Table 5.

X-adrenoleukodystrophy–disability rating scale levels before and after hematopoietic cell transplantation (HCT) in 94 patients with cerebral X-adrenoleukodystrophy

Level after HCT, no. (%)
Level before HCT
No.
0
I
II
III
IV
No data, because of death
0   13   8 (62)*  3 (23)   1 (7.6)   —   1 (7.6)   —  
I   21   1 (4.8)   6 (28)†  4 (19)†  3 (14)   6 (28)†  1 (4.8)  
II   36   1 (2.8)   1 (2.8)   10 (2.8)‡  1 (2.8)   19 (53)∥  4 (11)  
III   12   —   —   —   1 (8.3)   10 (83)§  1 (8.3)  
IV   1   —   —   —   —   1 (100)*  —  
Missing data   11   —   —   1 (9)   —   —   5 (45)  
Totals   94   10   10   16   5   37   11  
Deaths
 		 35
 		 1
 		 2
 		 5
 		 0
 		 16
 		 11
 
Level after HCT, no. (%)
Level before HCT
No.
0
I
II
III
IV
No data, because of death
0   13   8 (62)*  3 (23)   1 (7.6)   —   1 (7.6)   —  
I   21   1 (4.8)   6 (28)†  4 (19)†  3 (14)   6 (28)†  1 (4.8)  
II   36   1 (2.8)   1 (2.8)   10 (2.8)‡  1 (2.8)   19 (53)∥  4 (11)  
III   12   —   —   —   1 (8.3)   10 (83)§  1 (8.3)  
IV   1   —   —   —   —   1 (100)*  —  
Missing data   11   —   —   1 (9)   —   —   5 (45)  
Totals   94   10   10   16   5   37   11  
Deaths
 		 35
 		 1
 		 2
 		 5
 		 0
 		 16
 		 11
 
*

Denotes 1 death

†

Denotes 2 deaths

‡

Denotes 3 deaths

§

Denotes 4 deaths

∥

Denotes 9 deaths

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