Table 1

Vector biodistribution in selected rhesus monkey tissues following in utero and postnatal readministration of scAAV-LP1-FVII-coop

TissueViral genome copies per cell
BM 0.38 
Cerebellum 0.02 
Jejunum 0.03 
Left ventricle 2.65 
Liver caudate 35.89 
Liver left lateral 9.35 
Liver right lateral 41.86 
Lung right middle 1.94 
Right adrenal gland 1.05 
Right axial lymph node 0.03 
Right ovary 4.53 
Spinal cord 0.045 
Spleen 0.40 
Naive liver 0.00 
Water 0.00 
TissueViral genome copies per cell
BM 0.38 
Cerebellum 0.02 
Jejunum 0.03 
Left ventricle 2.65 
Liver caudate 35.89 
Liver left lateral 9.35 
Liver right lateral 41.86 
Lung right middle 1.94 
Right adrenal gland 1.05 
Right axial lymph node 0.03 
Right ovary 4.53 
Spinal cord 0.045 
Spleen 0.40 
Naive liver 0.00 
Water 0.00 

Rhesus monkeys were injected in utero with 4 × 1011 vg/kg scAAV5-LP1-hFVII-coop near term, and administered a second dose of 4 × 1011 vg scAAV8-LP1-hFVII-coop IV 1 year after birth. Tissue samples were collected at ∼ 1.5 years of age and viral genome copy number per cell was quantified by quantitative PCR.

or Create an Account

Close Modal
Close Modal