Table 1.

Patient characteristics


No. of patients enrolled  

100  
Median patient sex, M/F   67/33  
Median patient age at diagnosis, y (range)   1.4 (0.1-14)  
Median patient age at HSCT, y (range)   2.5 (0.3-15)  
Median interval between diagnosis and HSCT, mo (range)   6 (0.3-49)  
Median WBC count at diagnosis,* × 109/L (range)   34 (3-240)  
Median monocyte count at diagnosis,† × 109/L (range)   5.5 (1-50)  
Median platelet count at diagnosis,‡ × 109/L (range)   65 (9-530)  
Percentage of HbF at diagnosis§ (range)   9 (0-80)  
Karyotype  
Normal karyotype   66  
Monosomy 7   20  
Trisomy 8   9  
Other abnormalities   4  
Missing/unknown   1  
No. of patients with clinical evidence of NF1∥   14  
Median WBC count at HSCT,¶ × 109/L (range)   9.6 (0.7-320)  
Percentage of marrow blasts at HSCT** (range)   6 (0-85)  
Splenectomy before HSCT   24  
Median spleen size at HSCT,†† cm (range)   5 (0-16)  
Patient HCMV serology  
Negative   57  
Positive   39  
Unknown
 
4
 

No. of patients enrolled  

100  
Median patient sex, M/F   67/33  
Median patient age at diagnosis, y (range)   1.4 (0.1-14)  
Median patient age at HSCT, y (range)   2.5 (0.3-15)  
Median interval between diagnosis and HSCT, mo (range)   6 (0.3-49)  
Median WBC count at diagnosis,* × 109/L (range)   34 (3-240)  
Median monocyte count at diagnosis,† × 109/L (range)   5.5 (1-50)  
Median platelet count at diagnosis,‡ × 109/L (range)   65 (9-530)  
Percentage of HbF at diagnosis§ (range)   9 (0-80)  
Karyotype  
Normal karyotype   66  
Monosomy 7   20  
Trisomy 8   9  
Other abnormalities   4  
Missing/unknown   1  
No. of patients with clinical evidence of NF1∥   14  
Median WBC count at HSCT,¶ × 109/L (range)   9.6 (0.7-320)  
Percentage of marrow blasts at HSCT** (range)   6 (0-85)  
Splenectomy before HSCT   24  
Median spleen size at HSCT,†† cm (range)   5 (0-16)  
Patient HCMV serology  
Negative   57  
Positive   39  
Unknown
 
4
 

WBC indicates white blood cell.

*Three unknown; †6 unknown; ‡3 unknown; §23 unknown; ∥8 unknown; ¶8 unknown; **13 unknown; ††6 unknown.

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