Baseline characteristics of relapsed and refractory patients treated with haplo donors
No. . | Age and sex . | Previous therapy . | Severity . | Clonality PNH MK . | Donor . | ABO compatibility . | CMV status . | |
---|---|---|---|---|---|---|---|---|
1 | 35 M | ATG/CsA | SAA | + | 46XY | 38 F, sister | Matched | Matched |
2 | 52 M | ATG/CsA | SAA | + | 46XY | 50 M, brother | Matched | Matched |
3 | 45 F | ATG/CsA | SAA | − | 46XX | 47 M, brother | Matched | Matched |
4 | 27 F | ATG/CsA | SAA | + | 46XX | 24 M, brother | Matched | Matched |
5 | 33 M | HiCY | vSAA | − | 46XY | 50 M, rather | Matched | Matched |
6 | 17 M | HiCY | vSAA | + | 46XY | 56 F, mother | Matched | Mismatched (donor −) |
7 | 54 M | ATG/CSA, EPAG | vSAA | − | 46XY | 71 M, brother | Matched | Matched |
8 | 26 F | ATG/CSA, EPAG | SAA | + | 46XX | 58 F, mother | Bidirectional | Matched |
9 | 59 M | ATG/CSA ×2, EPAG | SAA | − | t(13;21) | 29 M, son | Minor mismatched | Matched |
10 | 20 F | ATG/CsA | vSAA | + | 46XX | 45 M, father | Matched | Mismatched (donor −) |
11 | 11 M | ATG/CsA | vSAA | − | 46XY | 52 M, father | Matched | Matched |
12 | 69 M | ATG/CSA ×2, alemtuzumab, EPAG | SAA | + | Del13 | 42 M, son | Matched | Matched |
13 | 11 M | ATG/CsA | vSAA | − | 46XY | 36 M, father | Matched | Matched |
14 | 21 M | CSA | SAA | + | 46XY | 23 F, sister | Minor mismatched | Matched |
15 | 11 M | ATG/CsA | SAA | − | 46XY | 34 F, mother | Matched | Mismatched (donor +) |
16 | 5 M | ATG/CsA | SAA | − | 46XY | 32 F, mother | Matched | Matched |
17 | 34 F | ATG/CsA ×3 | vSAA | − | 46XX | 36 F, mother | Matched | Matched |
18 | 31 F | Matched sibling BMT | vSAA | + | 46XX | 44 M, father | Matched | Mismatched (donor +) |
19 | 7 M* | None (DKC, TERC mutation) | vSAA | − | 46XY | 30 F, mother | Matched | Matched |
20 | 46 M | ATG/ CsA | vSAA | + | 46XY | 24 M, son | Matched | Matched |
No. . | Age and sex . | Previous therapy . | Severity . | Clonality PNH MK . | Donor . | ABO compatibility . | CMV status . | |
---|---|---|---|---|---|---|---|---|
1 | 35 M | ATG/CsA | SAA | + | 46XY | 38 F, sister | Matched | Matched |
2 | 52 M | ATG/CsA | SAA | + | 46XY | 50 M, brother | Matched | Matched |
3 | 45 F | ATG/CsA | SAA | − | 46XX | 47 M, brother | Matched | Matched |
4 | 27 F | ATG/CsA | SAA | + | 46XX | 24 M, brother | Matched | Matched |
5 | 33 M | HiCY | vSAA | − | 46XY | 50 M, rather | Matched | Matched |
6 | 17 M | HiCY | vSAA | + | 46XY | 56 F, mother | Matched | Mismatched (donor −) |
7 | 54 M | ATG/CSA, EPAG | vSAA | − | 46XY | 71 M, brother | Matched | Matched |
8 | 26 F | ATG/CSA, EPAG | SAA | + | 46XX | 58 F, mother | Bidirectional | Matched |
9 | 59 M | ATG/CSA ×2, EPAG | SAA | − | t(13;21) | 29 M, son | Minor mismatched | Matched |
10 | 20 F | ATG/CsA | vSAA | + | 46XX | 45 M, father | Matched | Mismatched (donor −) |
11 | 11 M | ATG/CsA | vSAA | − | 46XY | 52 M, father | Matched | Matched |
12 | 69 M | ATG/CSA ×2, alemtuzumab, EPAG | SAA | + | Del13 | 42 M, son | Matched | Matched |
13 | 11 M | ATG/CsA | vSAA | − | 46XY | 36 M, father | Matched | Matched |
14 | 21 M | CSA | SAA | + | 46XY | 23 F, sister | Minor mismatched | Matched |
15 | 11 M | ATG/CsA | SAA | − | 46XY | 34 F, mother | Matched | Mismatched (donor +) |
16 | 5 M | ATG/CsA | SAA | − | 46XY | 32 F, mother | Matched | Matched |
17 | 34 F | ATG/CsA ×3 | vSAA | − | 46XX | 36 F, mother | Matched | Matched |
18 | 31 F | Matched sibling BMT | vSAA | + | 46XX | 44 M, father | Matched | Mismatched (donor +) |
19 | 7 M* | None (DKC, TERC mutation) | vSAA | − | 46XY | 30 F, mother | Matched | Matched |
20 | 46 M | ATG/ CsA | vSAA | + | 46XY | 24 M, son | Matched | Matched |
F, female; M, male.
Denotes patient with inherited SAA.