Table 1

Outline of study design

GroupMMF, oral administration
Sirolimus, oral administration
Daclizumab, intravenous administration
Dose/scheduleDurationDose/scheduleDurationDose/schedule
NA NA NA NA NA 
25 mg/kg twice daily From d −7 to d 70 2 mg/kg once daily From d +3 to d 70 2 mg/kg at d −1; 1 mg/kg at d 15 
25 mg/kg twice daily From d −7 to d 70 4 mg/kg once daily; 2 mg/kg once daily From d 1 to d 7; from d 8 to d 70 NA; NA 
GroupMMF, oral administration
Sirolimus, oral administration
Daclizumab, intravenous administration
Dose/scheduleDurationDose/scheduleDurationDose/schedule
NA NA NA NA NA 
25 mg/kg twice daily From d −7 to d 70 2 mg/kg once daily From d +3 to d 70 2 mg/kg at d −1; 1 mg/kg at d 15 
25 mg/kg twice daily From d −7 to d 70 4 mg/kg once daily; 2 mg/kg once daily From d 1 to d 7; from d 8 to d 70 NA; NA 

For each group (n = 3), the AAV2-hF.IX vector at a dose of 8 × 1012 vg/kg was used.

NA indicates not applicable.

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