Table 2.

Diagnostic and treatment resources in Latin America

Diagnostic resourceNo. of patients (N = 204)%Countries (N = 9)
Bone marrow biopsy    
 Availability according to survey   
 Availability in preliminary data 201 98  
Paroxysmal nocturnal hemoglobinuria clones    
 Availability according to survey   
 Availability in preliminary data 125 61  
Cytogenetics    
 Availability according to survey   
 Availability in preliminary data 92 45  
Clastogenic effect of diepoxybutane    
 Availability according to survey   
 Availability in preliminary data 68 33  
Telomere length test    
 Availability according to survey   
 Availability in preliminary data 52 25  
Treatment availability    
 ATG/cyclosporine   
 Horse ATG   
 Stem cell transplantation   
 Unrelated stem cell transplantation   
 Eltrombopag for second-line treatment   
Diagnostic resourceNo. of patients (N = 204)%Countries (N = 9)
Bone marrow biopsy    
 Availability according to survey   
 Availability in preliminary data 201 98  
Paroxysmal nocturnal hemoglobinuria clones    
 Availability according to survey   
 Availability in preliminary data 125 61  
Cytogenetics    
 Availability according to survey   
 Availability in preliminary data 92 45  
Clastogenic effect of diepoxybutane    
 Availability according to survey   
 Availability in preliminary data 68 33  
Telomere length test    
 Availability according to survey   
 Availability in preliminary data 52 25  
Treatment availability    
 ATG/cyclosporine   
 Horse ATG   
 Stem cell transplantation   
 Unrelated stem cell transplantation   
 Eltrombopag for second-line treatment   

ATG, antithymocyte globulin.

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