FigureĀ 1.
Noncodon optimized AAV-cFVIII-BDD vector structure. ITR, inverted tandem repeat; SI, synthetic chimeric intron; SPA, synthetic polyadenylation sequence; TTR, transthyretin promoter.

Noncodon optimized AAV-cFVIII-BDD vector structure. ITR, inverted tandem repeat; SI, synthetic chimeric intron; SPA, synthetic polyadenylation sequence; TTR, transthyretin promoter.

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