Table 1

Patient and iPS cell characteristics

PatientIDUA mutationsSexAge at HCT, yTime after HCT, yDonor cellsNo. of iPS colonies per 100 000 cells
P1 Y167X Male 1.1 0.2 KC 
 W402X      
P2 W402X Male 1.8 0.8 KC 14 
 W402X    MSC 
PatientIDUA mutationsSexAge at HCT, yTime after HCT, yDonor cellsNo. of iPS colonies per 100 000 cells
P1 Y167X Male 1.1 0.2 KC 
 W402X      
P2 W402X Male 1.8 0.8 KC 14 
 W402X    MSC 

iPS indicates induced pluripotent stem; IDUA, iduronidase gene; HCT, hematopoietic cell transplantation; P, patient; Y, tyrosine; X, unknown amino acid; KC, keratinocytes; W, tryptophan; and MSC, mesenchymal stromal cells.

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