General clinical characteristics of long-term BHFS survivors
| Clinical characteristics . | Patients (%) (total n = 69) . |
|---|---|
| Age, y | |
| 0-5 | 29 (42) |
| >5-10 | 21 (30) |
| >10 | 18 (26) |
| NA | 1 (1) |
| Sex | |
| M | 37 (54) |
| F | 25 (36) |
| NA | 7 (10) |
| GA at birth, wk | |
| ≥37 | 19 (28) |
| 30-36 | 38 (55) |
| <30 | 9 (13) |
| NA | 3 (4) |
| First transfusion | |
| In utero at GA, wk | 41 (59) |
| ≥30 | 7 (10) |
| 20-29 | 24 (35) |
| <20 | 2 (3) |
| NA | 8 (12) |
| Postnatal | 28 (41) |
| Current status | |
| Transfusion-dependent | 53 (77) |
| Transplanted | 14 (20) |
| Deceased* | 2 (3) |
| Clinical characteristics . | Patients (%) (total n = 69) . |
|---|---|
| Age, y | |
| 0-5 | 29 (42) |
| >5-10 | 21 (30) |
| >10 | 18 (26) |
| NA | 1 (1) |
| Sex | |
| M | 37 (54) |
| F | 25 (36) |
| NA | 7 (10) |
| GA at birth, wk | |
| ≥37 | 19 (28) |
| 30-36 | 38 (55) |
| <30 | 9 (13) |
| NA | 3 (4) |
| First transfusion | |
| In utero at GA, wk | 41 (59) |
| ≥30 | 7 (10) |
| 20-29 | 24 (35) |
| <20 | 2 (3) |
| NA | 8 (12) |
| Postnatal | 28 (41) |
| Current status | |
| Transfusion-dependent | 53 (77) |
| Transplanted | 14 (20) |
| Deceased* | 2 (3) |
NA, data not available.
*Both patients suffered from severe developmental delay. One patient died at the age of 11 y owing to pneumonia and respiratory failure.28 The other patient died of fungal infection and severe graft-versus-host disease after HSC transplantation at the age of 13 y (4 mo after transplantation).58