Table 3

Summary of efficacy endpoints

EndpointsNo. (%)[95% CI] or (range)
Overall CR + CRi + PR 16 (41) [26%, 58%] 
CR+CRi 12 (31) [17%, 48%] 
Median duration of CR+CRi, wk 20.5 (3.8-273.3) 
CR 10 (26) [13%, 42%] 
Median duration of CR, wk 27 (4.1-273.3) 
CRi 2 (5) — 
PR in T-ALL patients* 4 (10)  
    CR + CRi + PR 11 (42) [23%, 63%] 
    CR+CRi 8 (31) [14%, 52%] 
PR in T-LBL patients 
    CR + CRi + PR 5 (38) [14%, 68%] 
    CR 4 (31) [9%, 61%] 
DFS, median wks 20 (11-56) 
DFS at 1 year 7 (25) [6%, 50%] 
OS, median wks 20 (13-36) 
Survival at 1 year 7 (28) [15%, 43%] 
EndpointsNo. (%)[95% CI] or (range)
Overall CR + CRi + PR 16 (41) [26%, 58%] 
CR+CRi 12 (31) [17%, 48%] 
Median duration of CR+CRi, wk 20.5 (3.8-273.3) 
CR 10 (26) [13%, 42%] 
Median duration of CR, wk 27 (4.1-273.3) 
CRi 2 (5) — 
PR in T-ALL patients* 4 (10)  
    CR + CRi + PR 11 (42) [23%, 63%] 
    CR+CRi 8 (31) [14%, 52%] 
PR in T-LBL patients 
    CR + CRi + PR 5 (38) [14%, 68%] 
    CR 4 (31) [9%, 61%] 
DFS, median wks 20 (11-56) 
DFS at 1 year 7 (25) [6%, 50%] 
OS, median wks 20 (13-36) 
Survival at 1 year 7 (28) [15%, 43%] 

CR indicates complete remission; CRi, incomplete remission; CR+CRi, complete remission with or without hematologic recovery, PR, partial remission; DFS, disease-free survival; OS, overall survival.

*

N = 26.

N = 13.

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