Patient characteristics
UPN . | PNH type . | TE . | Tx/year . | Hb . | ARC . | LDH . | T bili . | ||||||
---|---|---|---|---|---|---|---|---|---|---|---|---|---|
Before . | During . | Before . | During . | Before . | During . | Before . | During . | Before . | During . | Before . | During . | ||
3 | AA-PNH | BC, DVT | No | 6 | 0 | 8.9 | 10.2 | 123 | 102 | 4000 | 397 | 45 | 17 |
11 | C-PNH | BC | No | 6 | 0 | 6 | 12.5 | 200 | 147 | 1500 | 478 | 40 | 20.2 |
18 | C-PNH | No | No | 1 | 0 | 9.9 | 11.1 | 80 | 121 | 2108 | 411 | 11 | 17 |
5 | AA-PNH | BC | No | 4 | 0 | 8.9 | 11.4 | 130 | 158 | 1765 | 487 | 12 | 19 |
20 | C-PNH | DVT, PE | No | 2 | 0 | 10.2 | 10.6 | 95 | 78 | 2439 | 571 | 9 | 13.8 |
9 | AA-PNH | No | No | 12 | 0 | 8.7 | 11.6 | 241 | 246 | 3000 | 353 | 25 | 11.3 |
13 | C-PNH | No | DVT | 0 | 0 | 9.2 | 9.9 | 73 | 95 | 3000 | 492 | 30 | 23 |
10 | AA-PNH | No | No | 6 | 0 | 7.2 | 9.3 | 33 | 195 | 2000 | 354 | 62 | 30.2 |
2 | C-PNH | No | No | 6 | 0 | 7 | 10.9 | 200 | 282 | 2500 | 623 | 45 | 26.4 |
12 | Int-PNH | No | No | 6 | 0 | 8 | 9.9 | 172 | 191 | 1000 | 467 | 21 | 36.1 |
14 | C-PNH | No | No | 2 | 0 | 8.5 | 10.1 | 150 | 102 | 3500 | 450 | 21 | 13.9 |
16 | C-PNH | No | No | 6 | 0 | 8.5 | 8.9 | 200 | 257 | 2100 | 421 | 11 | 33 |
17 | C-PNH | MVT | No | 6 | 0 | 9 | 9.9 | 150 | 139 | 3553 | 553 | 12 | 10.8 |
8 | C-PNH | DVT | No | 4 | 0 | 8.3 | 9.6 | 250 | 184 | 3700 | 565 | 9.7 | 17.9 |
22 | AA-PNH | BC | No | 6 | 0 | 9 | 10 | 170 | 202 | 800 | 299 | 8 | 71 |
21 | AA-PNH | No | No | 1 | 0 | 9.1 | 9.6 | 85 | 52 | 1925 | 621 | 12.8 | 11.9 |
1 | C-PNH | No | DVT | 12 | 0.8 | 7.5 | 8.8 | 160 | 145 | 1500 | 453 | 24 | 21.8 |
4 | C-PNH | BC | No | 6 | 0.6 | 7 | 10.2 | 150 | 120 | 2000 | 465 | 25 | 17.3 |
7 | AA-PNH | No | No | 36 | 0.8 | 5.9 | 9.7 | 350 | 240 | 2100 | 362 | 20 | 15.5 |
15 | C-PNH | No | No | 12 | 0.8 | 10.6 | 10.2 | 205 | 235 | 3000 | 515 | 16 | 17.4 |
19 | C-PNH | DVT, PE | No | 6 | 5.8 | 5 | 8.7 | 160 | 161 | 2000 | 507 | 10 | 16.7 |
6 | C-PNH | No | No | 8 | 1.1 | 7.7 | 8.2 | 175 | 352 | 1000 | 865 | 9 | 27 |
UPN . | PNH type . | TE . | Tx/year . | Hb . | ARC . | LDH . | T bili . | ||||||
---|---|---|---|---|---|---|---|---|---|---|---|---|---|
Before . | During . | Before . | During . | Before . | During . | Before . | During . | Before . | During . | Before . | During . | ||
