Table 1.

Demographics in sponsored clinical trials

DemographicsCases of severe IDIN, n (%)
(n = 21)
Sex  
Female 13 (61.9) 
Male 8 (38.1) 
Age category, y  
0-5 3 (14.3) 
6-11 6 (28.6) 
12-16 1 (4.8) 
17-35 5 (23.8) 
36-64 6 (28.6) 
Diagnosis  
Thalassemia major 12 (57.1) 
Thalassemia intermedia 1 (4.8) 
Hereditary hemochromatosis 2 (9.5) 
Hereditary spherocytosis 2 (9.5) 
Myelodysplasia 2 (9.5) 
Sickle cell anemia 1 (4.8) 
SCD 1 (4.8) 
DemographicsCases of severe IDIN, n (%)
(n = 21)
Sex  
Female 13 (61.9) 
Male 8 (38.1) 
Age category, y  
0-5 3 (14.3) 
6-11 6 (28.6) 
12-16 1 (4.8) 
17-35 5 (23.8) 
36-64 6 (28.6) 
Diagnosis  
Thalassemia major 12 (57.1) 
Thalassemia intermedia 1 (4.8) 
Hereditary hemochromatosis 2 (9.5) 
Hereditary spherocytosis 2 (9.5) 
Myelodysplasia 2 (9.5) 
Sickle cell anemia 1 (4.8) 
SCD 1 (4.8) 

In 1 case, 1 patient had 2 events of severe IDIN.

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