Table 1.

cALD patient and transplant characteristics (N = 66)

Data
Age, y 8.3 (4.4-47.1) 
Baseline Loes score 9 (1-19.5) 
Baseline gadolinium intensity score 2 (1-3) 
CSF total protein, mg/dL 37 (11-186) 
Preparative regimen, n  
 Nonmyeloablative 14 
 Myeloablative 52 
Stem cell source, n  
 Umbilical cord blood 34 
 Unrelated donor 11 
 Sibling marrow donor 19 
 Parent donor 
Total nucleated cell dose, 108 cells/kg 0.90 (0.24-8.25) 
CD34 dose, 106 cells/kg 1.43 (0.11-15.97) 
ANC recovery, d 16 (9-45) 
Platelet recovery, d 34 (13-244) 
Day-60 CD15 chimerism, % 100 (14.1-100) 
Day-60 CD3 chimerism, % 93.5 (0-100) 
Data
Age, y 8.3 (4.4-47.1) 
Baseline Loes score 9 (1-19.5) 
Baseline gadolinium intensity score 2 (1-3) 
CSF total protein, mg/dL 37 (11-186) 
Preparative regimen, n  
 Nonmyeloablative 14 
 Myeloablative 52 
Stem cell source, n  
 Umbilical cord blood 34 
 Unrelated donor 11 
 Sibling marrow donor 19 
 Parent donor 
Total nucleated cell dose, 108 cells/kg 0.90 (0.24-8.25) 
CD34 dose, 106 cells/kg 1.43 (0.11-15.97) 
ANC recovery, d 16 (9-45) 
Platelet recovery, d 34 (13-244) 
Day-60 CD15 chimerism, % 100 (14.1-100) 
Day-60 CD3 chimerism, % 93.5 (0-100) 

All data are median (range), unless noted otherwise.

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