Table 4.

Outcome

ID Duration DF (d) Dose Range (DF) mg/kg/d Long-Term Outcome3-150
 
Responders3-151 
 
 UPN01  61  10-20 Alive: NED, D + 1046 [976 d]  
 UPN04  26 15-5-15  Alive: NED, D + 833 [782 d]  
 UPN08 36  10-20  Death: relapsed ALL, D + 191 [130 d] 
 UPN14  35  10-25  Death: fungal sepsis, CMV pneumonitis, D + 47 [2 d]  
 UPN18  14  10-20  Death: respiratory failure, intracranial hemorrhage, D + 68 [43 d] 
 UPN19  26  10-60  Alive: NED, D + 324 [241 d] 
 UPN22  34  10-60  Alive: NED, D + 224 [179 d] 
 UPN23  45  10-40  Alive: NED, D + 217 [138 d] 
 
Nonresponders  
 
 UPN02  4  10-15  Death: ARF, D + 26 [1 d]  
 UPN03  5  15  Death: fungal sepsis, D + 25 [0 d]  
 UPN05  15  10-25  Death: progressive VOD, ARF, D + 27 [1 d]  
 UPN06  2  10 Death: fungal sepsis, D + 15 [0 d]  
 UPN07  10-15  Death: CMV pneumonitis, enterobacter, fungal sepsis, D + 45 [3 d]  
 UPN09  11  10-40  Death: progressive VOD, D + 40 [3 d]  
 UPN12  11  10 Death: DAH, D + 37 [2 d]  
 UPN15  10  10-35 Death: progressive VOD, D + 29 [4 d]  
 UPN16  35 10-60  Death: CMV pneumonitis, fungal sepsis, D + 89 [2 d]  
 UPN17  11  10-20  Death: CMV pneumonitis, D + 56 [18 d]  
 UPN21  18  10-60  Death: progressive VOD, D + 55 [0 d] 
ID Duration DF (d) Dose Range (DF) mg/kg/d Long-Term Outcome3-150
 
Responders3-151 
 
 UPN01  61  10-20 Alive: NED, D + 1046 [976 d]  
 UPN04  26 15-5-15  Alive: NED, D + 833 [782 d]  
 UPN08 36  10-20  Death: relapsed ALL, D + 191 [130 d] 
 UPN14  35  10-25  Death: fungal sepsis, CMV pneumonitis, D + 47 [2 d]  
 UPN18  14  10-20  Death: respiratory failure, intracranial hemorrhage, D + 68 [43 d] 
 UPN19  26  10-60  Alive: NED, D + 324 [241 d] 
 UPN22  34  10-60  Alive: NED, D + 224 [179 d] 
 UPN23  45  10-40  Alive: NED, D + 217 [138 d] 
 
Nonresponders  
 
 UPN02  4  10-15  Death: ARF, D + 26 [1 d]  
 UPN03  5  15  Death: fungal sepsis, D + 25 [0 d]  
 UPN05  15  10-25  Death: progressive VOD, ARF, D + 27 [1 d]  
 UPN06  2  10 Death: fungal sepsis, D + 15 [0 d]  
 UPN07  10-15  Death: CMV pneumonitis, enterobacter, fungal sepsis, D + 45 [3 d]  
 UPN09  11  10-40  Death: progressive VOD, D + 40 [3 d]  
 UPN12  11  10 Death: DAH, D + 37 [2 d]  
 UPN15  10  10-35 Death: progressive VOD, D + 29 [4 d]  
 UPN16  35 10-60  Death: CMV pneumonitis, fungal sepsis, D + 89 [2 d]  
 UPN17  11  10-20  Death: CMV pneumonitis, D + 56 [18 d]  
 UPN21  18  10-60  Death: progressive VOD, D + 55 [0 d] 

Abbreviations: NED, no evaluable disease; DAH, diffuse alveolar hemorrhage; ARF, acute renal failure; CMV, cytomegalovirus.

F3-150

Follow-up at day post SCT [number of days post discontinuation of DF].

F3-151

Responders: Bilirubin decrease <2.0 mg/dL with resolution of VOD − associated symptoms and signs.

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