Table 1.

Demographics of the study cohort

CharacteristicN = 174
Diagnosis, n (%)  
ASM 27 (16) 
SM-AHN 119 (68) 
MCL 28 (16) 
Age  
Median (IQR) 68 (61-73) 
Range 31-88 
Sex, n (%)  
Male 102 (59) 
Female 72 (41) 
Race, n (%)  
White 150 (86) 
Black or African American 1 (1) 
Asian 3 (2) 
Other/unknown 20 (11) 
Ethnicity, n (%)  
Hispanic or Latino 2 (1) 
Not Hispanic or Latino 156 (90) 
Unknown 16 (9) 
Months between initial diagnosis and clinical trial screening  
Median (IQR) 11 (4-30) 
Range 0-638 
Unknown 
Months between last therapy and clinical trial screening  
Median (IQR) 1.41 (0.82-3.78) 
Range 0-242 
No. of previous therapies  
Median (IQR) 1 (0-2) 
Range 0-6 
Previous treatment with midostaurin, n (%) 81 (47) 
Serum tryptase, ng/mL  
Median (IQR) 210 (125-432) 
Range 12-1600 
BM mast cell burden, %  
Median (IQR) 40 (20-70) 
Range 1-95 
Unknown 
No. of WHO organ damage findings  
Median (IQR) 1 (1-2) 
Range 0-5 
No. of mIWG organ damage findings  
Median (IQR) 1 (0-3) 
Range 0-6 
CharacteristicN = 174
Diagnosis, n (%)  
ASM 27 (16) 
SM-AHN 119 (68) 
MCL 28 (16) 
Age  
Median (IQR) 68 (61-73) 
Range 31-88 
Sex, n (%)  
Male 102 (59) 
Female 72 (41) 
Race, n (%)  
White 150 (86) 
Black or African American 1 (1) 
Asian 3 (2) 
Other/unknown 20 (11) 
Ethnicity, n (%)  
Hispanic or Latino 2 (1) 
Not Hispanic or Latino 156 (90) 
Unknown 16 (9) 
Months between initial diagnosis and clinical trial screening  
Median (IQR) 11 (4-30) 
Range 0-638 
Unknown 
Months between last therapy and clinical trial screening  
Median (IQR) 1.41 (0.82-3.78) 
Range 0-242 
No. of previous therapies  
Median (IQR) 1 (0-2) 
Range 0-6 
Previous treatment with midostaurin, n (%) 81 (47) 
Serum tryptase, ng/mL  
Median (IQR) 210 (125-432) 
Range 12-1600 
BM mast cell burden, %  
Median (IQR) 40 (20-70) 
Range 1-95 
Unknown 
No. of WHO organ damage findings  
Median (IQR) 1 (1-2) 
Range 0-5 
No. of mIWG organ damage findings  
Median (IQR) 1 (0-3) 
Range 0-6 

IQR, interquartile range.

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