Table 1.

Relevant randomized clinical trials comparing transplant with standard treatment in NDMM patients aged up to 70 years

StudyStarting yearNumber of randomized patientsInductionTransplant regimenStandard regimenSurvival benefit of transplant
IFM9010  1990 200 VMCP/VBAP Mel 140/TBI-8 VMCP/VBAP EFS + OS 
MAG9011  1990 185 VAMP Cc/Cy/VP/Mel 140/TBI-12 VMCP EFS 
MAG9114  1991 190 VAMP Bu/Mel 140 or Mel 200 VMCP EFS 
MRC712  1993 401 VAMPC Mel 200 or Mel 140/TBI ABCM PFS + OS 
S932116  1993 516 VAD Mel 140/TBI-12 VBMCP None 
PETHEMA15  1994 164 VBMCP/VBAD Mel 200 or Mel 140/TBI-12 VBMCP/VBAD None 
M97G13  1997 194 VAD Mel 100  ×  2 MP EFS + OS 
IFM200917,18  2010 700 VRD ( ×  3) Mel 200 VRD ( ×  5) PFS 
DETERMINATION19  2010 722 VRD ( ×  3) Mel 200 VRD ( ×  5) PFS + EFS 
EMN02/HO9520  2011 1197 VCD ( ×  3 or 4) Mel 200 ( ×  1 or  ×  2) VMP PFS + PFS2 + OS 
FORTE21  2015 474 KRD or KCD ( ×  4) Mel 200 KRD ( ×  8) PFS 
EMN CARTITUDE623  2024 750 planned DVRD ( ×  4) Mel 200 cilta-cel 
StudyStarting yearNumber of randomized patientsInductionTransplant regimenStandard regimenSurvival benefit of transplant
IFM9010  1990 200 VMCP/VBAP Mel 140/TBI-8 VMCP/VBAP EFS + OS 
MAG9011  1990 185 VAMP Cc/Cy/VP/Mel 140/TBI-12 VMCP EFS 
MAG9114  1991 190 VAMP Bu/Mel 140 or Mel 200 VMCP EFS 
MRC712  1993 401 VAMPC Mel 200 or Mel 140/TBI ABCM PFS + OS 
S932116  1993 516 VAD Mel 140/TBI-12 VBMCP None 
PETHEMA15  1994 164 VBMCP/VBAD Mel 200 or Mel 140/TBI-12 VBMCP/VBAD None 
M97G13  1997 194 VAD Mel 100  ×  2 MP EFS + OS 
IFM200917,18  2010 700 VRD ( ×  3) Mel 200 VRD ( ×  5) PFS 
DETERMINATION19  2010 722 VRD ( ×  3) Mel 200 VRD ( ×  5) PFS + EFS 
EMN02/HO9520  2011 1197 VCD ( ×  3 or 4) Mel 200 ( ×  1 or  ×  2) VMP PFS + PFS2 + OS 
FORTE21  2015 474 KRD or KCD ( ×  4) Mel 200 KRD ( ×  8) PFS 
EMN CARTITUDE623  2024 750 planned DVRD ( ×  4) Mel 200 cilta-cel 

ABCM, doxorubicin-carmustine-cyclophosphamide-melphalan; CC, lomustine; cilta-cel, ciltacabtagene-autoleucel; Cy, cyclophosphamide; DVRD, daratumumab-bortezomib-lenalidomide-dexamethasone; VAD, vincristine-doxorubicin-dexamethasone; VAMP, vincristine-doxorubicin- methylprednisolone; VAMPC, vincristine-doxorubicin-methylprednisolone-cyclophosphamide; VBAD, vincristine-carmustine-doxorubicin- dexamethasone; VBAP, vincristine-carmustine-doxorubicin-prednisone; VCD, bortezomib-cyclophosphamide-dexamethasone; VMCP, vincristine- melphalan-cyclophosphamide-prednisone; VMP, bortezomib-melphalan-dexamethasone; VP, etoposide; VRD, bortezomib-lenalidomide-dexamethasone.

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