3 | AA-PNH | BC, DVT | No | 6 | 0 | 8.9 | 10.2 | 123 | 102 | 4000 | 397 | 45 | 17 |
11 | C-PNH | BC | No | 6 | 0 | 6 | 12.5 | 200 | 147 | 1500 | 478 | 40 | 20.2 |
18 | C-PNH | No | No | 1 | 0 | 9.9 | 11.1 | 80 | 121 | 2108 | 411 | 11 | 17 |
5 | AA-PNH | BC | No | 4 | 0 | 8.9 | 11.4 | 130 | 158 | 1765 | 487 | 12 | 19 |
20 | C-PNH | DVT, PE | No | 2 | 0 | 10.2 | 10.6 | 95 | 78 | 2439 | 571 | 9 | 13.8 |
9 | AA-PNH | No | No | 12 | 0 | 8.7 | 11.6 | 241 | 246 | 3000 | 353 | 25 | 11.3 |
13 | C-PNH | No | DVT | 0 | 0 | 9.2 | 9.9 | 73 | 95 | 3000 | 492 | 30 | 23 |
10 | AA-PNH | No | No | 6 | 0 | 7.2 | 9.3 | 33 | 195 | 2000 | 354 | 62 | 30.2 |
2 | C-PNH | No | No | 6 | 0 | 7 | 10.9 | 200 | 282 | 2500 | 623 | 45 | 26.4 |
12 | Int-PNH | No | No | 6 | 0 | 8 | 9.9 | 172 | 191 | 1000 | 467 | 21 | 36.1 |
14 | C-PNH | No | No | 2 | 0 | 8.5 | 10.1 | 150 | 102 | 3500 | 450 | 21 | 13.9 |
16 | C-PNH | No | No | 6 | 0 | 8.5 | 8.9 | 200 | 257 | 2100 | 421 | 11 | 33 |
17 | C-PNH | MVT | No | 6 | 0 | 9 | 9.9 | 150 | 139 | 3553 | 553 | 12 | 10.8 |
8 | C-PNH | DVT | No | 4 | 0 | 8.3 | 9.6 | 250 | 184 | 3700 | 565 | 9.7 | 17.9 |
22 | AA-PNH | BC | No | 6 | 0 | 9 | 10 | 170 | 202 | 800 | 299 | 8 | 71 |
21 | AA-PNH | No | No | 1 | 0 | 9.1 | 9.6 | 85 | 52 | 1925 | 621 | 12.8 | 11.9 |
1 | C-PNH | No | DVT | 12 | 0.8 | 7.5 | 8.8 | 160 | 145 | 1500 | 453 | 24 | 21.8 |
4 | C-PNH | BC | No | 6 | 0.6 | 7 | 10.2 | 150 | 120 | 2000 | 465 | 25 | 17.3 |
7 | AA-PNH | No | No | 36 | 0.8 | 5.9 | 9.7 | 350 | 240 | 2100 | 362 | 20 | 15.5 |
15 | C-PNH | No | No | 12 | 0.8 | 10.6 | 10.2 | 205 | 235 | 3000 | 515 | 16 | 17.4 |
19 | C-PNH | DVT, PE | No | 6 | 5.8 | 5 | 8.7 | 160 | 161 | 2000 | 507 | 10 | 16.7 |
6 | C-PNH | No | No | 8 | 1.1 | 7.7 | 8.2 | 175 | 352 | 1000 | 865 | 9 | 27 |
AA-PNH, aplastic anemia-PNH; ARC, absolute reticulocyte count (×109); BC, Budd-Chiari syndrome; C-PNH, classic PNH; DVT, deep vein thrombosis; Hb, hemoglobin level; Int-PNH, intermediate PNH; MVT, mesenteric vein thrombosis; PE, pulmonary embolism; T bili, unfractionated bilirubin (μM/L); TE, thromboembolic events; Tx/year, number of packed red blood cell units transfused in the last year (before) or in 1 year during eculizumab treatment (during); UPN, unique patient number.