Response of 10 patients with factor X deficiency to HDM/ASCT12
Patient no. . | Response . | Melphalan, mg/m2 . | Factor X, pre-HDM/ASCT, % . | Factor X, post-HDM/ASCT, % . |
---|---|---|---|---|
4 | CR | 140 | 13 | 42 |
5* | Expired | 200 | 16 | |
6* | Expired | 200 | 16 | |
7 | PR | 200 | 17 | 15 |
10 | CR | 140 | 29 | 41 |
14 | NR | 140 | 38 | 39 |
15 | CR | 200 | 40 | 104 |
16* | Expired | 200 | 41 | |
18 | PR | 140 | 47 | 96 |
19 | CR | 200 | 19 | 86 |
Patient no. . | Response . | Melphalan, mg/m2 . | Factor X, pre-HDM/ASCT, % . | Factor X, post-HDM/ASCT, % . |
---|---|---|---|---|
4 | CR | 140 | 13 | 42 |
5* | Expired | 200 | 16 | |
6* | Expired | 200 | 16 | |
7 | PR | 200 | 17 | 15 |
10 | CR | 140 | 29 | 41 |
14 | NR | 140 | 38 | 39 |
15 | CR | 200 | 40 | 104 |
16* | Expired | 200 | 41 | |
18 | PR | 140 | 47 | 96 |
19 | CR | 200 | 19 | 86 |
Patient 5 expired at day 29 post-HDM/ASCT, patient 6 expired at day 15, and patient 16 at 6 months.