplemental data
Journal Articles

Complete correction of hemophilia B phenotype by FIX-Padua skeletal muscle gene therapy in an inhibitor-prone dog model

Robert A. French, Benjamin J. Samelson-Jones, Glenn P. Niemeyer, Clinton D. Lothrop, Jr, Elizabeth P. Merricks, Timothy C. Nichols, Valder R. Arruda
Journal: Blood Advances
Blood Adv (2018) 2 (5): 505–508.
https://doi.org/10.1182/bloodadvances.2017015313
Published: 2018
Includes: Supplemental data
Journal Articles

Hemophilia gene therapy comes of age

Lindsey A. George
Journal: Blood Advances
Blood Adv (2017) 1 (26): 2591–2599.
https://doi.org/10.1182/bloodadvances.2017009878
Published: 2017
Journal Articles

Enhanced liver gene transfer and evasion of preexisting humoral immunity with exosome-enveloped AAV vectors

Amine Meliani, Florence Boisgerault, Zachary Fitzpatrick, Solenne Marmier, Christian Leborgne, Fanny Collaud, Marcelo Simon Sola, Severine Charles, Giuseppe Ronzitti, Alban Vignaud, Laetitia van Wittenberghe, Beatrice Marolleau, Fabienne Jouen, Sisareuth Tan, Olivier Boyer, Olivier Christophe, Alain R. Brisson, Casey A. Maguire, Federico Mingozzi
Journal: Blood Advances
Blood Adv (2017) 1 (23): 2019–2031.
https://doi.org/10.1182/bloodadvances.2017010181
Published: 2017
Includes: Supplemental data