Mechanisms of AAV-FVIII persistence in the liver of dogs with severe HA more than 10 years after therapy. Nonintegrated episomal forms of the vector correlated with long-term FVIII expression. Random integration was frequent, but no full-length integrated vector genomes were detected. Integrations were not associated with oncogene upregulation and no histopathological evidence of tumorigenesis was found.

Mechanisms of AAV-FVIII persistence in the liver of dogs with severe HA more than 10 years after therapy. Nonintegrated episomal forms of the vector correlated with long-term FVIII expression. Random integration was frequent, but no full-length integrated vector genomes were detected. Integrations were not associated with oncogene upregulation and no histopathological evidence of tumorigenesis was found.

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