Outcome
ID . | Duration DF (d) . | Dose Range (DF) mg/kg/d . | Long-Term Outcome3-150 . |
---|---|---|---|
Responders3-151 | |||
UPN01 | 61 | 10-20 | Alive: NED, D + 1046 [976 d] |
UPN04 | 26 | 15-5-15 | Alive: NED, D + 833 [782 d] |
UPN08 | 36 | 10-20 | Death: relapsed ALL, D + 191 [130 d] |
UPN14 | 35 | 10-25 | Death: fungal sepsis, CMV pneumonitis, D + 47 [2 d] |
UPN18 | 14 | 10-20 | Death: respiratory failure, intracranial hemorrhage, D + 68 [43 d] |
UPN19 | 26 | 10-60 | Alive: NED, D + 324 [241 d] |
UPN22 | 34 | 10-60 | Alive: NED, D + 224 [179 d] |
UPN23 | 45 | 10-40 | Alive: NED, D + 217 [138 d] |
Nonresponders | |||
UPN02 | 4 | 10-15 | Death: ARF, D + 26 [1 d] |
UPN03 | 5 | 15 | Death: fungal sepsis, D + 25 [0 d] |
UPN05 | 15 | 10-25 | Death: progressive VOD, ARF, D + 27 [1 d] |
UPN06 | 2 | 10 | Death: fungal sepsis, D + 15 [0 d] |
UPN07 | 7 | 10-15 | Death: CMV pneumonitis, enterobacter, fungal sepsis, D + 45 [3 d] |
UPN09 | 11 | 10-40 | Death: progressive VOD, D + 40 [3 d] |
UPN12 | 11 | 10 | Death: DAH, D + 37 [2 d] |
UPN15 | 10 | 10-35 | Death: progressive VOD, D + 29 [4 d] |
UPN16 | 35 | 10-60 | Death: CMV pneumonitis, fungal sepsis, D + 89 [2 d] |
UPN17 | 11 | 10-20 | Death: CMV pneumonitis, D + 56 [18 d] |
UPN21 | 18 | 10-60 | Death: progressive VOD, D + 55 [0 d] |
ID . | Duration DF (d) . | Dose Range (DF) mg/kg/d . | Long-Term Outcome3-150 . |
---|---|---|---|
Responders3-151 | |||
UPN01 | 61 | 10-20 | Alive: NED, D + 1046 [976 d] |
UPN04 | 26 | 15-5-15 | Alive: NED, D + 833 [782 d] |
UPN08 | 36 | 10-20 | Death: relapsed ALL, D + 191 [130 d] |
UPN14 | 35 | 10-25 | Death: fungal sepsis, CMV pneumonitis, D + 47 [2 d] |
UPN18 | 14 | 10-20 | Death: respiratory failure, intracranial hemorrhage, D + 68 [43 d] |
UPN19 | 26 | 10-60 | Alive: NED, D + 324 [241 d] |
UPN22 | 34 | 10-60 | Alive: NED, D + 224 [179 d] |
UPN23 | 45 | 10-40 | Alive: NED, D + 217 [138 d] |
Nonresponders | |||
UPN02 | 4 | 10-15 | Death: ARF, D + 26 [1 d] |
UPN03 | 5 | 15 | Death: fungal sepsis, D + 25 [0 d] |
UPN05 | 15 | 10-25 | Death: progressive VOD, ARF, D + 27 [1 d] |
UPN06 | 2 | 10 | Death: fungal sepsis, D + 15 [0 d] |
UPN07 | 7 | 10-15 | Death: CMV pneumonitis, enterobacter, fungal sepsis, D + 45 [3 d] |
UPN09 | 11 | 10-40 | Death: progressive VOD, D + 40 [3 d] |
UPN12 | 11 | 10 | Death: DAH, D + 37 [2 d] |
UPN15 | 10 | 10-35 | Death: progressive VOD, D + 29 [4 d] |
UPN16 | 35 | 10-60 | Death: CMV pneumonitis, fungal sepsis, D + 89 [2 d] |
UPN17 | 11 | 10-20 | Death: CMV pneumonitis, D + 56 [18 d] |
UPN21 | 18 | 10-60 | Death: progressive VOD, D + 55 [0 d] |
Abbreviations: NED, no evaluable disease; DAH, diffuse alveolar hemorrhage; ARF, acute renal failure; CMV, cytomegalovirus.
Follow-up at day post SCT [number of days post discontinuation of DF].
Responders: Bilirubin decrease <2.0 mg/dL with resolution of VOD − associated symptoms and signs.